205. 脆弱X症候群関連疾患 Disease details / Clinical trials / Drug dev / DR info
臨床試験数 : 5 / 薬物数 : 11 - (DrugBank : 7) / 標的遺伝子数 : 25 - 標的パスウェイ数 : 31
薬物、開発者(Primary Sponsor)、臨床試験情報(症例登録開始年(Enrollment year)、フェーズ、ID、実施国)
Allopregnanolone
Randi J. Hagerman, MD
2015 Phase 2 NCT02603926 United States
Citocoline
Rush University Medical Center
2015 Phase 2 NCT02197104 United States
Clinical observation
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Corticotropin-releasing hormone
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Cyclophosphamide
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Laboratory biomarker analysis
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Magnetic resonance imaging
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Memantine
University of California, Davis
2007 - NCT00584948 United States
Prednisone
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Sulforaphane
University of California, Davis
2021 - NCT05233579 United States
Therapeutic immune globulin
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Randi J. Hagerman, MD
2015 Phase 2 NCT02603926 United States
Citocoline
Rush University Medical Center
2015 Phase 2 NCT02197104 United States
Clinical observation
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Corticotropin-releasing hormone
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Cyclophosphamide
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Laboratory biomarker analysis
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Magnetic resonance imaging
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Memantine
University of California, Davis
2007 - NCT00584948 United States
Prednisone
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Sulforaphane
University of California, Davis
2021 - NCT05233579 United States
Therapeutic immune globulin
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States