282. Congenital dyserythropoietic anemia Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 2 Drugs : 3 - (DrugBank : 2) / Drug target genes : 3 - Drug target pathways : 7

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Luspatercept
   FOndazione per la Ricerca sulle ANemie ed EMoglobinopatie in ItaliA - For Anemia
      2023   Phase 2   EUCTR2020-005736-30-IT   Italy
Omeprazole
   Soroka University Medical Center
      2013   Phase 4   NCT01795794   -
Reblozyl
   FOndazione per la Ricerca sulle ANemie ed EMoglobinopatie in ItaliA - For Anemia
      2023   Phase 2   EUCTR2020-005736-30-IT   Italy