244. Maple syrup urine disease Disease details / Clinical trials / Drug dev / DR info /


Clinical trial : 1 Drug : 1 - (DrugBank : 1) / Drug target gene : 0 - Drug target pathway : 0

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countires)
Phenylbutyrate
   Brendan Lee
      2013   Phase 2/Phase 3   NCT01529060   United States;