324. メチルグルタコン酸尿症 Disease details / Clinical trials / Drug dev / DR info

臨床試験数 : 6 / 薬物数 : 10 - (DrugBank : 3) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 10

薬物、開発者（Primary Sponsor）、臨床試験情報（症例登録開始年（Enrollment year）、フェーズ、ID、実施国）
Bezafibrate
   University Hospitals Bristol NHS Foundation Trust
      2019   Phase 2   EUCTR2015-001382-10-GB   United Kingdom
Elamipretide
   Stealth BioTherapeutics Inc.
      2026   Phase 4   NCT07531251   United Kingdom;United States
      2021   -   NCT04689360   -
      2017   Phase 2/Phase 3   NCT03098797   United States
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
   West Kazakhstan Medical University
      2022   -   NCT05910151   Kazakhstan
Triheptanoin
   Jerry Vockley, MD, PhD
      2009   -   NCT01461304   United States