318. Citrin deficiency Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 5 / Drugs : 3 - (DrugBank : 3) / Drug target gene : 0 - Drug target pathway : 0
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Sodium pyruvate
Department of Pediatrics, Kobe university Graduate School of Medicine
2012 - JPRN-UMIN000008528 Japan
Working group for citrin deficiency
2010 - JPRN-UMIN000004290 Japan
Triheptanoin
Oishi Kimihiko
2024 Phase 1 JPRN-jRCTs031230755 -
Department of Pediatrics, Kobe university Graduate School of Medicine
2012 - JPRN-UMIN000008528 Japan
Working group for citrin deficiency
2010 - JPRN-UMIN000004290 Japan
Triheptanoin
Oishi Kimihiko
2024 Phase 1 JPRN-jRCTs031230755 -
