205. Fragile X syndrome related disease Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 5 / Drugs : 11 - (DrugBank : 7) / Drug target genes : 25 - Drug target pathways : 31
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Allopregnanolone
Randi J. Hagerman, MD
2015 Phase 2 NCT02603926 United States
Citocoline
Rush University Medical Center
2015 Phase 2 NCT02197104 United States
Clinical observation
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Corticotropin-releasing hormone
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Cyclophosphamide
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Laboratory biomarker analysis
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Magnetic resonance imaging
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Memantine
University of California, Davis
2007 - NCT00584948 United States
Prednisone
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Sulforaphane
University of California, Davis
2021 - NCT05233579 United States
Therapeutic immune globulin
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Randi J. Hagerman, MD
2015 Phase 2 NCT02603926 United States
Citocoline
Rush University Medical Center
2015 Phase 2 NCT02197104 United States
Clinical observation
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Corticotropin-releasing hormone
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Cyclophosphamide
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Laboratory biomarker analysis
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Magnetic resonance imaging
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Memantine
University of California, Davis
2007 - NCT00584948 United States
Prednisone
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Sulforaphane
University of California, Davis
2021 - NCT05233579 United States
Therapeutic immune globulin
Children's Oncology Group
2004 Phase 3 NCT00033293 Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States