233. Wolfram syndrome Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 11 / Drugs : 17 - (DrugBank : 8) / Drug target genes : 12 - Drug target pathways : 41
Other names | Diabetes Insipidus, Diabetes mellitus, optic atrophy, and deafness syndrome;DIDMOAD syndrome; | ||
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Disease group | Endocrine diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
16 patients Age distribution
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Related info (in Japanese) | - | ||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | 7-1-7. Other diabetes mellitus | ||
Subtypes | - |