Drug Description in Trials / DrugBank / KEGG DRUG


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No. 薬物名(臨床試験情報から抽出) DrugBank KEGG DRUG KEGG GENES KEGG PATHWAY 指定難病告示番号
1(7R,8R,9R)-2.3-Dimethyl-8-hydroxy-7(2-methoxyethoxy)- 9-phenyl-7.8.9.10-tetrahydro-imidazo-[1.2-h].[1.7].- naphthyridine----1件: 301 💬
24-Methylpyrazole----1件: 301 💬
3[ACU-4429]----1件: 301 💬
4[ARC1905]----1件: 301 💬
5[EU/3/13/1208 orphan]----1件: 301 💬
6AAVB-039----1件: 301 💬
7ACDN-01----2件: 90, 301 💬
8ACU-4429----1件: 301 💬
9ALK-001----1件: 301 💬
10ALK-001 (No generic name)----1件: 301 💬
11ARC1905----1件: 301 💬
12ARC1905 20 MG/ML----1件: 301 💬
13Avacincaptad pegol1件: Avacincaptad pegol1件: Avacincaptad pegol sodium 💬 1件: C5 💬 11件: Alcoholic liver disease, Complement and coagulation cascades, Coronavirus disease, Herpes simplex virus 1 infection, Neuroactive ligand-receptor interaction, Neutrophil extracellular trap formation, Pertussis, Prion disease, Regulation of actin cytoskeleton, Staphylococcus aureus infection, Systemic lupus erythematosus 💬1件: 301 💬
14DC6001----1件: 301 💬
15Diagnostic Test: Ocular Coherence Tomography-Angiography (OCT-A)----2件: 90, 301 💬
16Disulfiram1件: Disulfiram1件: Disulfiram 💬 3件: ALDH1B1,
ALDH2,
ALDH3A2 💬
13件: Alcoholic liver disease, Arginine and proline metabolism, Ascorbate and aldarate metabolism, Fatty acid degradation, Glycerolipid metabolism, Glycolysis / Gluconeogenesis, Histidine metabolism, Lysine degradation, Pantothenate and CoA biosynthesis, Pyruvate metabolism, Tryptophan metabolism, Valine, leucine and isoleucine degradation, beta-Alanine metabolism 💬3件: 46, 90, 301 💬
17Docosahexaenoic Acid (DHA) Dietary Supplement----2件: 13, 301 💬
18Emixustat1件: Emixustat1件: Emixustat 💬 --1件: 301 💬
19Emixustat hydrochloride1件: Emixustat1件: Emixustat 💬 --1件: 301 💬
20EMIXUSTAT HYDROCHLORIDE (ACU-4429)1件: Emixustat1件: Emixustat 💬 --1件: 301 💬
21Gene Therapy Product-MCO-010----2件: 90, 301 💬
22Gene Therapy-vMCO-010----1件: 301 💬
23Genetic: Blood and/or skin biopsy----2件: 90, 301 💬
24Genetic: HG005----1件: 301 💬
25Genetic: JWK006----1件: 301 💬
26Genetic: OPGx-BEST1----1件: 301 💬
27Genetic: RTx-021----1件: 301 💬
28Genetic: SB-007----1件: 301 💬
29HESC-RPE----1件: 301 💬
30Injection----2件: 6, 301 💬
31Interferon Gamma1件: Interferon Gamma---9件: 18, 65, 85, 96, 107, 228, 299, 301, 326 💬
32INTERFERON GAMMA-1B2件: Interferon Gamma,
Interferon gamma-1b
1件: Interferon gamma-1b 💬 2件: IFNGR1,
IFNGR2 💬
18件: Chagas disease, Cytokine-cytokine receptor interaction, HIF-1 signaling pathway, Herpes simplex virus 1 infection, Inflammatory bowel disease, Influenza A, JAK-STAT signaling pathway, Kaposi sarcoma-associated herpesvirus infection, Leishmaniasis, Natural killer cell mediated cytotoxicity, Necroptosis, Osteoclast differentiation, PD-L1 expression and PD-1 checkpoint pathway in cancer, Pathways in cancer, Th1 and Th2 cell differentiation, Th17 cell differentiation, Toxoplasmosis, Tuberculosis 💬7件: 18, 65, 85, 228, 299, 301, 326 💬
33LBS-008, BPN-14967----1件: 301 💬
34Lentiviral vector containing ABCA4 gene----1件: 301 💬
35Lentiviral vector containing the ABCA4 gene----1件: 301 💬
36Long term follow up in all patients who received SAR422459 in previous study TDU135831件: SAR422459---1件: 301 💬
37MA09-hRPE----1件: 301 💬
38Madeos----1件: 301 💬
39Mesenchymal Stem Cell-Derived Exosomes1件: Mesenchymal Stem Cell-Derived Exosomes---2件: 127, 301 💬
40Metformin1件: Metformin2件: Metformin hydrochloride ,
Metformin 💬
2件: PRKAA1,
PRKAA2 💬
20件: AMPK signaling pathway, Adipocytokine signaling pathway, Alcoholic liver disease, Apelin signaling pathway, Autophagy - animal, Circadian rhythm, Fluid shear stress and atherosclerosis, FoxO signaling pathway, Glucagon signaling pathway, Hypertrophic cardiomyopathy, Insulin resistance, Insulin signaling pathway, Longevity regulating pathway, Longevity regulating pathway - multiple species, Non-alcoholic fatty liver disease, Oxytocin signaling pathway, PI3K-Akt signaling pathway, Thermogenesis, Tight junction, mTOR signaling pathway 💬31件: 2, 6, 8, 13, 46, 49, 60, 65, 66, 67, 74, 75, 77, 81, 84, 85, 86, 97, 113, 127, 158, 206, 218, 222, 225, 233, 265, 285, 298, 299, 301 💬
