Drug Description in Trials / DrugBank / KEGG DRUG

  

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No. Drug (Description in trials) DrugBank KEGG DRUG KEGG GENES KEGG PATHWAY Disease ID
11- deoxygalactonojirimycin----[1] 19 💬
21-deoxygalactonojirimycin hydrochloride[1] Migalastat[2] Migalastat hydrochloride ,
Migalastat 💬 		[1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
312 lead electrocardiogram----[1] 19 💬
412S-IT----[1] 19 💬
515-0 H20----[2] 6, 19 💬
61629063-78-0----[1] 19 💬
72(S)-(acetylamino)-4-methylpentanoic acid----[2] 19, 65 💬
82-aminoethanethiol[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[2] 19, 299 💬
92-hour holter monitor----[1] 19 💬
102-hydroxypropyl-BETA-cyclodextrin[1] Hydroxypropyl betadex---[1] 19 💬
1126 common fabry mutation types IN taiwan----[1] 19 💬
124D-310[1] 4D-310---[1] 19 💬
13500 0500 0----[1] 19 💬
1468GA-dotatate PET/MRI[1] Dotatate gallium Ga-68[1] Edotreotide gallium Ga-68 💬 [1] SSTR2 💬 [5] Gastric acid secretion, Growth hormone synthesis, secretion and action, Hormone signaling, Neuroactive ligand-receptor interaction, cAMP signaling pathway 💬[1] 19 💬
1589ZR-SBC-103[1] Lesinidase alfa[1] Lesinidase alfa 💬 [1] NAGLU 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
16A16ax06----[1] 19 💬
17AAV2/8.TBG.harsb----[1] 19 💬
18AAV9-CAG-COH-sgsh----[1] 19 💬
19AAV9-GLB1----[1] 19 💬
20Aavrh.10-hmpsiiia----[1] 19 💬
21Aavrh.10cuarsa----[1] 19 💬
22Aavrh.10cucln2----[1] 19 💬
23Aavrh.10cuhcln2 vector 2.85x10^11 genome copies----[1] 19 💬
24Aavrh.10cuhcln2 vector 9.0x10^11 genome copies----[1] 19 💬
25Abatacept[1] Abatacept[1] Abatacept 💬 [2] CD80,
CD86 💬 		[13] Allograft rejection, Autoimmune thyroid disease, Cell adhesion molecules, Graft-versus-host disease, Intestinal immune network for IgA production, Kaposi sarcoma-associated herpesvirus infection, Rheumatoid arthritis, Systemic lupus erythematosus, Toll-like receptor signaling pathway, Transcriptional misregulation in cancer, Type I diabetes mellitus, Viral myocarditis, Virion - Adenovirus 💬[26] 2, 13, 19, 41, 44, 46, 49, 50, 51, 53, 55, 60, 65, 84, 93, 95, 96, 97, 107, 160, 164, 222, 271, 284, 285, 300 💬
26Abcertin----[1] 19 💬
27Abdominal ultrasound----[2] 19, 231 💬
28ABO-101----[2] 19, 234 💬
29ABO-102[1] Rebisufligene etisparvovec---[1] 19 💬
30Accupro----[1] 19 💬
31Accuretic----[1] 19 💬
32Acetaminophen[1] Acetaminophen[1] Acetaminophen 💬 [2] PTGS1,
PTGS2 💬 		[23] Alzheimer disease, Arachidonic acid metabolism, C-type lectin receptor signaling pathway, Chemical carcinogenesis - DNA adducts, Efferocytosis, Human cytomegalovirus infection, Human papillomavirus infection, IL-17 signaling pathway, Kaposi sarcoma-associated herpesvirus infection, Leishmaniasis, MicroRNAs in cancer, NF-kappa B signaling pathway, Ovarian steroidogenesis, Oxytocin signaling pathway, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Platelet activation, Regulation of lipolysis in adipocytes, Retrograde endocannabinoid signaling, Serotonergic synapse, Small cell lung cancer, TNF signaling pathway, VEGF signaling pathway 💬[14] 11, 19, 34, 46, 49, 51, 70, 77, 86, 96, 222, 256, 300, 337 💬
33ACT-434964----[1] 19 💬
34Adalimumab[1] Adalimumab[1] Adalimumab 💬 [1] TNF 💬 [66] AGE-RAGE signaling pathway in diabetic complications, Adipocytokine signaling pathway, African trypanosomiasis, Alcoholic liver disease, Allograft rejection, Alzheimer disease, Amoebiasis, Amyotrophic lateral sclerosis, Antigen processing and presentation, Apoptosis, Asthma, C-type lectin receptor signaling pathway, Chagas disease, Coronavirus disease - COVID-19, Cytokine-cytokine receptor interaction, Dilated cardiomyopathy, Epstein-Barr virus infection, Fc epsilon RI signaling pathway, Fluid shear stress and atherosclerosis, Graft-versus-host disease, Hematopoietic cell lineage, Hepatitis B, Hepatitis C, Herpes simplex virus 1 infection, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Human papillomavirus infection, Hypertrophic cardiomyopathy, IL-17 signaling pathway, Inflammatory bowel disease, Influenza A, Insulin resistance, Legionellosis, Leishmaniasis, Lipid and atherosclerosis, MAPK signaling pathway, Malaria, NF-kappa B signaling pathway, NOD-like receptor signaling pathway, Natural killer cell mediated cytotoxicity, Necroptosis, Non-alcoholic fatty liver disease, Osteoclast differentiation, Pathogenic Escherichia coli infection, Pathways of neurodegeneration - multiple diseases, Pertussis, Prion disease, Proteoglycans in cancer, RIG-I-like receptor signaling pathway, Rheumatoid arthritis, Salmonella infection, Shigellosis, Sphingolipid signaling pathway, Systemic lupus erythematosus, T cell receptor signaling pathway, TGF-beta signaling pathway, TNF signaling pathway, Toll-like receptor signaling pathway, Toxoplasmosis, Tuberculosis, Type I diabetes mellitus, Type II diabetes mellitus, Viral protein interaction with cytokine and cytokine receptor, Yersinia infection, mTOR signaling pathway 💬[18] 19, 37, 40, 41, 46, 55, 56, 84, 96, 97, 107, 160, 164, 222, 226, 269, 270, 271 💬
