Drug Description in Trials / DrugBank / KEGG DRUG


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No. Drug (Description in trials) DrugBank KEGG DRUG KEGG GENES KEGG PATHWAY Disease ID
1(+)- Epicatechin[1] Epicatechin---[1] 113 💬
2(+)-Epicatechin[1] Epicatechin---[1] 113 💬
3(-)-Epicatechin[1] Epicatechin---[2] 86, 113 💬
412 mg/kg GSK2402968----[1] 113 💬
52'-O-(2-methoxyethyl) phosphorothioate antisense oligonucleotide targeting CD49d RNA----[1] 113 💬
62011-2012 seasonal flu vaccine Intramuscular----[2] 3, 113 💬
72011-2012 seasonal flu vaccine Subcutaneous----[2] 3, 113 💬
829180.00.00, 34681.00.00, 34681.01.00, 34681.02.00----[1] 113 💬
93 mg/kg GSK2402968----[1] 113 💬
104-Benzyl-2-naphthalen-1-yl-1,2,4- thiadiazolidine-3,5-dione----[1] 113 💬
114-benzyl-2-naphthalen-1-yl-1,2,4-thiadiazolidine-3,5-dione----[1] 113 💬
125-(ethylsulfonyl)-2-(naphthalen-2-yl)benzo[d]oxazole----[1] 113 💬
136 mg/kg GSK2402968----[1] 113 💬
14750 mg metformin and 7.5 g L-citrulline daily p.o.[2] Citrulline,
Metformin
[4] Metformin hydrochloride ,
Metformin ,
L-Citrulline ,
Citrulline malate 💬
[2] PRKAA1,
PRKAA2 💬
[20] AMPK signaling pathway, Adipocytokine signaling pathway, Alcoholic liver disease, Apelin signaling pathway, Autophagy - animal, Circadian rhythm, Fluid shear stress and atherosclerosis, FoxO signaling pathway, Glucagon signaling pathway, Hypertrophic cardiomyopathy, Insulin resistance, Insulin signaling pathway, Longevity regulating pathway, Longevity regulating pathway - multiple species, Non-alcoholic fatty liver disease, Oxytocin signaling pathway, PI3K-Akt signaling pathway, Thermogenesis, Tight junction, mTOR signaling pathway 💬[1] 113 💬
159 mg/kg GSK2402968----[1] 113 💬
16[AVI-4658]----[1] 113 💬
17[Deflazacort][1] Deflazacort[1] Deflazacort 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
18[FG-3019]----[2] 85, 113 💬
19[FTX-1821]----[1] 113 💬
20[Idebenone][1] Idebenone[1] Idebenone 💬 --[1] 113 💬
21[Magnesium Oxide][2] Magnesium,
Magnesium oxide
[1] Magnesium oxide 💬 --[1] 113 💬
22[MNK-1411]----[1] 113 💬
23[NA]----[34] 3, 6, 11, 13, 14, 19, 28, 35, 41, 46, 49, 50, 53, 57, 62, 63, 65, 75, 79, 85, 90, 96, 97, 98, 113, 127, 162, 195, 223, 229, 251, 294, 299, 302 💬
24[NS-065/NCNP-01]----[1] 113 💬
25[PF-06939926]----[1] 113 💬
26[RO7494222 (SRP-9001)]----[1] 113 💬
27[SRP-4045]----[1] 113 💬
28[SRP-4053]----[1] 113 💬
29[SRP-5051]----[1] 113 💬
30[SRP-9001]----[1] 113 💬
31[Synacthen Ampoules 250 microgrammi]----[1] 113 💬
32[vamorolone][1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
33[WVE-210201]----[1] 113 💬
34AAV1-gamma-sarcoglycan vector injection----[1] 113 💬
35ACE-031 (Extension of cohort 1 from core study, A031-03)----[1] 113 💬
36ACE-031 (Extension of cohort 2 from core study, A031-03)----[1] 113 💬
37ACE-031 (Extension of cohort 3 from core study, A031-03)----[1] 113 💬
38ACE-031 0.5 mg/kg q4wk----[1] 113 💬
39ACE-031 1.0 mg/kg q2wk----[1] 113 💬
40ACE-083----[2] 10, 113 💬
41Acetate[1] Acetate---[52] 1, 2, 6, 10, 11, 13, 22, 35, 40, 46, 49, 51, 60, 63, 64, 65, 66, 67, 70, 71, 73, 75, 76, 77, 78, 79, 81, 83, 85, 86, 88, 89, 90, 96, 97, 113, 145, 156, 158, 162, 171, 206, 222, 223, 224, 225, 227, 235, 251, 265, 298, 299 💬
42Activity Monitor----[1] 113 💬
43Actonel Once a week 5mg film coated tablets----[1] 113 💬
44Adeno-associated viral vector serotype 8 containing the human MD1 gene----[1] 113 💬
45Adeno-associated viral vector serotype 9 containing the human mini-dystrophin gene----[1] 113 💬
46Adeno-associated virus serotype 9 carrying the human Fukutin-Related protein and target sequence of the miR-208a----[1] 113 💬
47Adeno-associated virus serotype rh74 containing the human delandistrogene moxeparvovec dystrophin gene[1] Delandistrogene moxeparvovec[1] Delandistrogene moxeparvovec 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
48ADENO-ASSOCIATED VIRUS SEROTYPE RH74 CONTAINING THE HUMAN MICRO- DYSTROPHIN GENE----[1] 113 💬
49ADENO-ASSOCIATED VIRUS SEROTYPE RH74 CONTAINING THE HUMAN MICRO-DYSTROPHIN GENE----[1] 113 💬
50Agamree----[1] 113 💬
51Albuterol[1] Albuterol[2] Albuterol sulfate ,
Albuterol 💬
[1] ADRB2 💬 [11] Adrenergic signaling in cardiomyocytes, Calcium signaling pathway, Chemical carcinogenesis - receptor activation, Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Regulation of lipolysis in adipocytes, Renin secretion, Salivary secretion, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[9] 12, 13, 86, 89, 113, 231, 256, 299, 340 💬
52Allogeneic Cardiosphere-Derived Cells[1] Allogeneic Cardiosphere-Derived Cells---[2] 57, 113 💬
53Allogeneic Cardiosphere-Derived Cells (CAP-1002)[1] Allogeneic Cardiosphere-Derived Cells---[1] 113 💬
54Amino Acid Intake----[1] 113 💬
55Amino acids[1] Amino acids---[6] 6, 70, 90, 113, 240, 298 💬
56Amlodipine[1] Amlodipine[4] Amlodipine besylate ,
Amlodipine maleate ,
Amlodipine ,
Amlodipine benzoate 💬
[4] CACNA1C,
CACNA1D,
CACNA1F,
CACNA1S 💬
[37] Adrenergic signaling in cardiomyocytes, Aldosterone synthesis and secretion, Alzheimer disease, Amphetamine addiction, Arrhythmogenic right ventricular cardiomyopathy, Calcium signaling pathway, Carbohydrate digestion and absorption, Cardiac muscle contraction, Cellular senescence, Chemical carcinogenesis - receptor activation, Cholinergic synapse, Circadian entrainment, Cortisol synthesis and secretion, Cushing syndrome, Dilated cardiomyopathy, Dopaminergic synapse, GABAergic synapse, Glutamatergic synapse, GnRH secretion, GnRH signaling pathway, Growth hormone synthesis, secretion and action, Hypertrophic cardiomyopathy, Insulin secretion, Long-term potentiation, MAPK signaling pathway, Oxytocin signaling pathway, Pathways of neurodegeneration - multiple diseases, Prion disease, Renin secretion, Retrograde endocannabinoid signaling, Serotonergic synapse, Taste transduction, Tight junction, Type II diabetes mellitus, Vascular smooth muscle contraction, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[6] 51, 67, 79, 113, 222, 298 💬
57Amondys 45----[1] 113 💬
58Anti-myostati----[1] 113 💬
59Anti-Myostatin Adnectin----[1] 113 💬
60AOC 1001[1] AOC 1001[1] Delpacibart 💬 [1] TFRC 💬 [6] Endocytosis, Ferroptosis, HIF-1 signaling pathway, Hematopoietic cell lineage, TGF-beta signaling pathway, Virion - Lassa virus and SFTS virus 💬[1] 113 💬
61AOC 1001 (del-desiran)[1] AOC 1001[1] Delpacibart 💬 [1] TFRC 💬 [6] Endocytosis, Ferroptosis, HIF-1 signaling pathway, Hematopoietic cell lineage, TGF-beta signaling pathway, Virion - Lassa virus and SFTS virus 💬[1] 113 💬
62AOC 1020----[1] 113 💬
63AOC 1044----[1] 113 💬
64AOC-1020[1] AOC-1020---[1] 113 💬
65Apitegromab[1] Apitegromab[1] Apitegromab 💬 [1] MSTN 💬 [1] Cytokine-cytokine receptor interaction 💬[2] 3, 113 💬
66Arginine[1] Arginine[3] Arginine hydrochloride ,
Arginine ,
Arginine hydrochloride 💬
--[16] 2, 21, 46, 57, 58, 67, 72, 96, 97, 98, 113, 210, 223, 225, 251, 299 💬
67ARO-DM1 Intravenous (IV) Infusion----[1] 113 💬
68ARO-DM1 subcutaneous (SC) injection----[1] 113 💬
69ARO-DUX4 for Injection----[1] 113 💬
70ATA-100[1] ATA-100---[1] 113 💬
71ATA-100 (AAV9 encoding FKRP gene)[1] ATA-100---[1] 113 💬
72ATA-200----[1] 113 💬
73ATALUREN[1] Ataluren[1] Ataluren 💬 --[6] 19, 113, 140, 246, 299, 329 💬
74Ataluren 1000 mg[1] Ataluren[1] Ataluren 💬 --[1] 113 💬
75Ataluren 125 mg[1] Ataluren[1] Ataluren 💬 --[1] 113 💬
76Ataluren 250 mg[1] Ataluren[1] Ataluren 💬 --[1] 113 💬
77ATL 1102----[1] 113 💬
78ATL1102[1] ATL1102---[2] 13, 113 💬
79ATL1102 25mg[1] ATL1102---[1] 113 💬
80ATL1102 50mg[1] ATL1102---[1] 113 💬
81ATX-01[1] ATX-01---[1] 113 💬
82ATYR1940[1] ATYR-1940---[1] 113 💬
83Autologous bone marrow mononuclear cell transplantation----[1] 113 💬
84AVI-4658----[1] 113 💬
85AVI-4658 (Eteplirsen)[1] Eteplirsen[1] Eteplirsen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
86AVI-4658 (PMO)----[1] 113 💬
87AVI-4658 for Injection----[1] 113 💬
88BB-301[1] BB-301---[1] 113 💬
89BBP-418----[1] 113 💬
90BBP-418 (ribitol)[1] Ribitol[1] Ribitol 💬 --[1] 113 💬
91Behavioral: CHDR Monitoring Remotely (MORE)----[1] 113 💬
92Behavioral: Concurrent exercise training----[1] 113 💬
93Behavioral: Control Group Typically Developing----[1] 113 💬
94Behavioral: Diet----[2] 113, 265 💬
95Behavioral: Duchenne Muscular Dystrophy group with Deflazacort[1] Deflazacort[1] Deflazacort 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
96Behavioral: Duchenne Muscular Dystrophy group with Prednisone/Predisolone[1] Prednisone[1] Prednisone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
97Behavioral: Duchenne Muscular Dystrophy group without Corticosteroids therapy----[1] 113 💬
98Behavioral: Exercise----[6] 6, 46, 113, 265, 299, 344 💬
99Behavioral: Exercise Training on standard steroid regimen----[1] 113 💬
100Behavioral: Regular exercise----[1] 113 💬
101Behavioral: Withings Blood Pressure Monitor----[1] 113 💬
