| 1 | (S)-2-amino-6-(2-hydroxypropanoyl)-7,8-dihydropteridin-4(3H)-one | - | - | - | - | [1]  240 240 💬
 | 
| 2 | 5,6,7,8-tetrahydrobiopterin | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 3 | 6R-BH4 | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [3]  86 86, 124, 240 💬
 | 
| 4 | A16AX07 | - | - | - | - | [1]  240 240 💬
 | 
| 5 | Amino acids | [1]  Amino acids Amino acids | - | - | - | [3]  70 70, 240, 298 💬
 | 
| 6 | BH4 | - | - | - | - | [5]  51 51, 86, 124, 240, 299 💬
 | 
| 7 | Blood samples | - | - | - | - | [9]  13 13, 41, 51, 61, 97, 227, 240, 271, 280 💬
 | 
| 8 | BMN 165 | - | - | - | - | [1]  240 240 💬
 | 
| 9 | BMN 165 (rAvPAL-PEG) | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 10 | BMN 307 | - | - | - | - | [1]  240 240 💬
 | 
| 11 | BMN165 20mg/day | - | - | - | - | [1]  240 240 💬
 | 
| 12 | BMN165 40mg/day | - | - | - | - | [1]  240 240 💬
 | 
| 13 | CDX | - | - | - | - | [2]  222 222, 240 💬
 | 
| 14 | CDX 6114 | - | - | - | - | [1]  240 240 💬
 | 
| 15 | CNSA-001 | - | - | - | - | [1]  240 240 💬
 | 
| 16 | Cohort 1 0.225g | - | - | - | - | [1]  240 240 💬
 | 
| 17 | Cohort 2 0.75g | - | - | - | - | [1]  240 240 💬
 | 
| 18 | Cohort 3 2.25 g | - | - | - | - | [1]  240 240 💬
 | 
| 19 | Corn | [1]  Corn Corn | - | - | - | [2]  46 46, 240 💬
 | 
| 20 | Corn/soy oil | [1]  Corn Corn | - | - | - | [1]  240 240 💬
 | 
| 21 | Diet | - | - | - | - | [4]  86 86, 97, 240, 299 💬
 | 
| 22 | Dietary Supplement for PKU patients | - | - | - | - | [1]  240 240 💬
 | 
| 23 | Docosahexaenoic acid | [1]  Doconexent Doconexent | - | - | - | [7]  6 6, 49, 90, 94, 240, 299, 301 💬
 | 
| 24 | Free amino acids intake | [1]  Amino acids Amino acids | - | - | - | [1]  240 240 💬
 | 
| 25 | Glycomacropeptide-based protein substitute | - | - | - | - | [1]  240 240 💬
 | 
| 26 | HMI-102 | - | - | - | - | [1]  240 240 💬
 | 
| 27 | HMI-103 | - | - | - | - | [1]  240 240 💬
 | 
| 28 | Immunosuppression | - | - | - | - | [1]  240 240 💬
 | 
| 29 | KUVAN | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 30 | Kuvan 100mg soluble tablet | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 31 | KuvanTM Therapy | - | - | - | - | [1]  240 240 💬
 | 
| 32 | Kuvan® | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 33 | Kuvan® (sapropterin dihydrochloride) | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 34 | Large Neutral Amino Acid Therapy | - | - | - | - | [1]  240 240 💬
 | 
| 35 | Low calorie protein substitute | - | - | - | - | [1]  240 240 💬
 | 
| 36 | Medikinet | - | - | - | - | [1]  240 240 💬
 | 
| 37 | Moxifloxacin | [1]  Moxifloxacin Moxifloxacin | [1]  Moxifloxacin 
                
                    Moxifloxacin
                
             💬
 | - | - | [9]  2 2, 6, 46, 49, 85, 86, 113, 240, 299 💬
 | 
| 38 | N.a. | - | - | - | - | [10]  3 3, 6, 8, 13, 46, 96, 97, 240, 256, 271 💬
 | 
| 39 | Nap | - | - | - | - | [2]  96 96, 240 💬
 | 
| 40 | Palynziq | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 41 | PEG | - | - | - | - | [15]  6 6, 13, 41, 46, 60, 65, 78, 96, 97, 140, 144, 240, 246, 299, 337 💬
 | 
| 42 | PEGVALIASE | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 43 | Pegvaliase-Pqpz | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 44 | Phenoptin | - | - | - | - | [2]  124 124, 240 💬
 | 
| 45 | Phenylalanine | [1]  Phenylalanine Phenylalanine | [1]  Phenylalanine 
                
