282. Congenital dyserythropoietic anemia Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 4 /  Drugs : 7 - (DrugBank : 3) / Drug target genes : 4 - Drug target pathways : 10

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Analysis OF genetic modifiers
   Hospital Universitari Vall d'Hebron Research Institute
      2020   -   NCT07206095   Spain
Disease phenotyping
   Hospital Universitari Vall d'Hebron Research Institute
      2020   -   NCT07206095   Spain
Luspatercept
   FOndazione per la Ricerca sulle ANemie ed EMoglobinopatie in ItaliA - For Anemia
      2023   Phase 2   EUCTR2020-005736-30-IT   Italy
Omeprazole
   Soroka University Medical Center
      2013   Phase 4   NCT01795794   -
Reblozyl
   FOndazione per la Ricerca sulle ANemie ed EMoglobinopatie in ItaliA - For Anemia
      2023   Phase 2   EUCTR2020-005736-30-IT   Italy
Zoledronic acid
   Institute of Hematology & Blood Diseases Hospital, China
      2026   Phase 1/Phase 2   NCT07471516   China