255. Multiple carboxylase deficiency Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 2 / Drugs : 7 - (DrugBank : 0) / Drug target gene : 0 - Drug target pathway : 0
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
ORL-1B
Orpha Labs
2013 Phase 1/Phase 2 NCT03269045 -
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
ORL-1B
Orpha Labs
2013 Phase 1/Phase 2 NCT03269045 -
