MIGLUSTAT

( DrugBank: Miglustat / KEGG DRUG: Miglustat )


3 diseases
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease23
256Muscle glycogenosis35
IDDisease name (Link within this page)Number of trials
299Cystic fibrosis6

19. Lysosomal storage disease


Clinical trials : 1,038 / Drugs : 873 - (DrugBank : 121) / Drug target genes : 63 - Drug target pathways : 195 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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agemin
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256. Muscle glycogenosis


Clinical trials : 204 / Drugs : 153 - (DrugBank : 29) / Drug target genes : 19 - Drug target pathways : 59 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries

299. Cystic fibrosis


Clinical trials : 1,885 / Drugs : 1,782 - (DrugBank : 252) / Drug target genes : 110 - Drug target pathways : 190 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries