339. MECP2 duplication syndrome Disease details / Clinical trials / Drug dev / DR info /


Clinical trials : 2 Drugs : 3 - (DrugBank : 0) / Drug target gene : 0 - Drug target pathway : 0

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
HG204
   HuidaGene Therapeutics Co., Ltd.
      2024   -   NCT06615206   China
ION440
   Ionis Pharmaceuticals, Inc.
      2024   Phase 1/Phase 2   NCT06430385   United States
Sham procedure
   Ionis Pharmaceuticals, Inc.
      2024   Phase 1/Phase 2   NCT06430385   United States