244. Maple syrup urine disease Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 5 / Drugs : 12 - (DrugBank : 2) / Drug target gene : 0 - Drug target pathway : 0
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Isoleucine
Meta Healthcare Ltd
2024 - NCT06581991 -
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Phenylbutyrate
Brendan Lee
2013 Phase 2/Phase 3 NCT01529060 United States
PKU express plus
Vitaflo International, Ltd
2021 - NCT05051657 United Kingdom
Valine
Meta Healthcare Ltd
2024 - NCT06581991 -
Meta Healthcare Ltd
2024 - NCT06581991 -
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Phenylbutyrate
Brendan Lee
2013 Phase 2/Phase 3 NCT01529060 United States
PKU express plus
Vitaflo International, Ltd
2021 - NCT05051657 United Kingdom
Valine
Meta Healthcare Ltd
2024 - NCT06581991 -
