344. Very long-chain acyl-CoA dehydrogenase deficiency Disease details / Clinical trials / Drug dev / DR info /
Clinical trials : 6 / Drugs : 10 - (DrugBank : 2) / Drug target gene : 1 - Drug target pathways : 10
Other names | Very long-chain acyl-coenzyme A dehydrogenase deficiency;Very-long-chain acyl-CoA dehydrogenase (VLCAD) deficiency;VLCAD deficiency;VLCADD; | ||
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Disease group | Metabolic diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
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Related info (in Japanese) | - | ||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | 8-3-44. Very-long-chain acyl-CoA dehydrogenase (VLCAD) deficiency | ||
Subtypes | - |