152. PCDH19 related syndrome Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 11 Drugs : 4 - (DrugBank : 1) / Drug target genes : 16 - Drug target pathways : 8

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
CCD 1042, MD 9150000, mepalon 1042, SPT316
   Marinus Pharmaceuticals, Inc
      2019   Phase 3   EUCTR2018-004496-12-IT   Australia;Belgium;Czechia;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;United Kingdom;United States
   Marinus Pharmaceuticals, Inc.
      2019   Phase 3   EUCTR2018-004496-12-FR   Australia;France;Hungary;Italy;Netherlands;Poland;Spain;United Kingdom;United States
      2015   -   EUCTR2015-001324-36-IT   Italy;United States
      -   Phase 3   EUCTR2018-004496-12-DK   Australia;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Spain;United Kingdom;United States
CCD 1042, MD 9150000, mepalon 1042, SPT3162
   Marinus Pharmaceuticals, Inc.
      2020   Phase 3   EUCTR2018-004496-12-HU   Australia;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Spain;United Kingdom;United States
      2020   Phase 3   EUCTR2018-004496-12-GB   Australia;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;United Kingdom;United States
      2019   Phase 2   EUCTR2018-004496-12-NL   Australia;Belgium;Czechia;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Spain;United Kingdom;United States
      -   Phase 2   EUCTR2018-004496-12-PL   Australia;Belgium;Czechia;Denmark;France;Germany;Hungary;Ireland;Italy;Netherlands;Poland;Spain;United Kingdom;United States
Exome and/or whole genome sequencing
   Boston Children's Hospital
      2010   -   NCT01858285   United States
Ganaxolone
   Marinus Pharmaceuticals
      2019   Phase 2   NCT03865732   Australia;France;Hungary;Italy;Netherlands;Poland;United States
      2015   Phase 2   NCT02358538   Italy;United States
   Marinus Pharmaceuticals, Inc
      2019   Phase 3   EUCTR2018-004496-12-IT   Australia;Belgium;Czechia;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;United Kingdom;United States
   Marinus Pharmaceuticals, Inc.
      2020   Phase 3   EUCTR2018-004496-12-HU   Australia;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Spain;United Kingdom;United States
      2020   Phase 3   EUCTR2018-004496-12-GB   Australia;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;United Kingdom;United States
      2019   Phase 2   EUCTR2018-004496-12-NL   Australia;Belgium;Czechia;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Spain;United Kingdom;United States
      2019   Phase 3   EUCTR2018-004496-12-FR   Australia;France;Hungary;Italy;Netherlands;Poland;Spain;United Kingdom;United States
      2015   -   EUCTR2015-001324-36-IT   Italy;United States
      -   Phase 2   EUCTR2018-004496-12-PL   Australia;Belgium;Czechia;Denmark;France;Germany;Hungary;Ireland;Italy;Netherlands;Poland;Spain;United Kingdom;United States
      -   Phase 3   EUCTR2018-004496-12-DK   Australia;Belgium;Czech Republic;Denmark;France;Germany;Hungary;Israel;Italy;Netherlands;Poland;Spain;United Kingdom;United States