329. Aniridia Disease details / Clinical trials / Drug dev / DR info /


Clinical trials : 5 /  Drugs : 6 - (DrugBank : 2) / Drug target gene : 0 - Drug target pathway : 0

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Ataluren
   PTC Therapeutics
      2018   Phase 2   NCT04117880   -
      2016   Phase 2   NCT02647359   Canada;United States
Blood specimen
   M.D. Anderson Cancer Center
      1980   -   NCT00503893   United States
Conjunctival impression
   Fondation Ophtalmologique Adolphe de Rothschild
      2023   -   NCT05400590   France
Mitomycin
   Department of Ophthalmology, Keio University School of Medicine
      2013   -   JPRN-UMIN000002948   Japan
Peripheral venous blood sample
   Fondation Ophtalmologique Adolphe de Rothschild
      2023   -   NCT05400590   France
Questionnaire
   M.D. Anderson Cancer Center
      1980   -   NCT00503893   United States