201. Angelman syndrome Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 40 / Drugs : 48 - (DrugBank : 11) / Drug target genes : 22 - Drug target pathways : 22
| Other names | - | ||
|---|---|---|---|
| Disease group | Neuromuscular diseases | ||
|
Domestic patients
Med expenses recipients, FY2024 (corrected) (in Japanese) |
38 patients Age distribution
|
||
| Clinical research form (in Japanese) MHLW Intractable Diseases, FY2026 (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 13-1-9. Angelman syndrome | ||
| Sub-diseases (Clinical research forms may not be available for all sub-diseases.) | - | ||
