205. Fragile X syndrome related disease Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 5 Drugs : 11 - (DrugBank : 7) / Drug target genes : 25 - Drug target pathways : 31

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Allopregnanolone
   Randi J. Hagerman, MD
      2015   Phase 2   NCT02603926   United States
Citocoline
   Rush University Medical Center
      2015   Phase 2   NCT02197104   United States
Clinical observation
   Children's Oncology Group
      2004   Phase 3   NCT00033293   Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Corticotropin-releasing hormone
   Children's Oncology Group
      2004   Phase 3   NCT00033293   Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Cyclophosphamide
   Children's Oncology Group
      2004   Phase 3   NCT00033293   Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Laboratory biomarker analysis
   Children's Oncology Group
      2004   Phase 3   NCT00033293   Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Magnetic resonance imaging
   Children's Oncology Group
      2004   Phase 3   NCT00033293   Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Memantine
   University of California, Davis
      2007   -   NCT00584948   United States
Prednisone
   Children's Oncology Group
      2004   Phase 3   NCT00033293   Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States
Sulforaphane
   University of California, Davis
      2021   -   NCT05233579   United States
Therapeutic immune globulin
   Children's Oncology Group
      2004   Phase 3   NCT00033293   Australia;Canada;Netherlands;New Zealand;Puerto Rico;Switzerland;United States