102Behavioral: Withings Body+ scale----[1] 113 💬
103Behavioral: Withings Steel HR----[1] 113 💬
104Betaloc ZOK 100, 95 mg----[1] 113 💬
105Betaloc ZOK 25, 23,75 mg----[1] 113 💬
106BIO101----[1] 113 💬
107Biological: Umbilical Cord Based Allogenic Mesenchymal Stem Cell----[1] 113 💬
108Bisoprolol[1] Bisoprolol[2] Bisoprolol fumarate ,
Bisoprolol 💬
[1] ADRB1 💬 [13] Adrenergic signaling in cardiomyocytes, Calcium signaling pathway, Chemical carcinogenesis - receptor activation, Dilated cardiomyopathy, Gap junction, Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Regulation of lipolysis in adipocytes, Renin secretion, Salivary secretion, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[5] 57, 58, 67, 86, 113 💬
109Bisoprolol Fumarate[1] Bisoprolol[2] Bisoprolol fumarate ,
Bisoprolol 💬
[1] ADRB1 💬 [13] Adrenergic signaling in cardiomyocytes, Calcium signaling pathway, Chemical carcinogenesis - receptor activation, Dilated cardiomyopathy, Gap junction, Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Regulation of lipolysis in adipocytes, Renin secretion, Salivary secretion, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[1] 113 💬
110Bisphosphonate treatment----[2] 113, 299 💬
111Blood assays----[1] 113 💬
112Blood draw (genetic testing)----[1] 113 💬
113Blood sample----[33] 2, 3, 6, 8, 10, 13, 14, 19, 34, 46, 48, 49, 51, 53, 61, 63, 65, 66, 67, 77, 79, 84, 88, 96, 97, 107, 113, 127, 195, 206, 235, 274, 299 💬
114Blood test----[19] 2, 6, 13, 36, 46, 49, 51, 74, 79, 83, 96, 113, 127, 162, 227, 256, 280, 299, 300 💬
115BLS-M22[1] BLS-M22---[1] 113 💬
116BMN 044[1] BMN-044---[1] 113 💬
117BMN 044 IV 6 mg/kg[1] BMN-044---[1] 113 💬
118BMN 044 IV 9 mg/kg[1] BMN-044---[1] 113 💬
119BMN 044 SC 6 mg/kg[1] BMN-044---[1] 113 💬
120BMN 045[1] BMN-045---[1] 113 💬
121BMN 053----[1] 113 💬
122BMN 351----[1] 113 💬
123BMN053[1] BMN-053---[1] 113 💬
124BMS-986089----[1] 113 💬
125BMS-986089-01 (RO7239361) , anti-myostatin----[1] 113 💬
126BMS-986089-01 (RO7239361) Injections, 15 mg/Syringe (21.4 mg/mL)----[1] 113 💬
127BMS-986089-01 (RO7239361) Injections, 35 mg/Syringe (50 mg/mL)----[1] 113 💬
128BMS-986089-01 (RO7239361) Injections, 50 mg/Syringe (71.4 mg/mL)----[1] 113 💬
129BMS-986089-01 (RO7239361) Injections, 7.5 mg/Syringe (10.7 mg/mL)----[1] 113 💬
130BMS-986089-01 (RO7239361), anti-myostatin----[1] 113 💬
131BMS-986089-01 Injections, 15 mg/Syringe (21.4 mg/mL)----[1] 113 💬
132BMS-986089-01 Injections, 35 mg/Syringe (50 mg/mL)----[1] 113 💬
133BMS-986089-01 Injections, 50 mg/Syringe (71.4 mg/mL)----[1] 113 💬
134BMS-986089-01 Injections, 7.5 mg/Syringe (10.7 mg/mL)----[1] 113 💬
135BMS-986089-01, Anti-myostatin----[1] 113 💬
136Bocidelpar[1] Bocidelpar[2] Bocidelpar ,
Bocidelpar sulfate 💬
[1] PPARG 💬 [12] AMPK signaling pathway, Efferocytosis, Huntington disease, Lipid and atherosclerosis, Longevity regulating pathway, Non-alcoholic fatty liver disease, Osteoclast differentiation, PPAR signaling pathway, Pathways in cancer, Thermogenesis, Thyroid cancer, Transcriptional misregulation in cancer 💬[1] 113 💬
137BOTULINUM TOXIN TYPE A[1] Botulinum toxin type A[4] Botulinum toxin type A ,
OnabotulinumtoxinA ,
AbobotulinumtoxinA ,
Incobotulinumtoxin A 💬
[1] SNAP25 💬 [2] Insulin secretion, Synaptic vesicle cycle 💬[13] 2, 5, 6, 7, 13, 15, 17, 47, 70, 113, 149, 171, 226 💬
138Cabaletta----[1] 113 💬
139Calcichew D3 Forte----[1] 113 💬
140Calcifediol[1] Calcifediol[1] Calcifediol 💬 [1] VDR 💬 [5] Chemical carcinogenesis - receptor activation, Endocrine and other factor-regulated calcium reabsorption, Mineral absorption, Parathyroid hormone synthesis, secretion and action, Tuberculosis 💬[2] 86, 113 💬
141Canakinumab[1] Canakinumab[1] Canakinumab 💬 [1] IL1B 💬 [43] AGE-RAGE signaling pathway in diabetic complications, African trypanosomiasis, Alcoholic liver disease, Alzheimer disease, Amoebiasis, C-type lectin receptor signaling pathway, Chagas disease, Coronavirus disease, Cytokine-cytokine receptor interaction, Cytosolic DNA-sensing pathway, Fluid shear stress and atherosclerosis, Graft-versus-host disease, Hematopoietic cell lineage, Herpes simplex virus 1 infection, Human cytomegalovirus infection, IL-17 signaling pathway, Inflammatory bowel disease, Inflammatory mediator regulation of TRP channels, Influenza A, Legionellosis, Leishmaniasis, Lipid and atherosclerosis, MAPK signaling pathway, Malaria, Measles, NF-kappa B signaling pathway, NOD-like receptor signaling pathway, Necroptosis, Non-alcoholic fatty liver disease, Osteoclast differentiation, Pathogenic Escherichia coli infection, Pathways of neurodegeneration - multiple diseases, Pertussis, Prion disease, Rheumatoid arthritis, Salmonella infection, Shigellosis, TNF signaling pathway, Th17 cell differentiation, Toll-like receptor signaling pathway, Tuberculosis, Type I diabetes mellitus, Yersinia infection 💬[11] 46, 54, 56, 84, 106, 107, 108, 113, 266, 267, 269 💬
142Canakinumab Injection [Ilaris][1] Canakinumab[1] Canakinumab 💬 [1] IL1B 💬 [43] AGE-RAGE signaling pathway in diabetic complications, African trypanosomiasis, Alcoholic liver disease, Alzheimer disease, Amoebiasis, C-type lectin receptor signaling pathway, Chagas disease, Coronavirus disease, Cytokine-cytokine receptor interaction, Cytosolic DNA-sensing pathway, Fluid shear stress and atherosclerosis, Graft-versus-host disease, Hematopoietic cell lineage, Herpes simplex virus 1 infection, Human cytomegalovirus infection, IL-17 signaling pathway, Inflammatory bowel disease, Inflammatory mediator regulation of TRP channels, Influenza A, Legionellosis, Leishmaniasis, Lipid and atherosclerosis, MAPK signaling pathway, Malaria, Measles, NF-kappa B signaling pathway, NOD-like receptor signaling pathway, Necroptosis, Non-alcoholic fatty liver disease, Osteoclast differentiation, Pathogenic Escherichia coli infection, Pathways of neurodegeneration - multiple diseases, Pertussis, Prion disease, Rheumatoid arthritis, Salmonella infection, Shigellosis, TNF signaling pathway, Th17 cell differentiation, Toll-like receptor signaling pathway, Tuberculosis, Type I diabetes mellitus, Yersinia infection 💬[1] 113 💬
143CAP-1002----[1] 113 💬
144Cardicor (Merck brand)----[1] 113 💬
145Cardiovascular profile----[1] 113 💬
146Carvedilol[1] Carvedilol[2] Carvedilol ,
Carvedilol phosphate 💬
[5] ADRA1A,
ADRA1B,
ADRA1D,
ADRB1,
ADRB2 💬
[15] AMPK signaling pathway, Adrenergic signaling in cardiomyocytes, Calcium signaling pathway, Chemical carcinogenesis - receptor activation, Dilated cardiomyopathy, Gap junction, Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Regulation of lipolysis in adipocytes, Renin secretion, Salivary secretion, Vascular smooth muscle contraction, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[7] 6, 46, 57, 58, 86, 113, 210 💬
147CASIMERSEN[1] Casimersen[1] Casimersen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
148CAT-1004----[1] 113 💬
149Chronic Corticosteroid Therapy----[1] 113 💬
150Cialis 10 mg film-coated tablets----[2] 86, 113 💬
151Cialis 2.5 mg film-coated tablets----[2] 86, 113 💬
152Cialis 20 mg film-coated tablets----[2] 86, 113 💬
153Cialis 5 mg film-coated tablets----[2] 86, 113 💬
154Citrulline[1] Citrulline[2] L-Citrulline ,
Citrulline malate 💬
--[3] 21, 86, 113 💬
155Clenbuterol[1] Clenbuterol[2] Clenbuterol hydrochloride ,
Clenbuterol 💬
[1] ADRB2 💬 [11] Adrenergic signaling in cardiomyocytes, Calcium signaling pathway, Chemical carcinogenesis - receptor activation, Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Regulation of lipolysis in adipocytes, Renin secretion, Salivary secretion, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[6] 1, 2, 6, 57, 113, 256 💬
156Coenzyme Q10----[11] 2, 5, 6, 8, 10, 18, 49, 57, 107, 113, 193 💬
157Coenzyme Q10 and Lisinopril[1] Lisinopril[2] Lisinopril ,
Lisinopril 💬
[1] ACE 💬 [6] Chagas disease, Coronavirus disease, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[1] 113 💬
158Corticosteroid----[12] 13, 42, 43, 44, 45, 66, 84, 96, 97, 113, 222, 223 💬
159Corticosteroide----[1] 113 💬
160Corticosteroids----[13] 41, 46, 49, 63, 64, 97, 107, 113, 164, 222, 223, 296, 300 💬
161Cosintropina acetato----[1] 113 💬
162Cosyntropin----[1] 113 💬
163Cosyntropin acetate[2] Acetate,
Tetracosactide
[2] Cosyntropin ,
Tetracosactide acetate 💬
[1] MC2R 💬 [6] Aldosterone synthesis and secretion, Cortisol synthesis and secretion, Cushing syndrome, Hormone signaling, Neuroactive ligand-receptor interaction, cAMP signaling pathway 💬[1] 113 💬
164Cr13C----[1] 113 💬
165CRD-TMH-001----[1] 113 💬
166CRD007----[1] 113 💬
167Creatine[1] Creatine---[18] 1, 2, 3, 5, 6, 8, 13, 15, 21, 46, 49, 50, 97, 113, 156, 201, 256, 337 💬
168Creatine Monohydrate[1] Creatine---[5] 2, 8, 97, 113, 156 💬
169Creatine-13C[1] Creatine---[1] 113 💬
