307. Canavan disease Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 6 / Drugs : 11 - (DrugBank : 5) / Drug target genes : 2 - Drug target pathways : 2
Other names | - | ||
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Disease group | Neuromuscular diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
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Related info (in Japanese) | - | ||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | 11-8-24. Canavan disease | ||
Subtypes | - |