32. Autophagic vacuolar myopathy Disease details / Clinical trials / Drug dev / DR info /


Clinical trials : 2 Drug : 1 - (DrugBank : 1) / Drug target gene : 0 - Drug target pathway : 0

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
RP-A501
   Rocket Pharmaceuticals Inc.
      2023   Phase 2   NCT06092034   Germany;Italy;United Kingdom;United States
      2019   Phase 1   NCT03882437   United States