170Cyclosporin A----[12] 46, 49, 53, 54, 56, 60, 63, 93, 95, 113, 164, 222 💬
171Decortin----[2] 46, 113 💬
172DEFLAN*10CPR 6MG----[1] 113 💬
173Deflazacort[1] Deflazacort[1] Deflazacort 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[2] 30, 113 💬
174Deflazacort 6 mg Tablets[1] Deflazacort[1] Deflazacort 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
175Dehydroepiandrosterone 100 and 400 mg----[1] 113 💬
176Del-desiran (AOC 1001)[1] AOC 1001[1] Delpacibart 💬 [1] TFRC 💬 [6] Endocytosis, Ferroptosis, HIF-1 signaling pathway, Hematopoietic cell lineage, TGF-beta signaling pathway, Virion - Lassa virus and SFTS virus 💬[1] 113 💬
177Delandistrogene moxeparvovec[1] Delandistrogene moxeparvovec[1] Delandistrogene moxeparvovec 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
178Delandistrogene moxeparvovec (SRP-9001)[1] Delandistrogene moxeparvovec[1] Delandistrogene moxeparvovec 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
179Delandistrogene moxeparvovecProduct Code: RO7494222 (SRP-9001)Pharmaceutical Form: Solution for infusionINN or Proposed INN: delandistrogene moxeparvovecCAS Number: 2305040-16-6Current Sponsor code: RO7494222 (SRP-9001)Other descriptive name: Delandistrogene moxeparvovecConcentration unit: vector genomes (vg)/mLConcentration type: equalConcentration number: 1.33 x 10^13-----[1] 113 💬
180Delpacibart zotadirsen----[1] 113 💬
181DELTACORTENE*20CPR 5MG----[3] 49, 97, 113 💬
182Deramiocel (CAP-1002)----[1] 113 💬
183DEXMEDETOMIDINE[1] Dexmedetomidine[2] Dexmedetomidine ,
Dexmedetomidine hydrochloride 💬
[3] ADRA2A,
ADRA2B,
ADRA2C 💬
[4] Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, cGMP-PKG signaling pathway 💬[15] 2, 4, 6, 21, 22, 34, 46, 70, 107, 113, 171, 212, 215, 226, 280 💬
184Diagnostic Test: 30 seconds sit to stand test----[1] 113 💬
185Diagnostic Test: Beck depression inventory----[1] 113 💬
186Diagnostic Test: Berg balance scale----[1] 113 💬
187Diagnostic Test: Brief Pain Inventory Short-Form----[1] 113 💬
188Diagnostic Test: Cardiac MRI----[1] 113 💬
189Diagnostic Test: DM1-ActivC----[1] 113 💬
190Diagnostic Test: dosage of blood biomarker miR1----[1] 113 💬
191Diagnostic Test: Fatigue and Daytime Sleepiness Scale----[1] 113 💬
192Diagnostic Test: Functional Index-2----[1] 113 💬
193Diagnostic Test: GSGC----[1] 113 💬
194Diagnostic Test: Hand opening time----[1] 113 💬
195Diagnostic Test: Hyperpolarized 13C-Pyruvate----[3] 57, 84, 113 💬
196Diagnostic Test: Manual muscle testing----[1] 113 💬
197Diagnostic Test: McGill pain questionnaire----[1] 113 💬
198Diagnostic Test: Motor function scales----[2] 111, 113 💬
199Diagnostic Test: Muscle Elastography----[1] 113 💬
200Diagnostic Test: Muscle ultrasound----[5] 3, 15, 111, 113, 256 💬
201Diagnostic Test: Myotonia (from Individualised Neuromuscular Quality of Life Questionnaire)----[1] 113 💬
202Diagnostic Test: Myotonia Behaviour scale----[1] 113 💬
203Diagnostic Test: Pressure pain threshold----[4] 3, 15, 113, 256 💬
204Diagnostic Test: Quantitative muscle testing----[1] 113 💬
205Diagnostic Test: Quick Motor Function Test----[4] 3, 15, 113, 256 💬
206Diagnostic Test: R-PAct----[1] 113 💬
207Diagnostic Test: Scale for Assessment and Rating of Ataxia----[1] 113 💬
208Diagnostic Test: Six minute walking test----[1] 113 💬
209DILATREND----[1] 113 💬
210Dosing Extension----[1] 113 💬
211Drisapersen[1] Drisapersen[1] Drisapersen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
212DRISAPERSEN SODIUM[1] Drisapersen[1] Drisapersen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
213DS-5141b----[1] 113 💬
214DT-DEC01[1] DT-DEC01---[1] 113 💬
215DT-DEC01 (MB^N/MB^DMD DEC)[1] DT-DEC01---[1] 113 💬
216DYNE-101----[1] 113 💬
217DYNE-251[1] DYNE-251---[1] 113 💬
218EDASALONEXENT[1] Edasalonexent[1] Edasalonexent 💬 [1] RELA 💬 [76] AGE-RAGE signaling pathway in diabetic complications, Acute myeloid leukemia, Adipocytokine signaling pathway, Alcoholic liver disease, Alzheimer disease, Amoebiasis, Apoptosis, B cell receptor signaling pathway, C-type lectin receptor signaling pathway, Cadherin signaling, Cellular senescence, Chagas disease, Chemical carcinogenesis - reactive oxygen species, Chemical carcinogenesis - receptor activation, Chemokine signaling pathway, Chronic myeloid leukemia, Cocaine addiction, Coronavirus disease, Cytosolic DNA-sensing pathway, Diabetic cardiomyopathy, Epithelial cell signaling in Helicobacter pylori infection, Epstein-Barr virus infection, Fluid shear stress and atherosclerosis, HIF-1 signaling pathway, Hepatitis B, Hepatitis C, Herpes simplex virus 1 infection, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Human papillomavirus infection, IL-17 signaling pathway, Inflammatory bowel disease, Influenza A, Insulin resistance, Kaposi sarcoma-associated herpesvirus infection, Legionellosis, Leishmaniasis, Lipid and atherosclerosis, Longevity regulating pathway, MAPK signaling pathway, Measles, Mitophagy - animal, NF-kappa B signaling pathway, NOD-like receptor signaling pathway, Neurotrophin signaling pathway, Neutrophil extracellular trap formation, Non-alcoholic fatty liver disease, Osteoclast differentiation, PD-L1 expression and PD-1 checkpoint pathway in cancer, PI3K-Akt signaling pathway, Pancreatic cancer, Pathogenic Escherichia coli infection, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Pertussis, Prolactin signaling pathway, Prostate cancer, RIG-I-like receptor signaling pathway, Ras signaling pathway, Relaxin signaling pathway, Salmonella infection, Shigellosis, Small cell lung cancer, Sphingolipid signaling pathway, T cell receptor signaling pathway, TNF signaling pathway, Th1 and Th2 cell differentiation, Th17 cell differentiation, Toll-like receptor signaling pathway, Toxoplasmosis, Transcriptional misregulation in cancer, Tuberculosis, Viral carcinogenesis, Yersinia infection, cAMP signaling pathway 💬[1] 113 💬
219EMD 87580----[1] 113 💬
220EMEA/H/C/000638----[1] 113 💬
221EMFLAZA® (DEFLAZACORT)[1] Deflazacort[1] Deflazacort 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
222Empagliflozin[1] Empagliflozin[1] Empagliflozin 💬 --[17] 28, 46, 57, 58, 65, 67, 72, 77, 86, 96, 97, 113, 222, 223, 257, 298, 299 💬
223Empagliflozin Tablets[1] Empagliflozin[1] Empagliflozin 💬 --[2] 57, 113 💬
224EN001----[2] 10, 113 💬
225EnaHexal®, 10mg----[1] 113 💬
226Enalapril[1] Enalapril[2] Enalapril maleate ,
Enalapril 💬
[1] ACE 💬 [6] Chagas disease, Coronavirus disease, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[10] 13, 19, 46, 57, 66, 113, 210, 222, 223, 279 💬
227EnalHexal®, 5 mg----[1] 113 💬
228ENTR-601-44[1] ENTR-601-44---[1] 113 💬
229ENTR-601-45----[1] 113 💬
230EPA and DHA----[1] 113 💬
231EPI-321----[1] 113 💬
232Epicatechin[1] Epicatechin---[2] 86, 113 💬
233Epigallocatechin[1] Epigallocatechin---[5] 8, 13, 28, 85, 113 💬
234Epigallocatechin-Gallate[1] Epigallocatechin---[1] 113 💬
235Eplerenone[1] Eplerenone[1] Eplerenone 💬 [1] NR3C2 💬 [1] Aldosterone-regulated sodium reabsorption 💬[5] 57, 75, 113, 210, 215 💬
236ERX-963----[1] 113 💬
237Esomeprazole[1] Esomeprazole[5] Esomeprazole magnesium ,
Esomeprazole sodium ,
Esomeprazole ,
Esomeprazole strontium ,
Esomeprazole magnesium dihydrate 💬
[2] ATP4A,
ATP4B 💬
[3] Collecting duct acid secretion, Gastric acid secretion, Oxidative phosphorylation 💬[10] 6, 13, 46, 86, 98, 107, 113, 234, 298, 299 💬
238Esomeprazolo----[1] 113 💬
239Essential Amino Acids Supplementation intervention[1] Amino acids---[1] 113 💬
240ETEPLIRSEN[1] Eteplirsen[1] Eteplirsen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
241Eteplirsen Injection[1] Eteplirsen[1] Eteplirsen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
242Eucardic----[2] 57, 113 💬
243EV substance code: SUB188638----[1] 113 💬
244Exercise training on twice-weekly steroids----[1] 113 💬
245Exondys 51----[1] 113 💬
246EXONDYS 51™----[1] 113 💬
247Ezutromid[1] Ezutromid---[1] 113 💬
248FG-3019----[3] 85, 113, 222 💬
249Filgrastim[1] Filgrastim[1] Filgrastim 💬 [1] CSF3R 💬 [5] Cytokine-cytokine receptor interaction, Hematopoietic cell lineage, JAK-STAT signaling pathway, PI3K-Akt signaling pathway, Pathways in cancer 💬[30] 2, 6, 13, 25, 26, 28, 34, 35, 38, 40, 41, 42, 45, 46, 47, 49, 51, 60, 62, 63, 65, 96, 113, 164, 256, 283, 284, 285, 296, 331 💬
250Flavocoxid----[1] 113 💬
251Fordadistrogene movaparvovec[1] Fordadistrogene movaparvovec---[1] 113 💬
252Fragment antibody targeting human TfR1 conjugated to phosphorodiamidate morpholino oligomer----[1] 113 💬
253FTX-1821----[1] 113 💬
254Gadolinium[1] Gadolinium---[8] 13, 34, 46, 65, 77, 86, 113, 305 💬
255Genetic: AB-1003 dose level 1----[1] 113 💬
256Genetic: AB-1003 dose level 2----[1] 113 💬
257Genetic: BB-301: Dose escalation phase 1b cohort 1[1] BB-301---[1] 113 💬
258Genetic: BB-301: Dose escalation phase 1b cohort 2[1] BB-301---[1] 113 💬
259Genetic: BB-301: Dose escalation phase 1b cohort 3[1] BB-301---[1] 113 💬
260Genetic: BB-301: Dose expansion phase 2a[1] BB-301---[1] 113 💬
261Genetic: BBM-D101----[1] 113 💬
262Genetic: Delandistrogene Moxeparvovec[1] Delandistrogene moxeparvovec[1] Delandistrogene moxeparvovec 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
263Genetic: end-of-life nursing education consortium-pediatric palliative care as web based-training plus usual care----[2] 113, 299 💬
264Genetic: GEN6050X intravenous injection----[1] 113 💬
265Genetic: Genetic characterization----[1] 113 💬
266Genetic: Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- Second cohort----[1] 113 💬
267Genetic: HG302----[1] 113 💬
268Genetic: INS1201----[1] 113 💬
269Genetic: Laboratory Tests----[2] 113, 256 💬
270Genetic: No Intervention----[2] 19, 113 💬
271Genetic: Non invasive prenatal diagnosis----[3] 8, 113, 206 💬
272Genetic: PF-06939926----[1] 113 💬
273Genetic: rAAV1.tMCK.human-alpha-sarcoglycan- First cohort----[1] 113 💬
274Genetic: RGX-202----[1] 113 💬
275Genetic: RNA extraction----[1] 113 💬
276Genetic: SGT-001----[1] 113 💬
277Genetic: SGT-003----[1] 113 💬
278Genetic: Single dose intravenous of BBM-D101----[1] 113 💬
279Genetic: SPOT-03----[1] 113 💬
280Genetic: SRD-001[1] SRD-001---[2] 57, 113 💬
281Genetic: SRP-6004[1] SRP-6004---[1] 113 💬
282Genetic: SRP-9003----[1] 113 💬
283Genetic: SRP-9004----[1] 113 💬
284Genetic: Triplet-primed PCR or Long-read sequencing----[1] 113 💬
285GenPHSat injection (Efficacy)----[1] 113 💬
286GenPHSat injection (Safety)----[1] 113 💬
287Gentamicin[1] Gentamicin[2] Gentamicin sulfate ,
Gentamicin 💬
--[4] 13, 36, 113, 299 💬
288Gentamicin infusions twice a week for six months[1] Gentamicin[2] Gentamicin sulfate ,
Gentamicin 💬
--[1] 113 💬
289Givinostat[1] Givinostat[1] Givinostat 💬 [11] HDAC1,
HDAC10,
HDAC11,
HDAC2,
HDAC3,
HDAC4,
HDAC5,
HDAC6,
HDAC7,
HDAC8,
HDAC9 💬
[20] ATP-dependent chromatin remodeling, Alcoholism, Amphetamine addiction, Amyotrophic lateral sclerosis, Apelin signaling pathway, Cell cycle, Chronic myeloid leukemia, Epstein-Barr virus infection, Human papillomavirus infection, Huntington disease, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, Notch signaling pathway, Pathways in cancer, Polycomb repressive complex, TGF-beta signaling pathway, Thyroid hormone signaling pathway, Transcriptional misregulation in cancer, Viral carcinogenesis 💬[2] 107, 113 💬
290Givinostat (hydrochloride monohydrate)[1] Givinostat[1] Givinostat 💬 [11] HDAC1,
HDAC10,
HDAC11,
HDAC2,
HDAC3,
HDAC4,
HDAC5,
HDAC6,
HDAC7,
HDAC8,
HDAC9 💬
[20] ATP-dependent chromatin remodeling, Alcoholism, Amphetamine addiction, Amyotrophic lateral sclerosis, Apelin signaling pathway, Cell cycle, Chronic myeloid leukemia, Epstein-Barr virus infection, Human papillomavirus infection, Huntington disease, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, Notch signaling pathway, Pathways in cancer, Polycomb repressive complex, TGF-beta signaling pathway, Thyroid hormone signaling pathway, Transcriptional misregulation in cancer, Viral carcinogenesis 💬[1] 113 💬
291GIVINOSTAT (hyrochloride monohydrate)[1] Givinostat[1] Givinostat 💬 [11] HDAC1,
HDAC10,
HDAC11,
HDAC2,
HDAC3,
HDAC4,
HDAC5,
HDAC6,
HDAC7,
HDAC8,
HDAC9 💬
[20] ATP-dependent chromatin remodeling, Alcoholism, Amphetamine addiction, Amyotrophic lateral sclerosis, Apelin signaling pathway, Cell cycle, Chronic myeloid leukemia, Epstein-Barr virus infection, Human papillomavirus infection, Huntington disease, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, Notch signaling pathway, Pathways in cancer, Polycomb repressive complex, TGF-beta signaling pathway, Thyroid hormone signaling pathway, Transcriptional misregulation in cancer, Viral carcinogenesis 💬[1] 113 💬
292Givinostat (idrocloruro monoidrato)[1] Givinostat[1] Givinostat 💬 [11] HDAC1,
HDAC10,
HDAC11,
HDAC2,
HDAC3,
HDAC4,
HDAC5,
HDAC6,
HDAC7,
HDAC8,
HDAC9 💬
[20] ATP-dependent chromatin remodeling, Alcoholism, Amphetamine addiction, Amyotrophic lateral sclerosis, Apelin signaling pathway, Cell cycle, Chronic myeloid leukemia, Epstein-Barr virus infection, Human papillomavirus infection, Huntington disease, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, Notch signaling pathway, Pathways in cancer, Polycomb repressive complex, TGF-beta signaling pathway, Thyroid hormone signaling pathway, Transcriptional misregulation in cancer, Viral carcinogenesis 💬[1] 113 💬
293Givinostat Hydrochloride[1] Givinostat[1] Givinostat 💬 [11] HDAC1,
HDAC10,
HDAC11,
HDAC2,
HDAC3,
HDAC4,
HDAC5,
HDAC6,
HDAC7,
HDAC8,
HDAC9 💬
[20] ATP-dependent chromatin remodeling, Alcoholism, Amphetamine addiction, Amyotrophic lateral sclerosis, Apelin signaling pathway, Cell cycle, Chronic myeloid leukemia, Epstein-Barr virus infection, Human papillomavirus infection, Huntington disease, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, Notch signaling pathway, Pathways in cancer, Polycomb repressive complex, TGF-beta signaling pathway, Thyroid hormone signaling pathway, Transcriptional misregulation in cancer, Viral carcinogenesis 💬[1] 113 💬
294Givinostat Hydrochloride - Cohort 2[1] Givinostat[1] Givinostat 💬 [11] HDAC1,
HDAC10,
HDAC11,
HDAC2,
HDAC3,
HDAC4,
HDAC5,
HDAC6,
HDAC7,
HDAC8,
HDAC9 💬
[20] ATP-dependent chromatin remodeling, Alcoholism, Amphetamine addiction, Amyotrophic lateral sclerosis, Apelin signaling pathway, Cell cycle, Chronic myeloid leukemia, Epstein-Barr virus infection, Human papillomavirus infection, Huntington disease, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, Notch signaling pathway, Pathways in cancer, Polycomb repressive complex, TGF-beta signaling pathway, Thyroid hormone signaling pathway, Transcriptional misregulation in cancer, Viral carcinogenesis 💬[1] 113 💬
295GlucoCorticoid----[7] 46, 49, 66, 113, 223, 228, 300 💬
296Glutamine[1] L-Glutamine[1] Glutamine 💬 --[7] 87, 89, 96, 97, 113, 245, 299 💬
297GNT0004----[1] 113 💬
298GNT0006----[1] 113 💬
299Gold[1] Gold---[71] 2, 5, 6, 11, 13, 17, 19, 21, 22, 28, 34, 35, 46, 49, 50, 53, 54, 56, 57, 58, 60, 63, 64, 65, 66, 68, 71, 75, 76, 77, 79, 84, 85, 86, 88, 91, 93, 95, 96, 97, 98, 107, 113, 127, 137, 158, 162, 167, 171, 193, 206, 215, 218, 222, 223, 224, 226, 227, 228, 230, 235, 271, 291, 294, 296, 298, 299, 310, 318, 331, 340 💬
300GOLODIRSEN[1] Golodirsen[1] Golodirsen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
301Golodirsen 50 MG/1 ML Intravenous Solution [VYONDYS 53][1] Golodirsen[1] Golodirsen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
302Granulocyte colony-stimulating factor (Filgrastim)[1] Filgrastim[1] Filgrastim 💬 [1] CSF3R 💬 [5] Cytokine-cytokine receptor interaction, Hematopoietic cell lineage, JAK-STAT signaling pathway, PI3K-Akt signaling pathway, Pathways in cancer 💬[1] 113 💬
303GRT6019----[1] 113 💬
304GSK2402968----[1] 113 💬
305GSK2402968 3mg/kg/week----[1] 113 💬
306GSK2402968 6 mg/kg/week----[1] 113 💬
307GSK2402968 6mg/kg/week----[1] 113 💬
308Guanidine[1] Guanidine[1] Guanidine hydrochloride 💬 --[2] 46, 113 💬
309GYM329[1] GYM329---[2] 3, 113 💬
310H44AON188----[1] 113 💬
311H51AON23----[1] 113 💬
312Haemostasis tests----[1] 113 💬
313HB-adMSCs----[8] 2, 4, 6, 13, 14, 46, 49, 113 💬
314HIDROFEROL----[1] 113 💬
315Hidroferol®----[1] 113 💬
316HLA-identical allogeneic mesoangioblasts----[1] 113 💬
317HMABs----[1] 113 💬
318Hormonal profile----[1] 113 💬
319HT-100----[1] 113 💬
320Human Umbilical Cord Mesenchymal Stem Cells[1] Human Umbilical Cord Mesenchymal Stem Cells---[5] 13, 96, 97, 113, 271 💬
321Human Umbilical Cord Mesenchymal Stem Cells (UC-MSC)[1] Human Umbilical Cord Mesenchymal Stem Cells---[1] 113 💬
322Ibuprofen[1] Ibuprofen[5] Ibuprofen ,
Ibuprofen aluminum ,
Ibuprofen lysine ,
Ibuprofen sodium ,
Ibuprofen sodium 💬
[2] PTGS1,
PTGS2 💬
[23] Alzheimer disease, Arachidonic acid metabolism, C-type lectin receptor signaling pathway, Chemical carcinogenesis - DNA adducts, Efferocytosis, Human cytomegalovirus infection, Human papillomavirus infection, IL-17 signaling pathway, Kaposi sarcoma-associated herpesvirus infection, Leishmaniasis, MicroRNAs in cancer, NF-kappa B signaling pathway, Ovarian steroidogenesis, Oxytocin signaling pathway, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Platelet activation, Regulation of lipolysis in adipocytes, Retrograde endocannabinoid signaling, Serotonergic synapse, Small cell lung cancer, TNF signaling pathway, VEGF signaling pathway 💬[8] 13, 46, 65, 96, 107, 113, 271, 299 💬
323IBUPROFEN 200MG[1] Ibuprofen[5] Ibuprofen ,
Ibuprofen aluminum ,
Ibuprofen lysine ,
Ibuprofen sodium ,
Ibuprofen sodium 💬
[2] PTGS1,
PTGS2 💬
