344. Very long-chain acyl-CoA dehydrogenase deficiency Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 6 / Drugs : 10 - (DrugBank : 2) / Drug target gene : 1 - Drug target pathways : 10
Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
Bezafibrate
Rigshospitalet, Denmark
2009 Phase 2 NCT00983788 Denmark
Exercise
University Medical Center Groningen
2016 - NCT03531554 Netherlands
Glycerol/saline
Oregon Health and Science University
2016 - NCT02517307 United States
Hyperinsulinemic euglycemic clamp
Oregon Health and Science University
2016 - NCT02517307 United States
Intralipid/heparin
Oregon Health and Science University
2016 - NCT02517307 United States
Ketone ester drink
University Medical Center Groningen
2016 - NCT03531554 Netherlands
Magnetic resonance imaging
University Medical Center Groningen
2016 - NCT03531554 Netherlands
Muscle biopsy
University Medical Center Groningen
2016 - NCT03531554 Netherlands
Nutritional ketone supplement
Oregon Health and Science University
2022 Early Phase 1 NCT05411835 United States
UX007
Ultragenyx Pharmaceutical Inc
2014 Phase 2 NCT02214160 United Kingdom;United States
2014 Phase 2 NCT01886378 United Kingdom;United States
Rigshospitalet, Denmark
2009 Phase 2 NCT00983788 Denmark
Exercise
University Medical Center Groningen
2016 - NCT03531554 Netherlands
Glycerol/saline
Oregon Health and Science University
2016 - NCT02517307 United States
Hyperinsulinemic euglycemic clamp
Oregon Health and Science University
2016 - NCT02517307 United States
Intralipid/heparin
Oregon Health and Science University
2016 - NCT02517307 United States
Ketone ester drink
University Medical Center Groningen
2016 - NCT03531554 Netherlands
Magnetic resonance imaging
University Medical Center Groningen
2016 - NCT03531554 Netherlands
Muscle biopsy
University Medical Center Groningen
2016 - NCT03531554 Netherlands
Nutritional ketone supplement
Oregon Health and Science University
2022 Early Phase 1 NCT05411835 United States
UX007
Ultragenyx Pharmaceutical Inc
2014 Phase 2 NCT02214160 United Kingdom;United States
2014 Phase 2 NCT01886378 United Kingdom;United States