169. Menkes disease Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 7 Drugs : 7 - (DrugBank : 4) / Drug target genes : 9 - Drug target pathways : 16

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Copper
   Hamamatsu University School of Medicine
      2014   -   JPRN-UMIN000030626   Japan
   Kobe Unniversitu Graduate School of Medicine
      2011   -   JPRN-UMIN000005259   Japan
Copper histidinate
   Sentynl Therapeutics, Inc.
      2019   -   NCT04074512   -
Copper histidine
   Cyprium Therapeutics, Inc.
      2009   Phase 3   NCT00811785   United States
   Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
      1990   Phase 1/Phase 2   NCT00001262   United States
Diethyldithiocarbamate
   Kobe Unniversitu Graduate School of Medicine
      2011   -   JPRN-UMIN000005259   Japan
Droxidopa
   Stephen G. Kaler, MD
      2021   Phase 1/Phase 2   NCT04977388   United States
Histidine
   Hamamatsu University School of Medicine
      2014   -   JPRN-UMIN000030626   Japan
   Kobe Unniversitu Graduate School of Medicine
      2011   -   JPRN-UMIN000005259   Japan
Long term follow-UP
   Cyprium Therapeutics, Inc.
      2019   -   NCT04337684   United States