333. Hutchinson-Gilford syndrome Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 9 Drugs : 7 - (DrugBank : 4) / Drug target genes : 4 - Drug target pathways : 5

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Lonafarnib
   Boston Children's Hospital
      2009   Phase 2   NCT00879034   United States
   Eiger BioPharmaceuticals
      2020   -   NCT03895528   -
   Monica E. Kleinman
      2007   Phase 2   NCT00425607   United States
   PRG Science & Technology Co., Ltd.
      2025   Phase 2   NCT06775041   United States
   The Children's Hospital Zhejiang University School of Medicine
      2021   -   ChiCTR2100050052   China
Lonafarnib, zoledronic acid, and pravastatin
   Boston Children's Hospital
      2009   Phase 2   NCT00916747   United States
Pravastatin
   Boston Children's Hospital
      2009   Phase 2   NCT00879034   United States
Progerinin
   PRG Science & Technology Co., Ltd.
      2025   Phase 2   NCT06775041   United States
      2020   Phase 1   NCT04512963   United States
Umbilical cord blood unit
   Bundang CHA Hospital
      2019   Phase 1/Phase 2   NCT03871972   Korea, Republic of
Zoledronic acid
   Boston Children's Hospital
      2009   Phase 2   NCT00879034   United States
Zoledronic acid, pravastatin
   Assistance Publique Hopitaux De Marseille
      2008   Phase 2   NCT00731016   France