255. Multiple carboxylase deficiency Disease details / Clinical trials / Drug dev / DR info /


Clinical trials : 2 /  Drugs : 7 - (DrugBank : 0) / Drug target gene : 0 - Drug target pathway : 0

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
ORL-1B
   Orpha Labs
      2013   Phase 1/Phase 2   NCT03269045   -