324. Methylglutaconic aciduria Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 6 /  Drugs : 10 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 10

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Bezafibrate
   University Hospitals Bristol NHS Foundation Trust
      2019   Phase 2   EUCTR2015-001382-10-GB   United Kingdom
Elamipretide
   Stealth BioTherapeutics Inc.
      2026   Phase 4   NCT07531251   United Kingdom;United States
      2021   -   NCT04689360   -
      2017   Phase 2/Phase 3   NCT03098797   United States
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Triheptanoin
   Jerry Vockley, MD, PhD
      2009   -   NCT01461304   United States