324. Methylglutaconic aciduria Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 4 / Drugs : 3 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 10
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Bezafibrate
University Hospitals Bristol NHS Foundation Trust
2019 Phase 2 EUCTR2015-001382-10-GB United Kingdom
Elamipretide
Stealth BioTherapeutics Inc.
2021 - NCT04689360 -
2017 Phase 2/Phase 3 NCT03098797 United States
Triheptanoin
Jerry Vockley, MD, PhD
2009 - NCT01461304 United States
University Hospitals Bristol NHS Foundation Trust
2019 Phase 2 EUCTR2015-001382-10-GB United Kingdom
Elamipretide
Stealth BioTherapeutics Inc.
2021 - NCT04689360 -
2017 Phase 2/Phase 3 NCT03098797 United States
Triheptanoin
Jerry Vockley, MD, PhD
2009 - NCT01461304 United States