35Adeno-associated viral (AAV) serotype 8 (AAV2/8) vector with liver-specific thyroxine-binding globulin (TBG) promoter, driving THE expression OF THE human arsb gene----[1] 19 💬
36Adeno-associated viral vector serotype 9 containing THE human N-acetyl-alpha-glucosaminidase gene----[1] 19 💬
37Adeno-associated virus serotype 2/6 encoding human alpha-galactosidase A cdna----[1] 19 💬
38Adeno-associated virus serotype 2/6 encoding human iduronate 2-sulfatase (hids) gene donor vector, SB-A6P-HNT donor vector----[1] 19 💬
39Adeno-associated virus serotype 2/6 encoding left SIDE-zinc finger nuclease (ZFN1), SB-A6P-zleft vector----[1] 19 💬
40Adeno-associated virus serotype 2/6 encoding right SIDE-zinc finger nuclease (ZFN2), SB-A6P-zright vector----[1] 19 💬
41Adeno-associated virus serotype HU68 containing THE human galc gene----[1] 19 💬
42Adeno-associated virus serotype RH.10 expressing BETA-galactosidase----[1] 19 💬
43Adjuvant IM therapy----[1] 19 💬
44Adjuvant immunomodulatory (IM) therapy----[1] 19 💬
45Administration KIT----[1] 19 💬
46Adrabetadex[1] Adrabetadex---[1] 19 💬
47Afegostat tartrate[1] Afegostat[2] Afegostat ,
Afegostat tartrate 💬 		--[1] 19 💬
48Agalsidase----[1] 19 💬
49Agalsidase alfa[1] Agalsidase alfa[1] Agalsidase alfa 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
50Agalsidase alpha[1] Agalsidase alfa[1] Agalsidase alfa 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
51Agalsidase beta[1] Agalsidase beta[1] Agalsidase beta 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
52Agalsidase beta from biosidus 1 MG/KG[1] Agalsidase beta[1] Agalsidase beta 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
53Agalsidasi alfa----[1] 19 💬
54Agalsidasi beta----[1] 19 💬
55AGT-181----[1] 19 💬
56AGT-182[1] AGT-182---[1] 19 💬
57AL01211----[2] 19, 67 💬
58Aldurazyme[1] Laronidase[1] Laronidase 💬 [1] IDUA 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[2] 19, 256 💬
59Aldurazyme*infus 1FL 5ML 500U[1] Laronidase[1] Laronidase 💬 [1] IDUA 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
60Alemtuzumab[1] Alemtuzumab[1] Alemtuzumab 💬 --[18] 13, 15, 19, 20, 36, 43, 44, 46, 51, 60, 65, 85, 96, 107, 283, 284, 285, 326 💬
61Alendronate sodium[1] Alendronic acid[2] Alendronate sodium ,
Alendronic acid 💬 		[1] FDPS 💬 [3] Human T-cell leukemia virus 1 infection, Influenza A, Terpenoid backbone biosynthesis 💬[2] 19, 299 💬
62ALFA-manosidadas humana recombinante----[1] 19 💬
63Allogeneic stem cell transplantation----[5] 19, 20, 49, 62, 84 💬
64Ambroxol[1] Ambroxol[2] Ambroxol hydrochloride ,
Ambroxol 💬 		--[3] 2, 6, 19 💬
65Ambroxol hydrochloride[1] Ambroxol[2] Ambroxol hydrochloride ,
Ambroxol 💬 		--[2] 6, 19 💬
66Ambroxol hydrochloride 30 MG tablet - 18 MG/KG/DAY[1] Ambroxol[2] Ambroxol hydrochloride ,
Ambroxol 💬 		--[1] 19 💬
67Ambroxol hydrochloride 30 MG tablet - 27 MG/KG/DAY[1] Ambroxol[2] Ambroxol hydrochloride ,
Ambroxol 💬 		--[1] 19 💬
68Ambroxol hydrochloride 30 MG tablet - 9 MG/KG/DAY[1] Ambroxol[2] Ambroxol hydrochloride ,
Ambroxol 💬 		--[1] 19 💬
69AMT-191----[1] 19 💬
70Anakinra[1] Anakinra[1] Anakinra 💬 [2] IL1R1,
IL1R2 💬 		[15] Amoebiasis, Cytokine-cytokine receptor interaction, Fluid shear stress and atherosclerosis, Hematopoietic cell lineage, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Inflammatory mediator regulation of TRP channels, MAPK signaling pathway, NF-kappa B signaling pathway, Osteoclast differentiation, Pathogenic Escherichia coli infection, Prostate cancer, Shigellosis, Th17 cell differentiation, Transcriptional misregulation in cancer 💬[19] 2, 13, 15, 19, 28, 37, 41, 46, 49, 50, 54, 56, 84, 86, 97, 106, 107, 266, 299 💬
71Antihistamine----[3] 13, 19, 46 💬
72Antipyretic----[2] 19, 257 💬
73Arimoclomol[1] Arimoclomol[2] Arimoclomol ,
Arimoclomol citrate 💬 		--[3] 2, 15, 19 💬
74Arimoclomol citrate[1] Arimoclomol[2] Arimoclomol ,
Arimoclomol citrate 💬 		--[2] 15, 19 💬
75Arylsulfatase A----[1] 19 💬
76AT-GTX-501----[1] 19 💬
77AT1001----[1] 19 💬
78AT1001 150 MG----[1] 19 💬
79AT2101----[1] 19 💬
80Ataluren[1] Ataluren[1] Ataluren 💬 --[6] 19, 113, 140, 246, 299, 329 💬
81ATG----[6] 13, 19, 60, 96, 222, 285 💬
82Audiology assessment with ABR----[1] 19 💬
83Autologous CD34+ cells transduced with A lentiviral vector containing THE human sgsh gene----[1] 19 💬
84Autologous CD34+ cells transduced with A lentiviral vector encoding THE arsa cdna----[1] 19 💬
85Autologous CD34+ hscs transduced EX vivo with CD11B LV encoding human IDS tagged with apoeii----[1] 19 💬
86Autologous plasmablasts----[1] 19 💬
87AVR-RD-01[1] AVR-RD-01---[1] 19 💬
88AVR-RD-02[1] AVR-RD-02---[1] 19 💬
89AX 250----[1] 19 💬
90AXO-AAV-GM2[1] Cobnabexagene anvuparvovec---[1] 19 💬
91AXO-AAV-GM2 high dose[1] Cobnabexagene anvuparvovec---[1] 19 💬
92AXO-AAV-GM2 LOW dose[1] Cobnabexagene anvuparvovec---[1] 19 💬
93AXO-AAV-GM2 middle dose[1] Cobnabexagene anvuparvovec---[1] 19 💬
94AXO-AAV-GM2 starting dose[1] Cobnabexagene anvuparvovec---[1] 19 💬
95AZ-3102[1] AZ-3102---[1] 19 💬
96Azathioprine[1] Azathioprine[2] Azathioprine ,
