244. Maple syrup urine disease Disease details / Clinical trials / Drug dev / DR info /


Clinical trials : 3 Drugs : 4 - (DrugBank : 3) / Drug target gene : 0 - Drug target pathway : 0

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Isoleucine
   Meta Healthcare Ltd
      2024   -   NCT06581991   -
Phenylbutyrate
   Brendan Lee
      2013   Phase 2/Phase 3   NCT01529060   United States
PKU express plus
   Vitaflo International, Ltd
      2021   -   NCT05051657   United Kingdom
Valine
   Meta Healthcare Ltd
      2024   -   NCT06581991   -