307. Canavan disease Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 6 Drugs : 8 - (DrugBank : 4) / Drug target genes : 2 - Drug target pathways : 2

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
AAV9 BBP-812
   Aspa Therapeutics
      2021   Phase 1/Phase 2   NCT04998396   United States
Glyceryl triacetate
   Assistance Publique - Hôpitaux de Paris
      2009   Phase 2   NCT00657748   France
GTA glyceryl triacetate
   Shaare Zedek Medical Center
      2008   -   NCT00724802   Israel
GTA: glyceryltriacetate
   Sheba Medical Center
      2006   Phase 1   NCT00278707   Israel
Levetiracetam
   Myrtelle Inc.
      2021   Phase 1/Phase 2   NCT04833907   United States
Prednisone
   Myrtelle Inc.
      2021   Phase 1/Phase 2   NCT04833907   United States
RAAV-OLIG001-aspa
   Myrtelle Inc.
      2021   Phase 1/Phase 2   NCT04833907   United States
RAAV9-CB6-aspa
   University of Florida
      2022   -   NCT05317780   United States