Azathioprine sodium 💬 		--[22] 6, 11, 13, 19, 35, 42, 43, 44, 45, 46, 49, 55, 63, 65, 66, 84, 85, 94, 95, 96, 97, 162 💬
97BBM-F101 injection----[1] 19 💬
98Biological assays----[1] 19 💬
99Blood draw----[7] 6, 19, 65, 67, 96, 231, 299 💬
100Blood sampling FOR biological and genetic analysis----[1] 19 💬
101BM110----[1] 19 💬
102BMN 110----[1] 19 💬
103BMN 110 - every other week----[1] 19 💬
104BMN 110 - weekly----[1] 19 💬
105BMN 110 every other week----[1] 19 💬
106BMN 110 weekly----[1] 19 💬
107BMN 190----[1] 19 💬
108BMN 250----[1] 19 💬
109Brain MRI/MRS/fmri----[1] 19 💬
110Brief pain inventory questionnaire----[1] 19 💬
111Brineura[1] Cerliponase alfa[1] Cerliponase alfa 💬 [1] TPP1 💬 [1] Lysosome 💬[1] 19 💬
112Busilvex[1] Busulfan[1] Busulfan 💬 --[4] 19, 36, 60, 65 💬
113Busilvex - 6 MG/ML - concentrato PER soluzione PER infusione - USO endovenoso - flaconcino - 10 ML 8 flaconcini[1] Busulfan[1] Busulfan 💬 --[2] 19, 65 💬
114Busulfan[1] Busulfan[1] Busulfan 💬 --[14] 19, 20, 28, 34, 36, 49, 51, 60, 65, 164, 274, 284, 285, 326 💬
115Busulfan, cyclophosphamide, antithymocyte globulin[1] Busulfan[1] Busulfan 💬 --[2] 19, 20 💬
116Busulfan, cyclophosphamide, ATG[1] Busulfan[1] Busulfan 💬 --[1] 19 💬
117Busulfano[1] Busulfan[1] Busulfan 💬 --[1] 19 💬
118Calcium carbonate[2] Calcium,
Calcium carbonate		[2] Calcium carbonate ,
Calcium carbonate 💬 		--[7] 13, 19, 46, 75, 96, 235, 299 💬
119Campath-1H[1] Alemtuzumab[1] Alemtuzumab 💬 --[6] 19, 20, 60, 65, 234, 326 💬
120Cannabidiol[1] Cannabidiol[1] Cannabidiol 💬 [2] CNR1,
CNR2 💬 		[4] Neuroactive ligand-receptor interaction, Rap1 signaling pathway, Retrograde endocannabinoid signaling, Thermogenesis 💬[18] 6, 8, 13, 19, 36, 46, 95, 96, 97, 140, 144, 145, 156, 157, 158, 193, 206, 271 💬
121Cannabis sativa L., folium CUM flore[1] Medical Cannabis[1] Cannabis 💬 --[1] 19 💬
122Cebsulfase alfa----[1] 19 💬
123Cellule CD34+ autologhe trasdotte CON idua LV codificante PER IL cdna dell'ALFA-L-iduronidasi----[1] 19 💬
124Cerdelga[1] Eliglustat[2] Eliglustat ,
Eliglustat tartrate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
125Cerezyme[1] Imiglucerase[2] Alglucerase ,
Imiglucerase 💬 		[1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
126Cerezyme 400 units powder FOR concentrate FOR solution FOR infusion[1] Imiglucerase[2] Alglucerase ,
Imiglucerase 💬 		[1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
127Cerezyme 400 unità polvere PER concentrato PER soluzione PER infusione----[1] 19 💬
128Cerezyme® / imiglucerase[1] Imiglucerase[2] Alglucerase ,
Imiglucerase 💬 		[1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
129Cerliponase alfa[1] Cerliponase alfa[1] Cerliponase alfa 💬 [1] TPP1 💬 [1] Lysosome 💬[1] 19 💬
130Cetirizine[1] Cetirizine[2] Cetirizine hydrochloride ,
Cetirizine 💬 		[1] HRH1 💬 [4] Calcium signaling pathway, Inflammatory mediator regulation of TRP channels, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction 💬[3] 13, 19, 35 💬
131Challenge agent: capsaicin----[1] 19 💬
132Chemically modified recombinant human sulfamidase----[1] 19 💬
133CHF6657----[1] 19 💬
134Cholecalciferol[1] Cholecalciferol[1] Cholecalciferol 💬 [1] VDR 💬 [5] Chemical carcinogenesis - receptor activation, Endocrine and other factor-regulated calcium reabsorption, Mineral absorption, Parathyroid hormone synthesis, secretion and action, Tuberculosis 💬[9] 13, 19, 34, 46, 49, 96, 97, 298, 299 💬
135Cholesterol[1] Cholesterol[1] Cholesterol 💬 --[5] 19, 90, 160, 222, 310 💬
136Clinimacs® TCR A/ß reagent KIT and clinimacs® CD19 system----[3] 19, 96, 222 💬
137Clofarabine[1] Clofarabine[1] Clofarabine 💬 [3] POLA1,
POLA2,
RRM1 💬 		[5] DNA replication, Drug metabolism - other enzymes, Glutathione metabolism, Purine metabolism, Pyrimidine metabolism 💬[5] 19, 20, 60, 96, 234 💬
138Contrast sensitivity measurement----[1] 19 💬
139Coversyl plus----[1] 19 💬
140Cryopreserved autologous CD34+ cells transduced with A lentiviral vector containing human sgsh gene----[1] 19 💬
141CSA----[5] 19, 49, 60, 63, 222 💬
142Cyclophosphamide[1] Cyclophosphamide[2] Cyclophosphamide ,
Cyclophosphamide 💬 		--[44] 11, 13, 14, 16, 19, 20, 26, 28, 35, 36, 40, 41, 42, 43, 44, 45, 46, 49, 50, 51, 52, 56, 60, 62, 65, 66, 84, 93, 96, 162, 164, 172, 205, 221, 222, 224, 265, 274, 283, 284, 285, 288, 326, 331 💬
143Cyclophosphamide 100 MG/KG[1] Cyclophosphamide[2] Cyclophosphamide ,
Cyclophosphamide 💬 		--[2] 19, 222 💬
144Cyclophosphamide 1200 MG/KG[1] Cyclophosphamide[2] Cyclophosphamide ,
Cyclophosphamide 💬 		--[2] 19, 222 💬
145Cyclosporine A[1] Cyclosporine[1] Cyclosporine 💬 [5] PPP3C,
PPP3C,
PPP3C,
PPP3R,
PPP3R 💬 		[33] Alzheimer disease, Amphetamine addiction, Amyotrophic lateral sclerosis, Axon guidance, B cell receptor signaling pathway, C-type lectin receptor signaling pathway, Calcium signaling pathway, Cellular senescence, Dopaminergic synapse, Glucagon signaling pathway, Glutamatergic synapse, Human T-cell leukemia virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Kaposi sarcoma-associated herpesvirus infection, Lipid and atherosclerosis, Long-term potentiation, MAPK signaling pathway, Natural killer cell mediated cytotoxicity, Oocyte meiosis, Osteoclast differentiation, Oxytocin signaling pathway, PD-L1 expression and PD-1 checkpoint pathway in cancer, Pathways of neurodegeneration - multiple diseases, Prion disease, Renin secretion, T cell receptor signaling pathway, Th1 and Th2 cell differentiation, Th17 cell differentiation, Tuberculosis, VEGF signaling pathway, Wnt signaling pathway, cGMP-PKG signaling pathway 💬[11] 19, 20, 36, 49, 50, 58, 60, 107, 228, 234, 283 💬