41METFORMIN HYDROCHLORIDE1件: Metformin2件: Metformin hydrochloride ,
Metformin 💬
2件: PRKAA1,
PRKAA2 💬
20件: AMPK signaling pathway, Adipocytokine signaling pathway, Alcoholic liver disease, Apelin signaling pathway, Autophagy - animal, Circadian rhythm, Fluid shear stress and atherosclerosis, FoxO signaling pathway, Glucagon signaling pathway, Hypertrophic cardiomyopathy, Insulin resistance, Insulin signaling pathway, Longevity regulating pathway, Longevity regulating pathway - multiple species, Non-alcoholic fatty liver disease, Oxytocin signaling pathway, PI3K-Akt signaling pathway, Thermogenesis, Tight junction, mTOR signaling pathway 💬5件: 81, 158, 265, 299, 301 💬
42OCU410ST1件: OCU410ST---1件: 301 💬
43OpCT-001----3件: 90, 301, 303 💬
44Oral disulfiram1件: Disulfiram1件: Disulfiram 💬 3件: ALDH1B1,
ALDH2,
ALDH3A2 💬
13件: Alcoholic liver disease, Arginine and proline metabolism, Ascorbate and aldarate metabolism, Fatty acid degradation, Glycerolipid metabolism, Glycolysis / Gluconeogenesis, Histidine metabolism, Lysine degradation, Pantothenate and CoA biosynthesis, Pyruvate metabolism, Tryptophan metabolism, Valine, leucine and isoleucine degradation, beta-Alanine metabolism 💬2件: 90, 301 💬
45Other: Saline----8件: 2, 6, 46, 97, 98, 256, 274, 301 💬
46Other: Standard of Care Sildenafil1件: Sildenafil2件: Sildenafil citrate ,
Sildenafil 💬
1件: PDE5A 💬 2件: Purine metabolism, cGMP-PKG signaling pathway 💬2件: 90, 301 💬
47Other: Visual Acuity (VA)----2件: 90, 301 💬
48Over the counter DHA/EPA dietary supplementation----1件: 301 💬
49Ranibizumab1件: Ranibizumab1件: Ranibizumab 💬 1件: VEGFA 💬 24件: AGE-RAGE signaling pathway in diabetic complications, Bladder cancer, Calcium signaling pathway, Chemical carcinogenesis - reactive oxygen species, Chemical carcinogenesis - receptor activation, Fluid shear stress and atherosclerosis, Focal adhesion, HIF-1 signaling pathway, Human cytomegalovirus infection, Human papillomavirus infection, Integrin signaling, Kaposi sarcoma-associated herpesvirus infection, MAPK signaling pathway, MicroRNAs in cancer, PI3K-Akt signaling pathway, Pancreatic cancer, Pathways in cancer, Proteoglycans in cancer, Rap1 signaling pathway, Ras signaling pathway, Relaxin signaling pathway, Renal cell carcinoma, Rheumatoid arthritis, VEGF signaling pathway 💬4件: 34, 166, 227, 301 💬
50Ranibizumab injection (0.5 mg)1件: Ranibizumab1件: Ranibizumab 💬 1件: VEGFA 💬 24件: AGE-RAGE signaling pathway in diabetic complications, Bladder cancer, Calcium signaling pathway, Chemical carcinogenesis - reactive oxygen species, Chemical carcinogenesis - receptor activation, Fluid shear stress and atherosclerosis, Focal adhesion, HIF-1 signaling pathway, Human cytomegalovirus infection, Human papillomavirus infection, Integrin signaling, Kaposi sarcoma-associated herpesvirus infection, MAPK signaling pathway, MicroRNAs in cancer, PI3K-Akt signaling pathway, Pancreatic cancer, Pathways in cancer, Proteoglycans in cancer, Rap1 signaling pathway, Ras signaling pathway, Relaxin signaling pathway, Renal cell carcinoma, Rheumatoid arthritis, VEGF signaling pathway 💬2件: 166, 301 💬
51Saffron supplementation----1件: 301 💬
52SAR4224591件: SAR422459---1件: 301 💬
53Sham----4件: 90, 211, 301, 303 💬
54Sildenafil1件: Sildenafil2件: Sildenafil citrate ,
Sildenafil 💬
1件: PDE5A 💬 2件: Purine metabolism, cGMP-PKG signaling pathway 💬17件: 6, 46, 50, 51, 85, 86, 90, 113, 210, 211, 212, 225, 226, 278, 294, 299, 301 💬
55SORAPRAZAN1件: Soraprazan---1件: 301 💬
56SPVN06----2件: 90, 301 💬
57StarGen----1件: 301 💬
58Stem/progenitor cells transplantation----2件: 90, 301 💬
59STG-0011件: STG-001---1件: 301 💬
60Tinlarebant1件: Tinlarebant1件: Tinlarebant 💬 --1件: 301 💬
61TinlarebantProduct Code: LBS-008, BPN-14967Pharmaceutical Form: TabletINN or Proposed INN: TinlarebantCAS Number: NACurrent Sponsor code: LBS-008, BPN-14967Concentration unit: mg milligram(s)Concentration type: equalConcentration number: 5-Pharmaceutical form of the placebo: TabletRoute of administration of the placebo: Oral use----1件: 301 💬
62TOBRAMYCIN1件: Tobramycin2件: Tobramycin ,
Tobramycin sulfate 💬
--2件: 299, 301 💬
63Vett Lentiviral con gene ABCA4----1件: 301 💬
64VG801----1件: 301 💬
65Zimura----1件: 301 💬