282. Congenital dyserythropoietic anemia Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 2 / Drugs : 3 - (DrugBank : 2) / Drug target genes : 3 - Drug target pathways : 7
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Luspatercept
FOndazione per la Ricerca sulle ANemie ed EMoglobinopatie in ItaliA - For Anemia
2023 Phase 2 EUCTR2020-005736-30-IT Italy
Omeprazole
Soroka University Medical Center
2013 Phase 4 NCT01795794 -
Reblozyl
FOndazione per la Ricerca sulle ANemie ed EMoglobinopatie in ItaliA - For Anemia
2023 Phase 2 EUCTR2020-005736-30-IT Italy
FOndazione per la Ricerca sulle ANemie ed EMoglobinopatie in ItaliA - For Anemia
2023 Phase 2 EUCTR2020-005736-30-IT Italy
Omeprazole
Soroka University Medical Center
2013 Phase 4 NCT01795794 -
Reblozyl
FOndazione per la Ricerca sulle ANemie ed EMoglobinopatie in ItaliA - For Anemia
2023 Phase 2 EUCTR2020-005736-30-IT Italy