146Cystadane anhydrous----[1] 19 💬
147Cystadrops[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
148Cystadrops 0.55% EYE drops, solution[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
149Cystagon[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[3] 8, 19, 299 💬
150Cystagon 150MG[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
151Cystagon 50MG[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
152Cysteamine[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[2] 19, 299 💬
153Cysteamine (mercaptamine) viscous solution[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
154Cysteamine bitartrate[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[4] 8, 19, 21, 299 💬
155Cysteamine bitartrate (INN: mercaptamine bitartrate[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
156Cysteamine bitartrate delayed-release capsules[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
157Cysteamine hydrochloride[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
158Dapagliflozin 10MG TAB[1] Dapagliflozin[1] Dapagliflozin 💬 --[3] 19, 97, 218 💬
159Deflegmin 75MG, kapsulki O przedluzonym uwalnianiu----[1] 19 💬
160Dexa scan----[4] 19, 46, 96, 299 💬
161Dexamethasone[1] Dexamethasone[3] Dexamethasone ,
Dexamethasone sodium phosphate ,
Dexamethasone phosphate 💬 		[1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[22] 13, 14, 16, 19, 28, 35, 63, 64, 70, 74, 75, 81, 84, 90, 96, 97, 222, 235, 257, 296, 299, 331 💬
162DFT383----[1] 19 💬
163Diagnosis OF fabry disease----[1] 19 💬
164Difenidramina cloridrato----[3] 11, 19, 63 💬
165Diphenhydramine[1] Diphenhydramine[4] Diphenhydramine ,
Diphenhydramine hydrochloride ,
Diphenhydramine salicylate ,
Diphenhydramine citrate 💬 		[1] HRH1 💬 [4] Calcium signaling pathway, Inflammatory mediator regulation of TRP channels, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction 💬[10] 13, 19, 49, 51, 70, 86, 96, 222, 256, 300 💬
166DNL126----[1] 19 💬
167DNL310 drug substance----[1] 19 💬
168Dried blood spot (DBS) sampling----[1] 19 💬
169DRX005B----[1] 19 💬
170DUOC-01----[3] 13, 19, 20 💬
171Echocardiogram----[3] 19, 215, 216 💬
172Echocardiography AT M24----[1] 19 💬
173Echocardiography AT T0----[1] 19 💬
174Elaprase[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
175Elaprase 2MG/ML[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
176Elaprase FOR intravenous (IV) infusion----[1] 19 💬
177Elaprase_0.5MG/KG----[1] 19 💬
178Electroencephalogram (EEG) awake and extended overnight----[1] 19 💬
179Elelyso----[1] 19 💬
180Elelyso 60 units/KG----[1] 19 💬
181Elfabrio[1] Pegunigalsidase alfa[1] Pegunigalsidase alfa 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
182Eliglustat[1] Eliglustat[2] Eliglustat ,
Eliglustat tartrate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
183Eliglustat GZ385660[1] Eliglustat[2] Eliglustat ,
Eliglustat tartrate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
184Eliglustat tartrate[1] Eliglustat[2] Eliglustat ,
Eliglustat tartrate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
185Eliglustat tartrate capsules[1] Eliglustat[2] Eliglustat ,
Eliglustat tartrate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
186Eliglustat tartrate – powder FOR oral suspension[1] Eliglustat[2] Eliglustat ,
Eliglustat tartrate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
187Elosulfase alfa[1] Elosulfase alfa[1] Elosulfase alfa 💬 [1] GALNS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
188ELX-02[1] ELX-02---[3] 19, 218, 299 💬
189Enalapril and other angiotensin converting enzyme inhibitors[1] Enalapril[2] Enalapril maleate ,
Enalapril 💬 		[1] ACE 💬 [6] Chagas disease, Coronavirus disease - COVID-19, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[1] 19 💬
190Enriched hematopoetic stem cell infusion----[2] 19, 284 💬
191Enzyme replacement----[1] 19 💬
192Enzyme replacement agent----[2] 19, 256 💬
193Enzyme replacement therapy----[1] 19 💬
194Epidiolex----[1] 19 💬
195ERT----[1] 19 💬
196EU-sourced cerezyme----[1] 19 💬
197Exercise test----[1] 19 💬
198EXG110 injection----[1] 19 💬
199Fabrazyme[1] Agalsidase beta[1] Agalsidase beta 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
200Fabrazyme (agalsidase beta) 1 MG/KG[1] Agalsidase beta[1] Agalsidase beta 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
201Fabrazyme - 35 MG polvere PER concentrato PER soluzione PER infusione endovenosa 1 flaconcino[1] Agalsidase beta[1] Agalsidase beta 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
202Fabrazyme 35 MG[1] Agalsidase beta[1] Agalsidase beta 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
