3. Spinal muscular atrophy Clinical trials / Disease details
Clinical trials : 217 / Drugs : 149 - (DrugBank : 33) / Drug target genes : 54 - Drug target pathways : 80
| Previous names | - | ||
|---|---|---|---|
| Other names | Myelopathic muscular atrophy; | ||
| Disease group | Neuromuscular diseases | ||
| Related info (in Japanese) | |||
| Specific pediatric chronic diseases, Japan (in Japanese) | 11-18-42. spinal muscular atrophy; SMA | ||
| Subtypes | No. | Name | Specific pediatric chronic diseases, Japan (in Japanese) |
| 3-1. | Spinal muscular atrophy type I;SMA I;Werdnig-Hoffman disease; | 11-18-42. spinal muscular atrophy; SMA | |
| 3-2. | Spinal muscular atrophy type II;SMA II;Dubowitz disease; | 11-18-42. spinal muscular atrophy; SMA | |
| 3-3. | Spinal muscular atrophy type III;SMA III;Kugelberg-Welander disease; | 11-18-42. spinal muscular atrophy; SMA | |
| 3-4. | Spinal muscular atrophy type IV;SMA IV; | 11-18-42. spinal muscular atrophy; SMA | |