260. Sitosterolemia Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 12 / Drugs : 11 - (DrugBank : 3) / Drug target gene : 1 - Drug target pathway : 1
Other names | - | ||
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Disease group | Metabolic diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
19 patients Age distribution
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Related info (in Japanese) | - | ||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | 8-12-134. Other disorder of lipid metabolism | ||
Subtypes | - |