333. Hutchinson-Gilford syndrome Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 9 / Drugs : 7 - (DrugBank : 4) / Drug target genes : 4 - Drug target pathways : 5
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Lonafarnib
Boston Children's Hospital
2009 Phase 2 NCT00879034 United States
Eiger BioPharmaceuticals
2020 - NCT03895528 -
Monica E. Kleinman
2007 Phase 2 NCT00425607 United States
PRG Science & Technology Co., Ltd.
2025 Phase 2 NCT06775041 United States
The Children's Hospital Zhejiang University School of Medicine
2021 - ChiCTR2100050052 China
Lonafarnib, zoledronic acid, and pravastatin
Boston Children's Hospital
2009 Phase 2 NCT00916747 United States
Pravastatin
Boston Children's Hospital
2009 Phase 2 NCT00879034 United States
Progerinin
PRG Science & Technology Co., Ltd.
2025 Phase 2 NCT06775041 United States
2020 Phase 1 NCT04512963 United States
Umbilical cord blood unit
Bundang CHA Hospital
2019 Phase 1/Phase 2 NCT03871972 Korea, Republic of
Zoledronic acid
Boston Children's Hospital
2009 Phase 2 NCT00879034 United States
Zoledronic acid, pravastatin
Assistance Publique Hopitaux De Marseille
2008 Phase 2 NCT00731016 France
Boston Children's Hospital
2009 Phase 2 NCT00879034 United States
Eiger BioPharmaceuticals
2020 - NCT03895528 -
Monica E. Kleinman
2007 Phase 2 NCT00425607 United States
PRG Science & Technology Co., Ltd.
2025 Phase 2 NCT06775041 United States
The Children's Hospital Zhejiang University School of Medicine
2021 - ChiCTR2100050052 China
Lonafarnib, zoledronic acid, and pravastatin
Boston Children's Hospital
2009 Phase 2 NCT00916747 United States
Pravastatin
Boston Children's Hospital
2009 Phase 2 NCT00879034 United States
Progerinin
PRG Science & Technology Co., Ltd.
2025 Phase 2 NCT06775041 United States
2020 Phase 1 NCT04512963 United States
Umbilical cord blood unit
Bundang CHA Hospital
2019 Phase 1/Phase 2 NCT03871972 Korea, Republic of
Zoledronic acid
Boston Children's Hospital
2009 Phase 2 NCT00879034 United States
Zoledronic acid, pravastatin
Assistance Publique Hopitaux De Marseille
2008 Phase 2 NCT00731016 France