[23] Alzheimer disease, Arachidonic acid metabolism, C-type lectin receptor signaling pathway, Chemical carcinogenesis - DNA adducts, Efferocytosis, Human cytomegalovirus infection, Human papillomavirus infection, IL-17 signaling pathway, Kaposi sarcoma-associated herpesvirus infection, Leishmaniasis, MicroRNAs in cancer, NF-kappa B signaling pathway, Ovarian steroidogenesis, Oxytocin signaling pathway, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Platelet activation, Regulation of lipolysis in adipocytes, Retrograde endocannabinoid signaling, Serotonergic synapse, Small cell lung cancer, TNF signaling pathway, VEGF signaling pathway 💬[1] 113 💬
324Idebenone[1] Idebenone[1] Idebenone 💬 --[9] 6, 8, 13, 17, 18, 21, 113, 115, 302 💬
325Idebenone 150 mg film-coated tablets[1] Idebenone[1] Idebenone 💬 --[1] 113 💬
326Idefirix----[3] 43, 44, 113 💬
327Ifetroban[1] Ifetroban[2] Ifetroban ,
Ifetroban sodium 💬
[1] TBXA2R 💬 [3] Calcium signaling pathway, Neuroactive ligand-receptor interaction, Platelet activation 💬[4] 51, 85, 86, 113 💬
328IGF-1----[1] 113 💬
329Imlifidase[1] Imlifidase[1] Imlifidase 💬 --[4] 43, 44, 113, 221 💬
330Increased exercise intensity----[1] 113 💬
331Inflammatory profile----[1] 113 💬
332IONIS-DMPKRx----[1] 113 💬
333Isosorbide[1] Isosorbide[1] Isosorbide 💬 --[1] 113 💬
334ISOSORBIDE DINITRATE[2] Isosorbide,
Isosorbide dinitrate
[2] Isosorbide ,
Isosorbide dinitrate 💬
--[1] 113 💬
335Isosorbide Dinitrate 20 mg[2] Isosorbide,
Isosorbide dinitrate
[2] Isosorbide ,
Isosorbide dinitrate 💬
--[1] 113 💬
336Isosorbide Dinitrate 40 mg[2] Isosorbide,
Isosorbide dinitrate
[2] Isosorbide ,
Isosorbide dinitrate 💬
--[1] 113 💬
337Isosorbide Dinitrate 60 mg[2] Isosorbide,
Isosorbide dinitrate
[2] Isosorbide ,
Isosorbide dinitrate 💬
--[1] 113 💬
338Isosorbide Dinitrate 80 mg[2] Isosorbide,
Isosorbide dinitrate
[2] Isosorbide ,
Isosorbide dinitrate 💬
--[1] 113 💬
339ITF2357----[4] 96, 107, 113, 267 💬
340ITF2357 10 mg/mL----[1] 113 💬
341IV infusion----[1] 113 💬
342JWK007 Single intravenous infusion administration----[1] 113 💬
343KETAMINE[1] Ketamine[2] Ketamine hydrochloride ,
Ketamine 💬
[5] GRIN1,
GRIN2A,
GRIN2B,
GRIN2C,
GRIN2D 💬
[21] Alcoholism, Alzheimer disease, Amphetamine addiction, Amyotrophic lateral sclerosis, Calcium signaling pathway, Circadian entrainment, Cocaine addiction, Dopaminergic synapse, Glutamatergic synapse, Huntington disease, Long-term potentiation, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Nicotine addiction, Pathways of neurodegeneration - multiple diseases, Prion disease, Rap1 signaling pathway, Ras signaling pathway, Spinocerebellar ataxia, Systemic lupus erythematosus, cAMP signaling pathway 💬[6] 6, 13, 70, 113, 156, 215 💬
344L-arginine[2] Arginine,
L-arginine
[3] Arginine hydrochloride ,
Arginine ,
Arginine hydrochloride 💬
--[10] 2, 21, 46, 67, 96, 97, 98, 113, 223, 299 💬
345L-Citrulline and Metformin & L-Citrulline[2] Citrulline,
Metformin
[4] Metformin hydrochloride ,
Metformin ,
L-Citrulline ,
Citrulline malate 💬
[2] PRKAA1,
PRKAA2 💬
[20] AMPK signaling pathway, Adipocytokine signaling pathway, Alcoholic liver disease, Apelin signaling pathway, Autophagy - animal, Circadian rhythm, Fluid shear stress and atherosclerosis, FoxO signaling pathway, Glucagon signaling pathway, Hypertrophic cardiomyopathy, Insulin resistance, Insulin signaling pathway, Longevity regulating pathway, Longevity regulating pathway - multiple species, Non-alcoholic fatty liver disease, Oxytocin signaling pathway, PI3K-Akt signaling pathway, Thermogenesis, Tight junction, mTOR signaling pathway 💬[1] 113 💬
346L-Glutamine[1] L-Glutamine[1] Glutamine 💬 --[2] 113, 299 💬
347Lamotrigin actavis----[3] 113, 114, 115 💬
348Lamotrigine[1] Lamotrigine[1] Lamotrigine 💬 [6] SCN1A,
SCN2A,
SCN3A,
SCN5A,
SCN8A,
SCN9A 💬
[5] Adrenergic signaling in cardiomyocytes, Cadherin signaling, Dopaminergic synapse, IgSF CAM signaling, Taste transduction 💬[7] 13, 34, 38, 113, 114, 115, 144 💬
349LE051----[1] 113 💬
350Lentiviral Vector Trans-Skip gene modified Autologous Mesoangioblasts----[1] 113 💬
351Lisinopril[1] Lisinopril[2] Lisinopril ,
Lisinopril 💬
[1] ACE 💬 [6] Chagas disease, Coronavirus disease, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[9] 19, 46, 49, 57, 66, 67, 113, 222, 223 💬
352Lonafarnib[1] Lonafarnib[1] Lonafarnib 💬 [2] FNTA,
FNTB 💬
[1] Terpenoid backbone biosynthesis 💬[2] 113, 333 💬
353Losartan[1] Losartan[2] Losartan potassium ,
Losartan 💬
[1] AGTR1 💬 [17] AGE-RAGE signaling pathway in diabetic complications, Adrenergic signaling in cardiomyocytes, Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Coronavirus disease, Cortisol synthesis and secretion, Cushing syndrome, Diabetic cardiomyopathy, Hormone signaling, Neuroactive ligand-receptor interaction, Pathways in cancer, Phospholipase D signaling pathway, Renin secretion, Renin-angiotensin system, Vascular smooth muscle contraction, cGMP-PKG signaling pathway 💬[20] 17, 19, 36, 46, 57, 58, 66, 67, 85, 96, 97, 98, 113, 164, 167, 179, 215, 222, 223, 299 💬
354LOSMAPIMOD[1] Losmapimod[1] Losmapimod 💬 [4] MAPK11,
MAPK12,
MAPK13,
MAPK14 💬
[64] AGE-RAGE signaling pathway in diabetic complications, Adrenergic signaling in cardiomyocytes, Alcoholic liver disease, Amyotrophic lateral sclerosis, C-type lectin receptor signaling pathway, Cadherin signaling, Cellular senescence, Chagas disease, Chemical carcinogenesis - reactive oxygen species, Coronavirus disease, Diabetic cardiomyopathy, Dopaminergic synapse, Efferocytosis, Epithelial cell signaling in Helicobacter pylori infection, Epstein-Barr virus infection, Fc epsilon RI signaling pathway, Fluid shear stress and atherosclerosis, FoxO signaling pathway, GnRH signaling pathway, Growth hormone synthesis, secretion and action, Hepatitis B, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, IL-17 signaling pathway, IgSF CAM signaling, Inflammatory mediator regulation of TRP channels, Kaposi sarcoma-associated herpesvirus infection, Leishmaniasis, Leukocyte transendothelial migration, Lipid and atherosclerosis, MAPK signaling pathway, NOD-like receptor signaling pathway, Neurotrophin signaling pathway, Neutrophil extracellular trap formation, Non-alcoholic fatty liver disease, Oocyte meiosis, Osteoclast differentiation, PD-L1 expression and PD-1 checkpoint pathway in cancer, Pathogenic Escherichia coli infection, Pathways of neurodegeneration - multiple diseases, Pertussis, Platelet activation, Prion disease, Progesterone-mediated oocyte maturation, Prolactin signaling pathway, Proteoglycans in cancer, RIG-I-like receptor signaling pathway, Rap1 signaling pathway, Relaxin signaling pathway, Retrograde endocannabinoid signaling, Salmonella infection, Shigellosis, Signaling pathways regulating pluripotency of stem cells, Sphingolipid signaling pathway, T cell receptor signaling pathway, TNF signaling pathway, Th1 and Th2 cell differentiation, Th17 cell differentiation, Thermogenesis, Toll-like receptor signaling pathway, Toxoplasmosis, Tuberculosis, VEGF signaling pathway, Yersinia infection 💬[2] 113, 222 💬
355Lucen----[1] 113 💬
356MAGNESIO[1] Magnesium---[1] 113 💬
357Magnesium[1] Magnesium---[23] 3, 6, 11, 13, 15, 46, 64, 70, 71, 93, 97, 113, 166, 225, 234, 235, 256, 284, 291, 296, 297, 298, 340 💬
358Magnesium oxide[2] Magnesium,
Magnesium oxide
[1] Magnesium oxide 💬 --[4] 6, 113, 166, 291 💬
359Mannitol[1] Mannitol[1] Mannitol 💬 --[8] 6, 13, 21, 28, 60, 96, 113, 299 💬
360Metabolic profile----[1] 113 💬
361Metformin[1] Metformin[2] Metformin hydrochloride ,
Metformin 💬
[2] PRKAA1,
PRKAA2 💬
[20] AMPK signaling pathway, Adipocytokine signaling pathway, Alcoholic liver disease, Apelin signaling pathway, Autophagy - animal, Circadian rhythm, Fluid shear stress and atherosclerosis, FoxO signaling pathway, Glucagon signaling pathway, Hypertrophic cardiomyopathy, Insulin resistance, Insulin signaling pathway, Longevity regulating pathway, Longevity regulating pathway - multiple species, Non-alcoholic fatty liver disease, Oxytocin signaling pathway, PI3K-Akt signaling pathway, Thermogenesis, Tight junction, mTOR signaling pathway 💬[31] 2, 6, 8, 13, 46, 49, 60, 65, 66, 67, 74, 75, 77, 81, 84, 85, 86, 97, 113, 127, 158, 206, 218, 222, 225, 233, 265, 285, 298, 299, 301 💬
362Metformin 500mg[1] Metformin[2] Metformin hydrochloride ,
Metformin 💬
[2] PRKAA1,
PRKAA2 💬
[20] AMPK signaling pathway, Adipocytokine signaling pathway, Alcoholic liver disease, Apelin signaling pathway, Autophagy - animal, Circadian rhythm, Fluid shear stress and atherosclerosis, FoxO signaling pathway, Glucagon signaling pathway, Hypertrophic cardiomyopathy, Insulin resistance, Insulin signaling pathway, Longevity regulating pathway, Longevity regulating pathway - multiple species, Non-alcoholic fatty liver disease, Oxytocin signaling pathway, PI3K-Akt signaling pathway, Thermogenesis, Tight junction, mTOR signaling pathway 💬[1] 113 💬
363Metformin and Metformin & L-Citrulline[2] Citrulline,
Metformin
