316. Carnitine cycle disorder Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 4 / Drugs : 12 - (DrugBank : 2) / Drug target genes : 2 - Drug target pathways : 11
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Bezafibrate
Assistance Publique - Hôpitaux de Paris
2006 Phase 3 NCT00336167 France
Rigshospitalet, Denmark
2009 Phase 2 NCT00983788 Denmark
Glycerol/saline
Oregon Health and Science University
2016 - NCT02517307 United States
Hyperinsulinemic euglycemic clamp
Oregon Health and Science University
2016 - NCT02517307 United States
Intralipid/heparin
Oregon Health and Science University
2016 - NCT02517307 United States
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Assistance Publique - Hôpitaux de Paris
2006 Phase 3 NCT00336167 France
Rigshospitalet, Denmark
2009 Phase 2 NCT00983788 Denmark
Glycerol/saline
Oregon Health and Science University
2016 - NCT02517307 United States
Hyperinsulinemic euglycemic clamp
Oregon Health and Science University
2016 - NCT02517307 United States
Intralipid/heparin
Oregon Health and Science University
2016 - NCT02517307 United States
Obtaining DRY blood spots from healthy children aged 8 days - 7 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
Obtaining DRY blood spots from healthy children aged 8-18 years
West Kazakhstan Medical University
2022 - NCT05910151 Kazakhstan
