339. MECP2 duplication syndrome Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 2 / Drugs : 3 - (DrugBank : 0) / Drug target gene : 0 - Drug target pathway : 0
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
HG204
HuidaGene Therapeutics Co., Ltd.
2024 - NCT06615206 China
ION440
Ionis Pharmaceuticals, Inc.
2024 Phase 1/Phase 2 NCT06430385 United States
Sham procedure
Ionis Pharmaceuticals, Inc.
2024 Phase 1/Phase 2 NCT06430385 United States
HuidaGene Therapeutics Co., Ltd.
2024 - NCT06615206 China
ION440
Ionis Pharmaceuticals, Inc.
2024 Phase 1/Phase 2 NCT06430385 United States
Sham procedure
Ionis Pharmaceuticals, Inc.
2024 Phase 1/Phase 2 NCT06430385 United States