158. Tuberous sclerosis Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 112 / Drugs : 71 - (DrugBank : 19) / Drug target genes : 35 - Drug target pathways : 118
Other names | Tuberous sclerosis complex; | ||
---|---|---|---|
Disease group | Neuromuscular diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
1,092 patients Age distribution
![]() |
||
Related info (in Japanese) | |||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | 11-6-16. tuberous sclerosis complex; TSC | ||
Subtypes | - |