[4] Metformin hydrochloride ,
Metformin ,
L-Citrulline ,
Citrulline malate 💬
[2] PRKAA1,
PRKAA2 💬
[20] AMPK signaling pathway, Adipocytokine signaling pathway, Alcoholic liver disease, Apelin signaling pathway, Autophagy - animal, Circadian rhythm, Fluid shear stress and atherosclerosis, FoxO signaling pathway, Glucagon signaling pathway, Hypertrophic cardiomyopathy, Insulin resistance, Insulin signaling pathway, Longevity regulating pathway, Longevity regulating pathway - multiple species, Non-alcoholic fatty liver disease, Oxytocin signaling pathway, PI3K-Akt signaling pathway, Thermogenesis, Tight junction, mTOR signaling pathway 💬[1] 113 💬
364METFORMINA[1] Metformin[2] Metformin hydrochloride ,
Metformin 💬
[2] PRKAA1,
PRKAA2 💬
[20] AMPK signaling pathway, Adipocytokine signaling pathway, Alcoholic liver disease, Apelin signaling pathway, Autophagy - animal, Circadian rhythm, Fluid shear stress and atherosclerosis, FoxO signaling pathway, Glucagon signaling pathway, Hypertrophic cardiomyopathy, Insulin resistance, Insulin signaling pathway, Longevity regulating pathway, Longevity regulating pathway - multiple species, Non-alcoholic fatty liver disease, Oxytocin signaling pathway, PI3K-Akt signaling pathway, Thermogenesis, Tight junction, mTOR signaling pathway 💬[2] 67, 113 💬
365METFORMINA - 500 30 COMPRESSE 500 MG----[1] 113 💬
366Methylphenidate[1] Methylphenidate[2] Methylphenidate hydrochloride ,
Methylphenidate 💬
[2] SLC6A2,
SLC6A3 💬
[8] Alcoholism, Amphetamine addiction, Cocaine addiction, Dopaminergic synapse, Neuroactive ligand signaling, Parkinson disease, Pathways of neurodegeneration - multiple diseases, Synaptic vesicle cycle 💬[7] 6, 13, 34, 84, 113, 179, 206 💬
367MetoHEXAL® Succ ® 23,75 mg Retardtabletten----[1] 113 💬
368MetoHEXAL® Succ ® 47,5 mg Retardtabletten----[1] 113 💬
369MetoHEXAL® Succ ® 95 mg Retardtabletten----[1] 113 💬
370Metoprolol[1] Metoprolol[4] Metoprolol tartrate ,
Metoprolol succinate ,
Metoprolol ,
Metoprolol fumarate 💬
[1] ADRB1 💬 [13] Adrenergic signaling in cardiomyocytes, Calcium signaling pathway, Chemical carcinogenesis - receptor activation, Dilated cardiomyopathy, Gap junction, Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Regulation of lipolysis in adipocytes, Renin secretion, Salivary secretion, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[6] 17, 57, 58, 113, 193, 226 💬
371Metoprolol succinate[1] Metoprolol[4] Metoprolol tartrate ,
Metoprolol succinate ,
Metoprolol ,
Metoprolol fumarate 💬
[1] ADRB1 💬 [13] Adrenergic signaling in cardiomyocytes, Calcium signaling pathway, Chemical carcinogenesis - receptor activation, Dilated cardiomyopathy, Gap junction, Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Regulation of lipolysis in adipocytes, Renin secretion, Salivary secretion, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[4] 57, 58, 113, 193 💬
372Mexiletine[1] Mexiletine[2] Mexiletine hydrochloride ,
Mexiletine 💬
[6] SCN1A,
SCN2A,
SCN3A,
SCN5A,
SCN8A,
SCN9A 💬
[5] Adrenergic signaling in cardiomyocytes, Cadherin signaling, Dopaminergic synapse, IgSF CAM signaling, Taste transduction 💬[6] 1, 2, 10, 113, 114, 115 💬
373Mexiletine 167 mg[1] Mexiletine[2] Mexiletine hydrochloride ,
Mexiletine 💬
[6] SCN1A,
SCN2A,
SCN3A,
SCN5A,
SCN8A,
SCN9A 💬
[5] Adrenergic signaling in cardiomyocytes, Cadherin signaling, Dopaminergic synapse, IgSF CAM signaling, Taste transduction 💬[1] 113 💬
374Mexiletine granules for prolonged-release oral suspension[1] Mexiletine[2] Mexiletine hydrochloride ,
Mexiletine 💬
[6] SCN1A,
SCN2A,
SCN3A,
SCN5A,
SCN8A,
SCN9A 💬
[5] Adrenergic signaling in cardiomyocytes, Cadherin signaling, Dopaminergic synapse, IgSF CAM signaling, Taste transduction 💬[1] 113 💬
375MNK-1411----[1] 113 💬
376Monocytes and megacaryocytes culture and RNA extraction----[1] 113 💬
377Moxifloxacin[1] Moxifloxacin[3] Moxifloxacin hydrochloride ,
Moxifloxacin ,
Moxifloxacin hydrochloride monohydrate 💬
--[10] 2, 6, 46, 49, 85, 86, 113, 226, 240, 299 💬
378Moxifloxacin Hydrochloride[1] Moxifloxacin[3] Moxifloxacin hydrochloride ,
Moxifloxacin ,
Moxifloxacin hydrochloride monohydrate 💬
--[2] 113, 299 💬
379Mult-ingredient supplement----[1] 113 💬
380MYO-029----[1] 113 💬
381Myoblast autologous graft----[1] 113 💬
382Myoblast transplantation----[1] 113 💬
383Myoblastes autologues----[1] 113 💬
384MYODM----[1] 113 💬
385MyoPAXon----[1] 113 💬
386N(4,5Bis methanesulfonyl2methylbenzoyl) guanidine hydrochloride monohydrate[1] Guanidine[1] Guanidine hydrochloride 💬 --[1] 113 💬
387N-(4,5-Bis methanesulfonyl-2-methyl-benzoyl)guanidine hydrochloride monohydrate[1] Guanidine[1] Guanidine hydrochloride 💬 --[1] 113 💬
388Nanosuspension)----[1] 113 💬
389Nebivolol[1] Nebivolol[2] Nebivolol ,
Nebivolol hydrochloride 💬
[1] ADRB1 💬 [13] Adrenergic signaling in cardiomyocytes, Calcium signaling pathway, Chemical carcinogenesis - receptor activation, Dilated cardiomyopathy, Gap junction, Hormone signaling, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, Regulation of lipolysis in adipocytes, Renin secretion, Salivary secretion, cAMP signaling pathway, cGMP-PKG signaling pathway 💬[4] 17, 85, 113, 167 💬
390Needle biopsy of the vastus lateralis muscle----[1] 113 💬
391Nitrate[1] Nitrate[1] Nitric acid 💬 --[6] 57, 58, 67, 85, 113, 299 💬
392NPC-14----[1] 113 💬
393NS-050/NCNP-03----[1] 113 💬
394NS-065/NCNP-01----[1] 113 💬
395NS-089/NCNP-02----[1] 113 💬
396Nébivolol----[1] 113 💬
397Oligomero morfolino fosforodiamidato per skipping dell’esone 45----[1] 113 💬
398Oligomero morfolino fosforodiamidato per skipping dell’esone 53----[1] 113 💬
399Omigapil[1] Omigapil---[1] 113 💬
400Other: 6-minute walk test----[1] 113 💬
401Other: 9-hole test----[1] 113 💬
402Other: Balance measurement----[1] 113 💬
403Other: beetroot juice extract----[1] 113 💬
404Other: Blood sample----[37] 2, 11, 13, 34, 35, 41, 44, 46, 48, 49, 50, 51, 53, 58, 61, 63, 65, 84, 86, 96, 97, 113, 160, 162, 177, 222, 223, 227, 234, 238, 240, 256, 279, 299, 335, 340, 348 💬
405Other: Blood test----[11] 10, 19, 46, 51, 57, 65, 66, 83, 86, 96, 113 💬
406Other: Cardiac MRI with contrast----[1] 113 💬
407Other: Cardiac MRI without contrast----[1] 113 💬
408Other: Complete physical examination----[2] 111, 113 💬
409Other: Dystrophin levels----[1] 113 💬
410Other: Exercise Training----[1] 113 💬
411Other: Gait analysis via video capture----[2] 3, 113 💬
412Other: Genetic Testing----[1] 113 💬
413Other: GIP + GLP-2----[2] 3, 113 💬
414Other: Heart Rate----[1] 113 💬
415Other: Ibuprofen and Isosorbide Dinitrate combination[3] Ibuprofen,
Isosorbide,
Isosorbide dinitrate
[7] Ibuprofen ,
Isosorbide ,
Isosorbide dinitrate ,
Ibuprofen aluminum ,
Ibuprofen lysine ,
Ibuprofen sodium ,
Ibuprofen sodium 💬
[2] PTGS1,
PTGS2 💬
[23] Alzheimer disease, Arachidonic acid metabolism, C-type lectin receptor signaling pathway, Chemical carcinogenesis - DNA adducts, Efferocytosis, Human cytomegalovirus infection, Human papillomavirus infection, IL-17 signaling pathway, Kaposi sarcoma-associated herpesvirus infection, Leishmaniasis, MicroRNAs in cancer, NF-kappa B signaling pathway, Ovarian steroidogenesis, Oxytocin signaling pathway, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Platelet activation, Regulation of lipolysis in adipocytes, Retrograde endocannabinoid signaling, Serotonergic synapse, Small cell lung cancer, TNF signaling pathway, VEGF signaling pathway 💬[1] 113 💬
416Other: Meal test----[2] 3, 113 💬
417Other: Measurement of exercise-induced fatigue----[1] 113 💬
418Other: Motor Milestone Assessments----[2] 111, 113 💬
419Other: Moviplate----[1] 113 💬
420Other: Muscle Biopsy (Safety)----[1] 113 💬
421Other: MyoAnkle----[1] 113 💬
422Other: Oromotor function and nutrition----[2] 111, 113 💬
423Other: PAQ-C (Physical activitiy questionare for children), MoCA (Montreal Cognitive Assessment), PBS (Pediatric Balance Scale), Modified Mini Mental State Examination, BMI (Body Mass Index)----[1] 113 💬
424Other: Pulmonary Function Test----[1] 113 💬
425Other: Purdue board test----[1] 113 💬
426Other: Quantification of myotonia----[1] 113 💬
427Other: Repeat MRI scan----[1] 113 💬
428Other: Standard steroid treatment----[1] 113 💬
429Other: Test du Box and Blocks----[1] 113 💬
430Other: Ventilatory/ respiratory and other support assessment----[1] 113 💬
431Oxatomide[1] Oxatomide[1] Oxatomide 💬 [1] ALOX5 💬 [6] Arachidonic acid metabolism, Efferocytosis, Fc epsilon RI signaling pathway, Ovarian steroidogenesis, Serotonergic synapse, Toxoplasmosis 💬[1] 113 💬
432Oxatomide (tinset)[1] Oxatomide[1] Oxatomide 💬 [1] ALOX5 💬 [6] Arachidonic acid metabolism, Efferocytosis, Fc epsilon RI signaling pathway, Ovarian steroidogenesis, Serotonergic synapse, Toxoplasmosis 💬[1] 113 💬
433P-188 NF----[1] 113 💬
434PAMREVLUMAB[1] Pamrevlumab[1] Pamrevlumab 💬 [1] CCN2 💬 [2] Apelin signaling pathway, Hippo signaling pathway 💬[2] 85, 113 💬
