158. Tuberous sclerosis Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 129 / Drugs : 56 - (DrugBank : 20) / Drug target genes : 35 - Drug target pathways : 116
| Other names | Tuberous sclerosis complex;TSC; | ||
|---|---|---|---|
| Disease group | Neuromuscular diseases | ||
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Domestic patients
Med expenses recipients (FY2023) |
1,092 patients Age distribution
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| Related info (in Japanese) | |||
| Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 11-7-18. tuberous sclerosis complex; TSC | ||
| Subtypes | - | ||

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