203Fabrazyme 5 MG[1] Agalsidase beta[1] Agalsidase beta 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
204FBX-101[1] FBX-101---[1] 19 💬
205Fexofenadine[1] Fexofenadine[2] Fexofenadine hydrochloride ,
Fexofenadine 💬 		[1] HRH1 💬 [4] Calcium signaling pathway, Inflammatory mediator regulation of TRP channels, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction 💬[4] 6, 13, 19, 46 💬
206FLT190[1] FLT190---[1] 19 💬
207FLT201[1] FLT201---[1] 19 💬
208Fludarabina accord - 25 MG/ML concentrato PER soluzione iniettabile O PER infusione 5 flaconcini IN vetro DA 2 ML[1] Fludarabine[2] Fludarabine phosphate ,
Fludarabine 💬 		[1] RRM1 💬 [4] Drug metabolism - other enzymes, Glutathione metabolism, Purine metabolism, Pyrimidine metabolism 💬[1] 19 💬
209Fludarabina fosfato[1] Fludarabine[2] Fludarabine phosphate ,
Fludarabine 💬 		[1] RRM1 💬 [4] Drug metabolism - other enzymes, Glutathione metabolism, Purine metabolism, Pyrimidine metabolism 💬[1] 19 💬
210Fludarabine[1] Fludarabine[2] Fludarabine phosphate ,
Fludarabine 💬 		[1] RRM1 💬 [4] Drug metabolism - other enzymes, Glutathione metabolism, Purine metabolism, Pyrimidine metabolism 💬[23] 11, 13, 19, 34, 35, 36, 44, 46, 49, 51, 60, 61, 62, 65, 85, 96, 107, 164, 222, 283, 284, 285, 326 💬
211Fluorescein angiography[1] Fluorescein[2] Fluorescein ,
Fluorescein sodium 💬 		--[2] 19, 41 💬
212GA-GCB[1] Velaglucerase alfa[1] Velaglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
213Gabapentin[1] Gabapentin[1] Gabapentin 💬 [5] CACNA2D1,
CACNA2D2,
CACNA2D3,
CACNA2D4,
SLC6A1 💬 		[10] Adrenergic signaling in cardiomyocytes, Arrhythmogenic right ventricular cardiomyopathy, Cardiac muscle contraction, Dilated cardiomyopathy, GABAergic synapse, Hypertrophic cardiomyopathy, MAPK signaling pathway, Neuroactive ligand signaling, Oxytocin signaling pathway, Synaptic vesicle cycle 💬[4] 6, 13, 19, 70 💬
214Galafold[1] Migalastat[2] Migalastat hydrochloride ,
Migalastat 💬 		[1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
215Galsulfase[1] Galsulfase[1] Galsulfase 💬 [1] ARSB 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
216GC1111_0.5MG/KG----[1] 19 💬
217GC1111_1.0MG/KG----[1] 19 💬
218GC1119----[1] 19 💬
219GC1123----[1] 19 💬
220GC1130A----[1] 19 💬
221Gelatine[1] Gelatin[2] Gelatin ,
Donkey glue 💬 		--[2] 19, 296 💬
222Gene activated A-galactosidase A----[1] 19 💬
223Gene activated human glucocerebrosidase----[1] 19 💬
224Gene activated human glucocerebrosidase, velaglucerase alfa[1] Velaglucerase alfa[1] Velaglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
225Gene therapy----[1] 19 💬
226GENE-activated human glucocerebrosidase----[1] 19 💬
227GENE-activated human glucocerebrosidase 200U/vial----[1] 19 💬
228GENE-activated human glucocerebrosidase 400U/vial----[1] 19 💬
229General and neurological examination----[1] 19 💬
230Genetic analyses----[1] 19 💬
231Genetic HMI-203----[1] 19 💬
232Genistein aglycone[1] Genistein[1] Genistein 💬 --[1] 19 💬
233GENZ-112638----[1] 19 💬
234GENZ-682452-AA----[1] 19 💬
235GENZ-682452-AU----[3] 6, 19, 67 💬
236GLA gene----[1] 19 💬
237Glucocerebrosidase----[1] 19 💬
238Glucocerebrosidase umano GENE-attivato----[1] 19 💬
239GNR-055----[1] 19 💬
240GNR-055 1.0-2.0-3.0 MG/KG----[1] 19 💬
241GNR-055 2.0 MG/KG----[1] 19 💬
242GNR-055 3.0 MG/KG----[1] 19 💬
243GR181413----[1] 19 💬
244GR181413A----[1] 19 💬
245GR181413A/AT1001 capsule----[1] 19 💬
246GR181413A/AT1001 solution----[1] 19 💬
247Growth hormone[1] Somatotropin[1] Somatropin 💬 [1] GHR 💬 [6] Cytokine-cytokine receptor interaction, Growth hormone synthesis, secretion and action, Hormone signaling, JAK-STAT signaling pathway, Neuroactive ligand-receptor interaction, PI3K-Akt signaling pathway 💬[16] 2, 19, 46, 77, 78, 96, 97, 107, 113, 156, 191, 193, 195, 238, 265, 299 💬
248GSK2788723----[1] 19 💬
249GZ/SAR402671----[2] 19, 67 💬
250GZ385660----[1] 19 💬
251GZ402665----[1] 19 💬
252GZ402671----[1] 19 💬
253GZ402671 / SAR402671----[1] 19 💬
254Hematopoetic stem cell transplantation----[6] 19, 65, 121, 160, 308, 326 💬
255Hematopoietic stem cell infusion----[2] 19, 20 💬
256Hematopoietic stem cell transplantation----[13] 11, 13, 14, 19, 20, 35, 46, 49, 51, 65, 96, 234, 285 💬
257HeparáN N sulfatasa humana recombinante----[1] 19 💬
258HGT-1110----[1] 19 💬
259HGT-1111----[1] 19 💬
260HGT-1410----[1] 19 💬
261HGT-2310----[1] 19 💬
262High dose AT-GTX-502----[1] 19 💬
263HM15421/GC1134A----[1] 19 💬
264Hucns-SC----[1] 19 💬
265Human glucocerebrosidase cdna----[1] 19 💬
266Human glucocerebrosidase gene into autologous peripheral blood stem cells----[1] 19 💬
267Human N-sulfoglucosamine sulfohydrolase fused TO A humanised monoclonal antibody targeting human transferrin receptor----[1] 19 💬
268Human placental derived stem cell----[4] 19, 20, 60, 284 💬
269Hunterase[1] Idursulfase beta[1] Idursulfase beta 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
270Hydroxypropyl-BETA-cyclodextrin----[1] 19 💬
271Hydroxypropyl-ß-cyclodextrin----[1] 19 💬
