227. Osler disease Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 56 / Drugs : 72 - (DrugBank : 21) / Drug target genes : 23 - Drug target pathways : 136
Other names | Hereditary hemorrhagic telangiectasia;Osler-Weber-Rendu disease; | ||
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Disease group | Chromosomal and gene abnormalities | ||
Domestic patients
Med expenses recipients (FY2023) |
991 patients Age distribution
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Related info (in Japanese) | - | ||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | 16-2-8. Hereditary hemorrhagic telangiectasia; HHT; Osler-Weber-Rendu disease | ||
Subtypes | - |