348. Lowe syndrome Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 2 / Drugs : 2 - (DrugBank : 1) / Drug target gene : 1 - Drug target pathways : 4
| Other names | Oculocerebrorenal syndrome of Lowe;OCRL; | ||
|---|---|---|---|
| Disease group | Neuromuscular diseases | ||
|
Domestic patients
Med expenses recipients, FY2024 (corrected) (in Japanese) |
- |
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| Clinical research form (in Japanese) MHLW Intractable Diseases, FY2026 (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 2-21-51. Lowe syndrome; oculocerebrorenal syndrome of Lowe; OCRL | ||
| Sub-diseases (Clinical research forms may not be available for all sub-diseases.) | - | ||
