324. Methylglutaconic aciduria Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 6 / Drugs : 10 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 10
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Bezafibrate
University Hospitals Bristol NHS Foundation Trust
2019 Phase 2 EUCTR2015-001382-10-GB United Kingdom
Elamipretide
Stealth BioTherapeutics Inc.
2026 Phase 4 NCT07531251 United Kingdom;United States
2021 - NCT04689360 -
2017 Phase 2/Phase 3 NCT03098797 United States
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Triheptanoin
Jerry Vockley, MD, PhD
2009 - NCT01461304 United States
University Hospitals Bristol NHS Foundation Trust
2019 Phase 2 EUCTR2015-001382-10-GB United Kingdom
Elamipretide
Stealth BioTherapeutics Inc.
2026 Phase 4 NCT07531251 United Kingdom;United States
2021 - NCT04689360 -
2017 Phase 2/Phase 3 NCT03098797 United States
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Triheptanoin
Jerry Vockley, MD, PhD
2009 - NCT01461304 United States
