32. Autophagic vacuolar myopathy Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 2 / Drug : 1 - (DrugBank : 1) / Drug target gene : 0 - Drug target pathway : 0
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
RP-A501
Rocket Pharmaceuticals Inc.
2023 Phase 2 NCT06092034 Germany;Italy;United Kingdom;United States
2019 Phase 1 NCT03882437 United States
Rocket Pharmaceuticals Inc.
2023 Phase 2 NCT06092034 Germany;Italy;United Kingdom;United States
2019 Phase 1 NCT03882437 United States