272Hydroxyurea[1] Hydroxyurea[1] Hydroxyurea 💬 [1] RRM2 💬 [5] Drug metabolism - other enzymes, Glutathione metabolism, Purine metabolism, Pyrimidine metabolism, p53 signaling pathway 💬[10] 3, 13, 19, 20, 46, 65, 85, 86, 107, 284 💬
273I2S----[1] 19 💬
274I2S-IT----[1] 19 💬
275IB1001----[2] 19, 65 💬
276Iduronate-2-sulfatase enzyme replacement therapy----[1] 19 💬
277Iduronate-2-sulfatase fused TO A FC polypeptide that binds TO THE human transferrin receptor----[1] 19 💬
278Idursulfasa[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
279Idursulfase[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
280Idursulfase (I2S)-IT[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
281Idursulfase beta[2] Idursulfase,
Idursulfase beta		[2] Idursulfase ,
Idursulfase beta 💬 		[1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
282Idursulfase(12S)-IT[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
283Idursulfase(I2S)-IT[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
284Idursulfase-IT[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
285Idursulfasi----[1] 19 💬
286IMD preparative regimen----[5] 19, 20, 125, 234, 326 💬
287Imiglucerasa[1] Imiglucerase[2] Alglucerase ,
Imiglucerase 💬 		[1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
288Imiglucerase[1] Imiglucerase[2] Alglucerase ,
Imiglucerase 💬 		[1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
289Imiglucerase GZ437843[1] Imiglucerase[2] Alglucerase ,
Imiglucerase 💬 		[1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
290Imiglucerasi----[1] 19 💬
291Imiglucérase (drug) pharmacokinetics----[1] 19 💬
292Inactive reminder capsules----[1] 19 💬
293Inactive reminder product----[1] 19 💬
294INN NOT available----[2] 19, 46 💬
295Innozide----[1] 19 💬
296Intracerebral administration OF aavrh.10cuarsa----[1] 19 💬
297Intrathecal recombinant human alpha iduronidase----[1] 19 💬
298Intraventricular access device----[1] 19 💬
299Iohexol[1] Iohexol[1] Iohexol 💬 --[2] 19, 67 💬
300IRT laronidase----[1] 19 💬
301Isaralgagene civaparvovec[1] Isaralgagene civaparvovec---[1] 19 💬
302Isofagamine tartrate----[1] 19 💬
303ISU302----[1] 19 💬
304IV migalastat HCL----[1] 19 💬
305IVA 336----[1] 19 💬
306Izcargo----[1] 19 💬
307JR-141----[1] 19 💬
308JR-141 or idursulfase[1] Idursulfase[1] Idursulfase 💬 [1] IDS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
309JR-171----[1] 19 💬
310JR-441----[1] 19 💬
311JR-446----[1] 19 💬
312JWK008 single intravenous infusion administration----[1] 19 💬
313Kanuma[1] Sebelipase alfa[1] Sebelipase alfa 💬 [1] LIPA 💬 [4] Cholesterol metabolism, Efferocytosis, Lysosome, Steroid biosynthesis 💬[1] 19 💬
314Ketogenic diet----[9] 13, 19, 21, 49, 67, 77, 127, 145, 148 💬
315Kidney transplant----[2] 19, 222 💬
316Laboratory tests----[3] 19, 113, 256 💬
317Lamazym[1] Velmanase alfa[1] Velmanase alfa 💬 [1] MAN2B1 💬 [2] Lysosome, Other glycan degradation 💬[1] 19 💬
318Laronidase[1] Laronidase[1] Laronidase 💬 [1] IDUA 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[2] 19, 256 💬
319Laronidase ERT[1] Laronidase[1] Laronidase 💬 [1] IDUA 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
320Laronidase therapy and A stem cell transplant[1] Laronidase[1] Laronidase 💬 [1] IDUA 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
321Ledipasvir/sofosbuvir[1] Ledipasvir[1] Ledipasvir 💬 --[1] 19 💬
322Lenograstim[1] Lenograstim[1] Lenograstim 💬 [1] CSF3R 💬 [5] Cytokine-cytokine receptor interaction, Hematopoietic cell lineage, JAK-STAT signaling pathway, PI3K-Akt signaling pathway, Pathways in cancer 💬[8] 2, 13, 16, 18, 19, 57, 65, 97 💬
323Lentivirus alpha-GAL A transduced stem cells----[1] 19 💬
324Lepunafusp alfa[1] Lepunafusp alfa---[1] 19 💬
325Leucovorin[1] Leucovorin[3] Leucovorin calcium ,
Folinic acid ,
Folinic acid calcium salt pentahydrate 💬 		--[2] 19, 46 💬
326Lisinopril[1] Lisinopril[2] Lisinopril ,
Lisinopril 💬 		[1] ACE 💬 [6] Chagas disease, Coronavirus disease - COVID-19, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[5] 19, 46, 66, 67, 113 💬
327Lopace----[1] 19 💬
328Loratadine[1] Loratadine[1] Loratadine 💬 [1] HRH1 💬 [4] Calcium signaling pathway, Inflammatory mediator regulation of TRP channels, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction 💬[5] 13, 19, 46, 89, 98 💬
329Losartan[1] Losartan[2] Losartan potassium ,
Losartan 💬 		[1] AGTR1 💬 [17] AGE-RAGE signaling pathway in diabetic complications, Adrenergic signaling in cardiomyocytes, Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Coronavirus disease - COVID-19, Cortisol synthesis and secretion, Cushing syndrome, Diabetic cardiomyopathy, Hormone signaling, Neuroactive ligand-receptor interaction, Pathways in cancer, Phospholipase D signaling pathway, Renin secretion, Renin-angiotensin system, Vascular smooth muscle contraction, cGMP-PKG signaling pathway 💬[15] 17, 19, 46, 58, 66, 67, 85, 96, 97, 113, 164, 167, 215, 222, 299 💬
330Losartan and other angiotensin receptor blockers[1] Losartan[2] Losartan potassium ,
