318. Citrin deficiency Disease details / Clinical trials / Drug dev / DR info /


Clinical trials : 5 /  Drugs : 3 - (DrugBank : 3) / Drug target gene : 0 - Drug target pathway : 0

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Sodium pyruvate
   Department of Pediatrics, Kobe university Graduate School of Medicine
      2012   -   JPRN-UMIN000008528   Japan
   Working group for citrin deficiency
      2010   -   JPRN-UMIN000004290   Japan
Triheptanoin
   Oishi Kimihiko
      2024   Phase 1   JPRN-jRCTs031230755   -