435PB1046 Injection----[1] 113 💬
436PBGENE-DMD (IV)----[1] 113 💬
437PEMIROLAST[1] Pemirolast[2] Pemirolast potassium ,
Pemirolast 💬
--[1] 113 💬
438Pending----[7] 6, 13, 19, 96, 97, 113, 302 💬
439Pentoxifylline[1] Pentoxifylline[1] Pentoxifylline 💬 --[13] 6, 26, 46, 56, 84, 93, 96, 97, 113, 222, 223, 296, 298 💬
440Peptide-conjugated phosphorodiamidate morpholino oligomer for exon 51 skipping----[1] 113 💬
441Peptide-conjugated phosphorodiamide morpholino oligomer for exon 51 skipping----[1] 113 💬
442Perindopril[1] Perindopril[3] Perindopril erbumine ,
Perindopril ,
Perindopril arginine 💬
[1] ACE 💬 [6] Chagas disease, Coronavirus disease, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[5] 57, 58, 113, 167, 222 💬
443Perindopril 2mg Tablets[1] Perindopril[3] Perindopril erbumine ,
Perindopril ,
Perindopril arginine 💬
[1] ACE 💬 [6] Chagas disease, Coronavirus disease, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[1] 113 💬
444PF-06252616----[1] 113 💬
445PF-06939926----[1] 113 💬
446PGN-EDO51----[1] 113 💬
447PGN-EDODM1----[1] 113 💬
448PGN-EDODM1 for infusion----[1] 113 💬
449Phase 1, SQY51----[1] 113 💬
450Phase 2a, SQY51 (cohort 1)----[1] 113 💬
451Phase 2a, SQY51 (cohort 2)----[1] 113 💬
452Phase 2a, SQY51 (cohort 3)----[1] 113 💬
453Phosphorodiamidate Morpholino Oligomer----[1] 113 💬
454Phosphorodiamidate morpholino oligomer for exon 45 skipping----[1] 113 💬
455Phosphorodiamidate morpholino oligomer for exon 53 skipping----[1] 113 💬
456Pitolisant[1] Pitolisant[2] Pitolisant ,
Pitolisant hydrochloride 💬
[1] HRH3 💬 [2] Neuroactive ligand signaling, Neuroactive ligand-receptor interaction 💬[3] 6, 113, 193 💬
457Pitolisant Oral Tablet[1] Pitolisant[2] Pitolisant ,
Pitolisant hydrochloride 💬
[1] HRH3 💬 [2] Neuroactive ligand signaling, Neuroactive ligand-receptor interaction 💬[1] 113 💬
458Plasmapheresis----[4] 11, 49, 113, 222 💬
459Powder for Oral Suspension)----[1] 113 💬
460PRD2175434----[1] 113 💬
461PREDNISOLONE[1] Prednisolone[1] Prednisolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[48] 3, 11, 13, 14, 18, 25, 26, 35, 38, 39, 40, 41, 43, 44, 45, 46, 49, 50, 51, 54, 56, 57, 60, 61, 63, 64, 65, 66, 75, 81, 84, 85, 95, 96, 97, 107, 111, 113, 145, 162, 222, 223, 251, 269, 271, 296, 299, 300 💬
462Prednison----[4] 46, 84, 113, 300 💬
463Prednisone[1] Prednisone[1] Prednisone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[58] 2, 11, 13, 14, 18, 19, 26, 28, 35, 40, 41, 42, 43, 44, 45, 46, 48, 49, 50, 51, 53, 60, 61, 63, 64, 65, 66, 79, 81, 84, 85, 86, 90, 93, 95, 96, 97, 113, 127, 145, 162, 164, 205, 222, 223, 224, 228, 251, 269, 283, 284, 285, 288, 299, 300, 303, 307, 331 💬
464Prednisone 5 mg tablets[1] Prednisone[1] Prednisone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
465Primidone[1] Primidone[1] Primidone 💬 --[2] 2, 113 💬
466PRO044----[1] 113 💬
467PRO044 IV----[1] 113 💬
468PRO044 IV 6 mg/kg----[1] 113 💬
469PRO044 IV 9 mg/kg----[1] 113 💬
470PRO044 SC----[1] 113 💬
471PRO044 SC 6 mg/kg----[1] 113 💬
472PRO045----[1] 113 💬
473PRO045, 0.15 mg/kg/week----[1] 113 💬
474PRO045, 1.0 mg/kg/week----[1] 113 💬
475PRO045, 3.0 mg/kg/week----[1] 113 💬
476PRO045, 6.0 mg/kg/week----[1] 113 💬
477PRO045, 9.0 mg/kg/week----[1] 113 💬
478PRO045, selected dose----[1] 113 💬
479PRO051----[1] 113 💬
480PRO053----[1] 113 💬
481Protein-carbohydrate supplementation----[1] 113 💬
482PROVIGIL - 100 MG COMPRESSE 30 COMPRESSE----[1] 113 💬
483PS188----[1] 113 💬
484PS188 (company code)----[1] 113 💬
485PS220----[1] 113 💬
486PS524----[1] 113 💬
487PTC0161480, PTC124 Compound 1a, RPS2505, PTC-C124, 291844----[1] 113 💬
488PTC124----[4] 19, 113, 246, 299 💬
489RAAV1.CMV.huFollistatin344----[2] 15, 113 💬
490RAAV1.CMV.huFollistin344----[1] 113 💬
491RAAV2.5-CMV-minidystrophin (d3990)----[1] 113 💬
492RAAV8-hMD1----[1] 113 💬
493RAAV9-CK8-h-µD5----[1] 113 💬
494RAAV9-hFKRPco_miR-208a----[1] 113 💬
495RAAVrh74.MCK.GALGT2----[1] 113 💬
496RAAVrh74.MCK.micro-Dystrophin----[1] 113 💬
497RAG-18----[1] 113 💬
498Ramipril[1] Ramipril[1] Ramipril 💬 [1] ACE 💬 [6] Chagas disease, Coronavirus disease, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[10] 46, 49, 57, 66, 67, 113, 218, 222, 223, 257 💬
499Ranolazine[1] Ranolazine[2] Ranolazine ,
Ranolazine hydrochloride 💬
--[8] 2, 57, 58, 86, 96, 97, 113, 114 💬
500Raxone----[2] 113, 302 💬
501RAXONE - 150 MG- COMPRESSE RIVESTITE CON FILM- USO ORALE- FLACONE (HDPE)- 180 COMPRESSE----[1] 113 💬
502Recombinant human anti-GDF-8 antibody----[1] 113 💬
503Regimen Selection Phase Group 1 (COMPLETED)----[1] 113 💬
504Regimen Selection Phase Group 2----[1] 113 💬
505Regimen Selection Phase Group 3----[1] 113 💬
506Renadirsen[1] Renadirsen---[1] 113 💬
507Resveratrol[1] Resveratrol---[10] 2, 6, 8, 18, 46, 57, 89, 97, 113, 299 💬
508Revatio----[3] 85, 86, 113 💬
509RhIGF-I/rhIGFBP-3[1] rhIGFBP-3---[1] 113 💬
510RhIGFBP-3[1] rhIGFBP-3---[2] 113, 195 💬
511Ribitol[1] Ribitol[1] Ribitol 💬 --[1] 113 💬
512Rimeporide[1] Rimeporide---[1] 113 💬
513Risedronate[1] Risedronic acid[3] Risedronate sodium ,
Risedronic acid ,
Risedronate sodium monohydrate 💬
[1] FDPS 💬 [3] Human T-cell leukemia virus 1 infection, Influenza A, Terpenoid backbone biosynthesis 💬[2] 96, 113 💬
514Risedronate sodium[1] Risedronic acid[3] Risedronate sodium ,
Risedronic acid ,
Risedronate sodium monohydrate 💬
[1] FDPS 💬 [3] Human T-cell leukemia virus 1 infection, Influenza A, Terpenoid backbone biosynthesis 💬[5] 46, 50, 107, 113, 274 💬
515Rituxan treatment----[1] 113 💬
516RO720-4239/F01-01----[1] 113 💬
517RO7204239----[2] 3, 113 💬
518RO7239361----[1] 113 💬
519RO7239361 (BMS-986089)----[1] 113 💬
520RO7239361 Injections, 15 mg/Syringe (21.4 mg/mL)----[1] 113 💬
521RO7239361 Injections, 35 mg/Syringe (50 mg/mL)----[1] 113 💬
522RO7239361 Injections, 50 mg/Syringe (71.4 mg/mL)----[1] 113 💬
523RO7239361 Injections, 7.5 mg/Syringe (10.7 mg/mL)----[1] 113 💬
524RO7494222 (SRP-9001)----[1] 113 💬
525Saline injection----[1] 113 💬
526Sandimmun Optoral----[2] 53, 113 💬
527SAR446268----[1] 113 💬
528SAT-3247----[1] 113 💬
529SATRALIZUMAB[1] Satralizumab[1] Satralizumab 💬 [1] IL6R 💬 [11] Coronavirus disease, Cytokine-cytokine receptor interaction, HIF-1 signaling pathway, Hematopoietic cell lineage, Human cytomegalovirus infection, JAK-STAT signaling pathway, Non-alcoholic fatty liver disease, PI3K-Akt signaling pathway, Pathways in cancer, Th17 cell differentiation, Viral protein interaction with cytokine and cytokine receptor 💬[4] 11, 13, 86, 113 💬
530Satralizumab Prefilled Syringe[1] Satralizumab[1] Satralizumab 💬 [1] IL6R 💬 [11] Coronavirus disease, Cytokine-cytokine receptor interaction, HIF-1 signaling pathway, Hematopoietic cell lineage, Human cytomegalovirus infection, JAK-STAT signaling pathway, Non-alcoholic fatty liver disease, PI3K-Akt signaling pathway, Pathways in cancer, Th17 cell differentiation, Viral protein interaction with cytokine and cytokine receptor 💬[1] 113 💬
531ScAAV9.U7.ACCA----[1] 113 💬
532Semaglutide[1] Semaglutide[1] Semaglutide 💬 [1] GLP1R 💬 [4] Hormone signaling, Insulin secretion, Neuroactive ligand-receptor interaction, cAMP signaling pathway 💬[5] 6, 51, 84, 113, 299 💬
533Semaglutide (Rybelsus®)[1] Semaglutide[1] Semaglutide 💬 [1] GLP1R 💬 [4] Hormone signaling, Insulin secretion, Neuroactive ligand-receptor interaction, cAMP signaling pathway 💬[1] 113 💬
534Sevasemten[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
535Sevasemten 10 mg[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
536Sevasemten 12.5 mg[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
537Sevasemten 5 mg[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
538Sevasemten Dose 1[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
539Sevasemten Dose 2[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
540Sevasemten Dose 3[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
541Sevasemten Dose 4[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
542Sevasemten Dose 5[1] Sevasemten[1] Sevasemten 💬 [8] MYH1,
MYH13,
MYH15,
MYH2,
MYH3,
MYH4,
MYH7B,
MYH8 💬
[2] Cytoskeleton in muscle cells, Motor proteins 💬[1] 113 💬
543SGLT-2 inhibitor----[1] 113 💬
544SGLT2 inhibitor----[2] 113, 218 💬
545SGT-001----[1] 113 💬
546SGT-003----[1] 113 💬
547Sildenafil[1] Sildenafil[2] Sildenafil citrate ,
Sildenafil 💬
[1] PDE5A 💬 [2] Purine metabolism, cGMP-PKG signaling pathway 💬[17] 6, 46, 50, 51, 85, 86, 90, 113, 210, 211, 212, 225, 226, 278, 294, 299, 301 💬
548Sleep parameters----[1] 113 💬
549SMT C1100----[1] 113 💬
550SMT C1100 (F5----[1] 113 💬
551SMT C1100 (F5)----[1] 113 💬
552SMT C1100 (F6----[1] 113 💬
553SMT C1100 (F6)----[1] 113 💬
554SNT-MC17----[1] 113 💬
555Sodium Nitrate[2] Nitrate,
Sodium nitrate
[1] Nitric acid 💬 --[2] 58, 113 💬
556Sodium Nitrate - double dose[2] Nitrate,
Sodium nitrate
