202. Smith-Magenis syndrome Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 9 / Drugs : 8 - (DrugBank : 3) / Drug target genes : 3 - Drug target pathways : 4
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Acylated and unacylated ghrelin dosages
University Hospital, Toulouse
2021 - NCT04768803 France
Enviro-light artificial light BOX
Oregon Health and Science University
1998 - NCT00691574 United States
Hourly dosing OF THE nychtemeral secretion OF melatonin
Hôpital le Vinatier
2018 - NCT03492970 France
Melatonin
Oregon Health and Science University
1998 - NCT00691574 United States
Melatonin CR
National Human Genome Research Institute (NHGRI)
2007 Phase 1 NCT00506259 United States
RM-493
Rhythm Pharmaceuticals, Inc.
2020 Phase 2 EUCTR2017-000387-14-GR Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
2017 Phase 2 EUCTR2017-000387-14-GB Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
- Phase 2 EUCTR2017-000387-14-FR Australia;Canada;France;Germany;Greece;Ireland;Israel;Netherlands;Portugal;Spain;Turkey;United Kingdom;United States
Setmelanotide
Rhythm Pharmaceuticals, Inc.
2020 Phase 2 EUCTR2017-000387-14-GR Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
2017 Phase 2 EUCTR2017-000387-14-GB Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
- Phase 2 EUCTR2017-000387-14-FR Australia;Canada;France;Germany;Greece;Ireland;Israel;Netherlands;Portugal;Spain;Turkey;United Kingdom;United States
Tasimelteon
Vanda Pharmaceuticals
2016 Phase 1 NCT02776215 United States
2015 Phase 2/Phase 3 NCT02231008 United States
University Hospital, Toulouse
2021 - NCT04768803 France
Enviro-light artificial light BOX
Oregon Health and Science University
1998 - NCT00691574 United States
Hourly dosing OF THE nychtemeral secretion OF melatonin
Hôpital le Vinatier
2018 - NCT03492970 France
Melatonin
Oregon Health and Science University
1998 - NCT00691574 United States
Melatonin CR
National Human Genome Research Institute (NHGRI)
2007 Phase 1 NCT00506259 United States
RM-493
Rhythm Pharmaceuticals, Inc.
2020 Phase 2 EUCTR2017-000387-14-GR Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
2017 Phase 2 EUCTR2017-000387-14-GB Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
- Phase 2 EUCTR2017-000387-14-FR Australia;Canada;France;Germany;Greece;Ireland;Israel;Netherlands;Portugal;Spain;Turkey;United Kingdom;United States
Setmelanotide
Rhythm Pharmaceuticals, Inc.
2020 Phase 2 EUCTR2017-000387-14-GR Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
2017 Phase 2 EUCTR2017-000387-14-GB Canada;France;Germany;Greece;Israel;Netherlands;Spain;United Kingdom;United States
- Phase 2 EUCTR2017-000387-14-FR Australia;Canada;France;Germany;Greece;Ireland;Israel;Netherlands;Portugal;Spain;Turkey;United Kingdom;United States
Tasimelteon
Vanda Pharmaceuticals
2016 Phase 1 NCT02776215 United States
2015 Phase 2/Phase 3 NCT02231008 United States