297. Alagille syndrome Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 45 / Drugs : 21 - (DrugBank : 10) / Drug target genes : 3 - Drug target pathways : 5
Other names | - | ||
---|---|---|---|
Disease group | Gastrointestinal diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
48 patients Age distribution
![]() |
||
Related info (in Japanese) | - | ||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | 12-8-24. Alagille syndrome | ||
Subtypes | - |