[1] Nitric acid 💬 --[1] 113 💬
557SomatoKine/IPLEX----[1] 113 💬
558Somatropin----[14] 3, 74, 75, 78, 97, 107, 113, 187, 193, 195, 222, 238, 274, 276 💬
559Spironolactone[1] Spironolactone[1] Spironolactone 💬 [1] NR3C2 💬 [1] Aldosterone-regulated sodium reabsorption 💬[12] 46, 57, 58, 67, 86, 113, 210, 214, 218, 222, 223, 225 💬
560SRD-001[1] SRD-001---[2] 57, 113 💬
561SRP-4045----[1] 113 💬
562SRP-4053----[1] 113 💬
563SRP-5051----[1] 113 💬
564SRP-6004[1] SRP-6004---[1] 113 💬
565SRP-9001----[1] 113 💬
566SRP-9003----[1] 113 💬
567SRP-9004----[1] 113 💬
568SRP-9005[1] SRP-9005---[1] 113 💬
569Standard of Care----[18] 6, 13, 49, 51, 57, 58, 63, 64, 79, 84, 96, 97, 113, 171, 223, 228, 240, 291 💬
570Stem Cell----[3] 2, 113, 296 💬
571Stem Cells----[4] 2, 4, 96, 113 💬
572Sunphenon----[2] 13, 113 💬
573Sunphenon EGCG----[3] 13, 17, 113 💬
574Sustanon (testosterone)[1] Testosterone[1] Testosterone 💬 [1] AR 💬 [4] Chemical carcinogenesis - receptor activation, Oocyte meiosis, Pathways in cancer, Prostate cancer 💬[1] 113 💬
575Sustanon 250----[1] 113 💬
576Suvodirsen[1] Suvodirsen---[1] 113 💬
577Synacthen Ampoules 250 mcg----[1] 113 💬
578Synacthen Ampoules 250 microgrammi----[1] 113 💬
579Tacrolimus[1] Tacrolimus[2] Tacrolimus ,
Tacrolimus 💬
[5] PPP3CA,
PPP3CB,
PPP3CC,
PPP3R1,
PPP3R2 💬
[33] Alzheimer disease, Amphetamine addiction, Amyotrophic lateral sclerosis, Axon guidance, B cell receptor signaling pathway, C-type lectin receptor signaling pathway, Calcium signaling pathway, Cellular senescence, Dopaminergic synapse, Glucagon signaling pathway, Glutamatergic synapse, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Kaposi sarcoma-associated herpesvirus infection, Lipid and atherosclerosis, Long-term potentiation, MAPK signaling pathway, Natural killer cell mediated cytotoxicity, Oocyte meiosis, Osteoclast differentiation, Oxytocin signaling pathway, PD-L1 expression and PD-1 checkpoint pathway in cancer, Pathways of neurodegeneration - multiple diseases, Prion disease, Renin secretion, T cell receptor signaling pathway, Th1 and Th2 cell differentiation, Th17 cell differentiation, Tuberculosis, VEGF signaling pathway, Wnt signaling pathway, cGMP-PKG signaling pathway 💬[37] 2, 6, 11, 13, 36, 46, 49, 50, 51, 53, 56, 57, 60, 61, 62, 63, 65, 66, 95, 96, 97, 113, 151, 158, 164, 222, 223, 224, 226, 227, 228, 234, 283, 284, 285, 286, 299 💬
580Tadalafil[1] Tadalafil[1] Tadalafil 💬 [1] PDE5A 💬 [2] Purine metabolism, cGMP-PKG signaling pathway 💬[8] 6, 51, 75, 77, 84, 86, 113, 210 💬
581Tadalafil 20 MG[1] Tadalafil[1] Tadalafil 💬 [1] PDE5A 💬 [2] Purine metabolism, cGMP-PKG signaling pathway 💬[1] 113 💬
582Tadalafil and Sildenafil[2] Sildenafil,
Tadalafil
[3] Tadalafil ,
Sildenafil citrate ,
Sildenafil 💬
[1] PDE5A 💬 [2] Purine metabolism, cGMP-PKG signaling pathway 💬[1] 113 💬
583Taking of blood----[1] 113 💬
584Talfirastide----[2] 57, 113 💬
585TAMOX----[1] 113 💬
586Tamoxifen[1] Tamoxifen[2] Tamoxifen citrate ,
Tamoxifen 💬
[2] ESR1,
ESR2 💬
[10] Breast cancer, Chemical carcinogenesis - receptor activation, Endocrine and other factor-regulated calcium reabsorption, Estrogen signaling pathway, GnRH secretion, Hormone signaling, Pathways in cancer, Prolactin signaling pathway, Proteoglycans in cancer, Thyroid hormone signaling pathway 💬[6] 2, 65, 86, 113, 227, 299 💬
587Tamoxifen 20mg Hexal® Filmtabletten[1] Tamoxifen[2] Tamoxifen citrate ,
Tamoxifen 💬
[2] ESR1,
ESR2 💬
[10] Breast cancer, Chemical carcinogenesis - receptor activation, Endocrine and other factor-regulated calcium reabsorption, Estrogen signaling pathway, GnRH secretion, Hormone signaling, Pathways in cancer, Prolactin signaling pathway, Proteoglycans in cancer, Thyroid hormone signaling pathway 💬[1] 113 💬
588TAMOXIFEN CITRATE[1] Tamoxifen[2] Tamoxifen citrate ,
Tamoxifen 💬
[2] ESR1,
ESR2 💬
[10] Breast cancer, Chemical carcinogenesis - receptor activation, Endocrine and other factor-regulated calcium reabsorption, Estrogen signaling pathway, GnRH secretion, Hormone signaling, Pathways in cancer, Prolactin signaling pathway, Proteoglycans in cancer, Thyroid hormone signaling pathway 💬[1] 113 💬
589TAS-205----[1] 113 💬
590TAS-205 [Ambulatory Cohort] [Non-ambulatory Cohort]----[1] 113 💬
591Tehalose 30gr----[1] 113 💬
592Temerit----[1] 113 💬
593Testosterone[1] Testosterone[1] Testosterone 💬 [1] AR 💬 [4] Chemical carcinogenesis - receptor activation, Oocyte meiosis, Pathways in cancer, Prostate cancer 💬[9] 1, 2, 3, 13, 60, 76, 78, 113, 265 💬
594Testosterone decanoate[2] Testosterone,
Testosterone decanoate
[2] Testosterone ,
Testosterone decanoate 💬
[1] AR 💬 [4] Chemical carcinogenesis - receptor activation, Oocyte meiosis, Pathways in cancer, Prostate cancer 💬[1] 113 💬
595Testosterone Enanthate[2] Testosterone,
Testosterone enanthate
[2] Testosterone ,
Testosterone enanthate 💬
[1] AR 💬 [4] Chemical carcinogenesis - receptor activation, Oocyte meiosis, Pathways in cancer, Prostate cancer 💬[1] 113 💬
596Testosterone isocaproate[2] Testosterone,
Testosterone isocaproate
[1] Testosterone 💬 [1] AR 💬 [4] Chemical carcinogenesis - receptor activation, Oocyte meiosis, Pathways in cancer, Prostate cancer 💬[1] 113 💬
597Testosterone phenylpropionate[2] Testosterone,
Testosterone phenylpropionate
[2] Testosterone ,
Testosterone phenylpropionate 💬
[1] AR 💬 [4] Chemical carcinogenesis - receptor activation, Oocyte meiosis, Pathways in cancer, Prostate cancer 💬[1] 113 💬
598Testosterone propionate[2] Testosterone,
Testosterone propionate
[2] Testosterone ,
Testosterone propionate 💬
[1] AR 💬 [4] Chemical carcinogenesis - receptor activation, Oocyte meiosis, Pathways in cancer, Prostate cancer 💬[1] 113 💬
599Tetracosactide[1] Tetracosactide[2] Cosyntropin ,
Tetracosactide acetate 💬
[1] MC2R 💬 [6] Aldosterone synthesis and secretion, Cortisol synthesis and secretion, Cushing syndrome, Hormone signaling, Neuroactive ligand-receptor interaction, cAMP signaling pathway 💬[4] 83, 113, 145, 222 💬
600TETRACOSACTIDE ESACETATO[1] Tetracosactide[2] Cosyntropin ,
Tetracosactide acetate 💬
[1] MC2R 💬 [6] Aldosterone synthesis and secretion, Cortisol synthesis and secretion, Cushing syndrome, Hormone signaling, Neuroactive ligand-receptor interaction, cAMP signaling pathway 💬[1] 113 💬
601TETRACOSACTIDE HEXAACETATE[1] Tetracosactide[2] Cosyntropin ,
Tetracosactide acetate 💬
[1] MC2R 💬 [6] Aldosterone synthesis and secretion, Cortisol synthesis and secretion, Cushing syndrome, Hormone signaling, Neuroactive ligand-receptor interaction, cAMP signaling pathway 💬[1] 113 💬
602Tideglusib[1] Tideglusib---[3] 2, 5, 113 💬
603To be determined----[2] 96, 113 💬
604Tranilast[1] Tranilast[1] Tranilast 💬 --[4] 46, 84, 106, 113 💬
605Translarna----[1] 113 💬
606Translarna 1000 mg granules for oral suspension----[1] 113 💬
607Translarna 125 mg granules for oral suspension----[1] 113 💬
608Translarna 250 mg granules for oral suspension----[1] 113 💬
609Treatment Phase Group 4----[1] 113 💬
610Treatment taken----[1] 113 💬
611Trehalose[1] Trehalose---[4] 2, 6, 18, 113 💬
612TRIATEC----[1] 113 💬
613ULSC----[1] 113 💬
614Umbilical cord mesenchymal stem cell----[2] 18, 113 💬
615Umbilical cord mesenchymal stem cells----[5] 13, 46, 57, 97, 113 💬
616Vamarolone----[1] 113 💬
617Vamorolone[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[2] 97, 113 💬
618Vamorolone 0.25 mg/day/day[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
619Vamorolone 0.25 mg/kg/day[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
620Vamorolone 0.75 mg/day/day[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
621Vamorolone 0.75 mg/kg/day[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
622Vamorolone 2.0 mg/day/day[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
623Vamorolone 2.0 mg/kg/day[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
624Vamorolone 40 mg/mL oral suspension[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
625Vamorolone 6.0 mg/day/day[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
626Vamorolone 6.0 mg/kg/day[1] Vamorolone[1] Vamorolone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 113 💬
627VBP15----[1] 113 💬
628Vesleteplirsen[1] Vesleteplirsen---[1] 113 💬
629Viltepso----[1] 113 💬
630VILTOLARSEN[1] Viltolarsen[1] Viltolarsen 💬 [1] DMD 💬 [5] Arrhythmogenic right ventricular cardiomyopathy, Cytoskeleton in muscle cells, Dilated cardiomyopathy, Hypertrophic cardiomyopathy, Viral myocarditis 💬[1] 113 💬
631Vit C Vit E Zn Se----[1] 113 💬
632VX-670----[1] 113 💬
633Vyondys 53----[1] 113 💬
634WVE-210201----[1] 113 💬
635WVE-210201 (suvodirsen)[1] Suvodirsen---[1] 113 💬
636WVE-N531[1] WVE-N531---[1] 113 💬
637Xeomin----[7] 5, 6, 7, 13, 15, 17, 113 💬
638Yeast[1] Yeast[1] Dried yeast 💬 --[2] 97, 113 💬
639Zeleciment basivarsen (DYNE-101)----[1] 113 💬
640Zeleciment Rostudirsen (DYNE-251)[1] DYNE-251---[1] 113 💬