                    Phenylalanine
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 46 | Phenylalanine restricted diet | [1]  Phenylalanine Phenylalanine | [1]  Phenylalanine 
                
                    Phenylalanine
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 47 | Phenylalanine-free protein substitute in tablet form (XPhe minis) | [1]  Phenylalanine Phenylalanine | [1]  Phenylalanine 
                
                    Phenylalanine
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 48 | Phenylalanine-free protein substitute tablets | [1]  Phenylalanine Phenylalanine | [1]  Phenylalanine 
                
                    Phenylalanine
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 49 | Phenylketonuria-type diet | - | - | - | - | [1]  240 240 💬
 | 
| 50 | PKU Explore | - | - | - | - | [1]  240 240 💬
 | 
| 51 | PKU express plus | - | - | - | - | [1]  240 240 💬
 | 
| 52 | PKU Sphere | - | - | - | - | [1]  240 240 💬
 | 
| 53 | PKU sphere liquid | - | - | - | - | [1]  240 240 💬
 | 
| 54 | PKU Start | - | - | - | - | [1]  240 240 💬
 | 
| 55 | PKU/TYR GMP Protein Substitute | - | - | - | - | [1]  240 240 💬
 | 
| 56 | Protein intake | - | - | - | - | [1]  240 240 💬
 | 
| 57 | PTC923 | - | - | - | - | [1]  240 240 💬
 | 
| 58 | RAvPAL-PEG | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 59 | RAvPAL-PEG 0.001 mg/kg | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 60 | RAvPAL-PEG 0.003 mg/kg | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 61 | RAvPAL-PEG 0.01 mg/kg | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 62 | RAvPAL-PEG 0.03 mg/kg | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 63 | RAvPAL-PEG 0.1 mg/kg | [1]  Pegvaliase Pegvaliase | [1]  Pegvaliase 
                
                    Pegvaliase
                
             💬
 | [1]  PAH PAH 💬
 | [5]  Biosynthesis of amino acids Biosynthesis of amino acids, Folate biosynthesis, Metabolic pathways, Phenylalanine metabolism, Phenylalanine, tyrosine and tryptophan biosynthesis 💬 | [1]  240 240 💬
 | 
| 64 | RTX | - | - | - | - | [5]  11 11, 46, 65, 222, 240 💬
 | 
| 65 | RTX-134 | - | - | - | - | [1]  240 240 💬
 | 
| 66 | Sapropterin | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [3]  86 86, 124, 240 💬
 | 
| 67 | Sapropterin (Kuvan) | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 68 | SAPROPTERIN DIHYDROCHLORIDE | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 69 | Sapropterin dihydrochloride, 6R-BH4, tetrahydrobiopterin | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 70 | Sapropterin Dihydrocholoride | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 71 | SAPROPTERIN HYDROCHLORIDE | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 72 | Sapropterin, sapropterin dihydrochloride | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 73 | Sapropterin, sapropterin hydrochloride | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 74 | Sapropterindihydrochloride | - | - | - | - | [1]  240 240 💬
 | 
| 75 | Saproterin dihydrochloride | - | - | - | - | [1]  240 240 💬
 | 
| 76 | SYNB1618 | - | - | - | - | [1]  240 240 💬
 | 
| 77 | SYNB1934 | - | - | - | - | [1]  240 240 💬
 | 
| 78 | Synergy | - | - | - | - | [1]  240 240 💬
 | 
| 79 | T1401 | - | - | - | - | [1]  240 240 💬
 | 
| 80 | Tetrahydrobiopterin | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 | 
| 81 | Tetrahydrobiopterin (BH4) | [1]  Sapropterin Sapropterin | [1]  Sapropterin 
                
                    Sapropterin
                
             💬
 | - | - | [1]  240 240 💬
 |