279. Huge venous malformation with cervical, oral and pharyngeal diffuse lesion Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 24 / Drugs : 24 - (DrugBank : 12) / Drug target genes : 6 - Drug target pathways : 132
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Alpelisib
Murdoch Childrens Research Institute
2024 Phase 2 NCT05983159 Australia
Apixaban
Oslo University Hospital
2025 Phase 2 NCT06729034 Norway
Bleomycin + fibrovein
Oslo University Hospital
2011 Phase 4 NCT01347294 Norway
Bleomycin baxter
Department of Radiology, Oslo University Hospital, Norway
2011 Phase 4 EUCTR2011-001455-37-NO Norway
Dehydrated alcohol (absolute alcohol) BP FOR injection
ORFAGEN
2009 Phase 2 EUCTR2009-011276-29-FR France
Direct puncture repair / ethanol
Al-Azhar University
2018 - NCT05586919 Egypt
Direct puncture repair / polidocanol
Al-Azhar University
2018 - NCT05586919 Egypt
Enalapril
Oslo University Hospital
2025 Phase 2 NCT06788314 Norway
Ethanol
Shanghai Jiao Tong University School of Medicine Affiliated Ninth People's Hospital
2023 Phase 0 ChiCTR2300071751 China
Shanghai Ninth People's Hospital, Shanghai Jiao Tong University School of Medicine
2015 Phase 1 study ChiCTR-OIB-15007455 China
Shanghai Ninth People's Hospital, Shanghai JiaoTong University School of Medicine
2025 - ChiCTR2500102907 China
Ethanol 96% GEL
Orfagen
2007 Phase 2 NCT00462462 France;United States
Ethanol 98% solution
Orfagen
2007 Phase 2 NCT00462462 France;United States
Ethanol BP
ORFAGEN
2009 Phase 2 EUCTR2009-011276-29-FR France
Ethanol GEL
ORFAGEN
2009 Phase 2 EUCTR2009-011276-29-FR France
Ethanol-amine oleate sclerotherapy injection
Suez Canal University
2019 - NCT04930952 Egypt
Ethanolamine oleate
Danjo Atsushi
2009 Phase 2 JPRN-jRCTs071180067 -
Nomura Tadashi
2021 Phase 3 JPRN-jRCT2051200046 -
Fibrin
The First Affiliated Hospital of Sun Yat-Sen University
2022 Phase 2 ChiCTR2100053242 China
Fibrovein
Department of Radiology, Oslo University Hospital, Norway
2011 Phase 4 EUCTR2011-001455-37-NO Norway
L0122
ORFAGEN
2009 Phase 2 EUCTR2009-011276-29-FR France
Mirdametinib
Murdoch Childrens Research Institute
2024 Phase 2 NCT05983159 Australia
Polidocanol
Mori Hiroki
2024 Phase 2 JPRN-jRCTs031230604 Japan;Non
Uka Mayu
2021 - JPRN-jRCTs061200036 -
Qtorin 3.9% rapamycin anhydrous GEL
Palvella Therapeutics, Inc.
2024 Phase 2 NCT06653842 United States
Rapamycin
Peking Union Medical College Hospital
2018 Phase 4 NCT03767660 China
Sirolimus
Children's Hospital Medical Center, Cincinnati
2009 Phase 2 NCT00975819 United States
Gifu University Hospital
2020 Phase 3 JPRN-UMIN000038973 Japan
Medical University of South Carolina
2022 Phase 2 NCT04861064 United States
Shanghai Ninth People's Hospital
2021 Phase 0 ChiCTR2100052762 China
Trametinib tablet
Stanford University
2020 Phase 2 NCT04258046 United States
Murdoch Childrens Research Institute
2024 Phase 2 NCT05983159 Australia
Apixaban
Oslo University Hospital
2025 Phase 2 NCT06729034 Norway
Bleomycin + fibrovein
Oslo University Hospital
2011 Phase 4 NCT01347294 Norway
Bleomycin baxter
Department of Radiology, Oslo University Hospital, Norway
2011 Phase 4 EUCTR2011-001455-37-NO Norway
Dehydrated alcohol (absolute alcohol) BP FOR injection
ORFAGEN
2009 Phase 2 EUCTR2009-011276-29-FR France
Direct puncture repair / ethanol
Al-Azhar University
2018 - NCT05586919 Egypt
Direct puncture repair / polidocanol
Al-Azhar University
2018 - NCT05586919 Egypt
Enalapril
Oslo University Hospital
2025 Phase 2 NCT06788314 Norway
Ethanol
Shanghai Jiao Tong University School of Medicine Affiliated Ninth People's Hospital
2023 Phase 0 ChiCTR2300071751 China
Shanghai Ninth People's Hospital, Shanghai Jiao Tong University School of Medicine
2015 Phase 1 study ChiCTR-OIB-15007455 China
Shanghai Ninth People's Hospital, Shanghai JiaoTong University School of Medicine
2025 - ChiCTR2500102907 China
Ethanol 96% GEL
Orfagen
2007 Phase 2 NCT00462462 France;United States
Ethanol 98% solution
Orfagen
2007 Phase 2 NCT00462462 France;United States
Ethanol BP
ORFAGEN
2009 Phase 2 EUCTR2009-011276-29-FR France
Ethanol GEL
ORFAGEN
2009 Phase 2 EUCTR2009-011276-29-FR France
Ethanol-amine oleate sclerotherapy injection
Suez Canal University
2019 - NCT04930952 Egypt
Ethanolamine oleate
Danjo Atsushi
2009 Phase 2 JPRN-jRCTs071180067 -
Nomura Tadashi
2021 Phase 3 JPRN-jRCT2051200046 -
Fibrin
The First Affiliated Hospital of Sun Yat-Sen University
2022 Phase 2 ChiCTR2100053242 China
Fibrovein
Department of Radiology, Oslo University Hospital, Norway
2011 Phase 4 EUCTR2011-001455-37-NO Norway
L0122
ORFAGEN
2009 Phase 2 EUCTR2009-011276-29-FR France
Mirdametinib
Murdoch Childrens Research Institute
2024 Phase 2 NCT05983159 Australia
Polidocanol
Mori Hiroki
2024 Phase 2 JPRN-jRCTs031230604 Japan;Non
Uka Mayu
2021 - JPRN-jRCTs061200036 -
Qtorin 3.9% rapamycin anhydrous GEL
Palvella Therapeutics, Inc.
2024 Phase 2 NCT06653842 United States
Rapamycin
Peking Union Medical College Hospital
2018 Phase 4 NCT03767660 China
Sirolimus
Children's Hospital Medical Center, Cincinnati
2009 Phase 2 NCT00975819 United States
Gifu University Hospital
2020 Phase 3 JPRN-UMIN000038973 Japan
Medical University of South Carolina
2022 Phase 2 NCT04861064 United States
Shanghai Ninth People's Hospital
2021 Phase 0 ChiCTR2100052762 China
Trametinib tablet
Stanford University
2020 Phase 2 NCT04258046 United States