255. Multiple carboxylase deficiency Disease details / Clinical trials / Drug dev / DR info /


Clinical trial : 1 Drug : 1 - (DrugBank : 0) / Drug target gene : 0 - Drug target pathway : 0

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countires)
ORL-1B
   Orpha Labs
      2013   Phase 1/Phase 2   NCT03269045   -