333. Hutchinson-Gilford syndrome Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 9 / Drugs : 7 - (DrugBank : 4) / Drug target genes : 4 - Drug target pathways : 5
| Other names | Hutchinson-Gilford progeria syndrome;HGPS; | ||
|---|---|---|---|
| Disease group | Chromosomal and gene abnormalities | ||
|
Domestic patients
Med expenses recipients (FY2023) |
- |
||
| Related info (in Japanese) | - | ||
| Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 11-8-25. Hutchinson-Gilford syndrome; Hutchinson-Gilford progeria syndrome; HGPS | ||
| Subtypes | - | ||
