324. Methylglutaconic aciduria Clinical trials / Disease details

Clinical trials : 4 / Drugs : 4 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathways : 10

1 trial found

diseases per page:

Showing 1 to 1 of 1 diseases

Filter by

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01461304 (ClinicalTrials.gov)	April 17, 2009	25/10/2011	Dietary Therapy for Inherited Disorders of Energy Metabolism	Dietary Therapy for Inherited Disorders of Energy Metabolism	Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency;Carnitine Palmitoyltransferase Deficiencies ...	Drug: triheptanoin	Jerry Vockley, MD, PhD	Ultragenyx Pharmaceutical Inc	No longer available	1 Month	N/A	All			United States

First Previous1Next Last