Losartan 💬 		[1] AGTR1 💬 [17] AGE-RAGE signaling pathway in diabetic complications, Adrenergic signaling in cardiomyocytes, Aldosterone synthesis and secretion, Apelin signaling pathway, Calcium signaling pathway, Coronavirus disease - COVID-19, Cortisol synthesis and secretion, Cushing syndrome, Diabetic cardiomyopathy, Hormone signaling, Neuroactive ligand-receptor interaction, Pathways in cancer, Phospholipase D signaling pathway, Renin secretion, Renin-angiotensin system, Vascular smooth muscle contraction, cGMP-PKG signaling pathway 💬[1] 19 💬
331LOW dose AT-GTX-502----[1] 19 💬
332Lucerastat[1] Lucerastat[1] Lucerastat 💬 [1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
333Lumbar puncture----[6] 6, 13, 19, 96, 97, 127 💬
334LY-M001----[1] 19 💬
335LY-M001 injection----[1] 19 💬
336LY3884961[1] LY3884961---[2] 6, 19 💬
337Lymphocyte gene therapy----[1] 19 💬
338LYS-GM101----[1] 19 💬
339LYS-SAF302[1] Olenasufligene relduparvovec---[1] 19 💬
340Lysodase[1] PEG-Glucocerebrosidase---[1] 19 💬
341Mabthera - 2 fiale 100 MG 10 ML[1] Rituximab[1] Rituximab 💬 [1] MS4A1 💬 [1] Hematopoietic cell lineage 💬[2] 19, 65 💬
342Magnetic resonance imaging----[11] 13, 19, 22, 28, 34, 46, 65, 205, 285, 299, 344 💬
343Mechanical stimulation with VON frey filaments----[1] 19 💬
344Medication TO suppress THE immune system----[1] 19 💬
345Melphalan[1] Melphalan[2] Melphalan ,
Melphalan hydrochloride 💬 		--[19] 11, 13, 14, 19, 20, 28, 34, 46, 60, 62, 65, 96, 107, 164, 222, 234, 284, 285, 299 💬
346Mepsevii----[1] 19 💬
347Mercaptamina[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
348Mercaptamine[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
349Mercaptamine bitartrate[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
350Mercaptamine hydrochloride[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
351Mercaptamine, mercamine, 2-aminoethanethiol[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
352Metazym----[1] 19 💬
353Methotrexate[1] Methotrexate[2] Methotrexate ,
Methotrexate sodium 💬 		[2] DHFR,
DHFR 💬 		[3] Folate biosynthesis, Folate transport and metabolism, One carbon pool by folate 💬[37] 11, 13, 19, 34, 35, 40, 41, 42, 43, 44, 45, 46, 49, 50, 51, 53, 54, 55, 60, 62, 65, 84, 93, 96, 97, 107, 162, 164, 172, 256, 270, 271, 284, 285, 286, 326, 331 💬
354Methylprednisolone[1] Methylprednisolone[2] Methylprednisolone ,
Methylprednisolone acetate 💬 		[1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[45] 2, 6, 11, 13, 14, 18, 19, 25, 26, 35, 38, 39, 40, 41, 42, 43, 45, 46, 49, 50, 51, 60, 62, 63, 64, 65, 66, 83, 84, 85, 86, 93, 96, 97, 127, 162, 164, 222, 224, 271, 283, 284, 285, 296, 300 💬
355Migalastat[1] Migalastat[2] Migalastat hydrochloride ,
Migalastat 💬 		[1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
356Migalastat HCL[1] Migalastat[2] Migalastat hydrochloride ,
Migalastat 💬 		[1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
357Migalastat HCL 150 MG[1] Migalastat[2] Migalastat hydrochloride ,
Migalastat 💬 		[1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
358Migalastat HCL 20 MG[1] Migalastat[2] Migalastat hydrochloride ,
Migalastat 💬 		[1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
359Migalastat hydrochloride[1] Migalastat[2] Migalastat hydrochloride ,
Migalastat 💬 		[1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
360Migalastat hydrocloride[1] Migalastat[2] Migalastat hydrochloride ,
Migalastat 💬 		[1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
361Miglustat[1] Miglustat[1] Miglustat 💬 [1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[3] 19, 256, 299 💬
362Montelukast[1] Montelukast[2] Montelukast sodium ,
Montelukast 💬 		[1] CYSLTR1 💬 [2] Calcium signaling pathway, Neuroactive ligand-receptor interaction 💬[9] 6, 13, 19, 46, 61, 63, 85, 98, 228 💬
363MRI with contrast agent injection----[1] 19 💬
364MRI without contrast agent injection----[1] 19 💬
365Mucoangin----[1] 19 💬
366Mycophenolate mofetil[2] Mycophenolate mofetil,
Mycophenolic acid		[4] Mycophenolate mofetil ,
Mycophenolate mofetil hydrochloride ,
Mycophenolate sodium ,
Mycophenolic acid 💬 		[2] IMPDH,
IMPDH 💬 		[2] Drug metabolism - other enzymes, Purine metabolism 💬[32] 2, 11, 13, 19, 20, 28, 35, 36, 42, 43, 44, 46, 49, 51, 53, 60, 62, 63, 65, 66, 93, 95, 96, 164, 222, 224, 226, 234, 283, 284, 285, 300 💬
367Mycophenylate mofetil----[2] 19, 20 💬
368Myelostim - 34 1 flaconcino liofilizzato 33.6 MIU + siringa preriempita solvente 1 ML----[2] 19, 65 💬
369N acetyl cysteine----[2] 6, 19 💬
370N acetyl L leucine----[1] 19 💬
371N-acetyl-L leucine----[1] 19 💬
372N-acetyl-L-leucine[1] L-Acetylleucine---[2] 19, 65 💬
373N-acetylcysteine[1] Acetylcysteine[1] Acetylcysteine 💬 --[14] 6, 13, 19, 20, 21, 49, 58, 85, 90, 111, 164, 296, 299, 337 💬
374N-acetylcysteine amide----[1] 19 💬
375N-acetylgalactosamine 4-sulfatase----[1] 19 💬
376Naglazyme[1] Galsulfase[1] Galsulfase 💬 [1] ARSB 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
377Neurocognitive testing----[1] 19 💬
378Neurology exam----[1] 19 💬
379NGN-101[1] NGN-101---[1] 19 💬
380NO investigational product----[1] 19 💬
381NO IT treatment----[1] 19 💬
382NON applicable----[2] 10, 19 💬
383Odiparcil[1] Odiparcil---[1] 19 💬
384OGT 918----[2] 19, 299 💬
385OGT918----[1] 19 💬
386OGT923----[1] 19 💬
387Olenasufligene relduparvovec[1] Olenasufligene relduparvovec---[1] 19 💬
388Olipudase alfa[1] Olipudase alfa[1] Olipudase alfa 💬 [1] SMPD1 💬 [4] Lysosome, Necroptosis, Sphingolipid metabolism, Sphingolipid signaling pathway 💬[1] 19 💬
389Omnipaque[1] Iohexol[1] Iohexol 💬 --[2] 19, 222 💬
390Ophthalmology exam----[1] 19 💬
391Optimized prophylactic IM therapy----[1] 19 💬
392Oral migalastat HCL----[1] 19 💬
393Osome----[1] 19 💬
394Osteopetrosis haploidentical only preparative regimen----[5] 19, 20, 125, 234, 326 💬
395Osteopetrosis only preparative regimen----[5] 19, 20, 125, 234, 326 💬
396OTL-200----[1] 19 💬
397OTL-200 dispersion FOR infusion----[1] 19 💬
398OTL-200 gene therapy----[1] 19 💬
399OTL-203[1] OTL-203---[1] 19 💬
400Oxygen flow AT THE optic nerve head measurement[1] Oxygen[1] Oxygen 💬 --[1] 19 💬
401Pabinafusp alfa[1] Pabinafusp alfa[1] Pabinafusp alfa 💬 [2] IDS,
TFRC 💬 		[9] Endocytosis, Ferroptosis, Glycosaminoglycan degradation, HIF-1 signaling pathway, Hematopoietic cell lineage, Lysosome, Phagosome, TGF-beta signaling pathway, Virion - Lassa virus and SFTS virus 💬[1] 19 💬
402Palliative care----[6] 19, 65, 121, 160, 308, 326 💬
403Paracetamolo DOC generici - 1000 MG compressa 16 compresse----[1] 19 💬
404Paricalcitol[1] Paricalcitol[1] Paricalcitol 💬 [1] VDR 💬 [5] Chemical carcinogenesis - receptor activation, Endocrine and other factor-regulated calcium reabsorption, Mineral absorption, Parathyroid hormone synthesis, secretion and action, Tuberculosis 💬[5] 19, 66, 218, 238, 298 💬
405PBGM01[1] PBGM01---[1] 19 💬
406PBKR03[1] PBKR03---[1] 19 💬
407Pegunigalsidase alfa[1] Pegunigalsidase alfa[1] Pegunigalsidase alfa 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
408Pegunigalsidase alpha----[1] 19 💬
409Pegunigalsidase-alfa----[1] 19 💬
410Pending----[7] 6, 13, 19, 96, 97, 113, 302 💬
411Pentosan polysulfat SP 54® injection solution----[1] 19 💬
412Pentosan polysulfate sodium[1] Pentosan polysulfate[1] Pentosan polysulfate sodium 💬 --[1] 19 💬
413Pentosan polysulphate SP54----[1] 19 💬
414Perdix----[1] 19 💬
415Picc or other central line placement----[1] 19 💬
416Plant cell recombinant glucocerebrosidase----[1] 19 💬
417PLX-200----[1] 19 💬
418Potable water----[1] 19 💬
419Prednisone[1] Prednisone[1] Prednisone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[54] 2, 11, 13, 14, 18, 19, 26, 28, 35, 40, 41, 42, 43, 44, 45, 46, 49, 50, 51, 53, 60, 61, 63, 64, 65, 66, 79, 81, 84, 85, 86, 90, 93, 95, 96, 97, 113, 145, 162, 164, 205, 222, 224, 228, 251, 269, 283, 285, 288, 299, 300, 303, 307, 331 💬
420Prednisone DOC generici - 5 MG compresse 10 compresse IN blister PVC-pvdc/ALU[1] Prednisone[1] Prednisone 💬 [1] NR3C1 💬 [1] Neuroactive ligand-receptor interaction 💬[1] 19 💬
421Prevenar13----[2] 19, 265 💬
422Prgcd[1] Taliglucerase alfa[1] Taliglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
423Procysbi[1] Cysteamine[3] Cysteamine ,
Cysteamine hydrochloride ,
Cysteamine bitartrate 💬 		--[1] 19 💬
424Prophylactic immunomodulatory (IM) therapy----[1] 19 💬
425PRX-102----[1] 19 💬
426PRX-102 1 MG/KG every 2 weeks----[1] 19 💬
427PRX-102 1 MG/KG every TWO weeks----[1] 19 💬
428PRX-102 2 MG/KG every 4 weeks----[1] 19 💬
429PRX-112----[1] 19 💬
430PRX102----[1] 19 💬
431PTC124----[4] 19, 113, 246, 299 💬
432Purified form OF THE lysosomal enzyme iduronate-2-sulfatase----[1] 19 💬
433Pyrimethamine[1] Pyrimethamine[1] Pyrimethamine 💬 --[4] 2, 4, 19, 65 💬
434Quality OF life questionnaire----[1] 19 💬
435Raav 2/6 hids donor----[1] 19 💬
436RAAV2/5-hnaglu----[1] 19 💬
437RAAV2/6 left ZFN vector----[1] 19 💬
438RAAV2/6 right ZFN vector----[1] 19 💬
439RAAV9.CMV.hnaglu----[1] 19 💬
440Rebisufligene etisparvovec[1] Rebisufligene etisparvovec---[1] 19 💬
441Recombinant adeno-associated virus 2/6 vector encoding THE cdna FOR human alpha galactosidase A----[1] 19 💬
442Recombinant alpha-galactosidase A[1] Agalsidase alfa[1] Agalsidase alfa 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
443Recombinant human acid sphingomyelinase----[1] 19 💬
444Recombinant human alpha-galactosidase----[1] 19 💬
445Recombinant human alpha-galactosidase abbreviated AS R-H-alpha-GAL----[1] 19 💬
446Recombinant human alpha-mannosidase----[1] 19 💬
447Recombinant human arylsulfatase A[1] Recombinant human arylsulfatase A---[1] 19 💬
448Recombinant human arysulfatase B, recombinant human N-acetylgalactosamine 4-sulfatase----[1] 19 💬
449Recombinant human beta glucuronidase----[1] 19 💬
450Recombinant human BETA-glucuronidase[1] Vestronidase alfa[1] Vestronidase alfa 💬 [1] uidA 💬 [6] Ascorbate and aldarate metabolism, Drug metabolism - other enzymes, Glycosaminoglycan degradation, Lysosome, Pentose and glucuronate interconversions, Porphyrin metabolism 💬[1] 19 💬
451Recombinant human betaglucuronidase----[1] 19 💬
452Recombinant human derived macrophage-targeted ß-glucocerebrosidase----[1] 19 💬
453Recombinant human glucerebrosidase----[1] 19 💬
454Recombinant human glucocerebrosidase----[1] 19 💬
455Recombinant human heparan N-sulfatase----[1] 19 💬
456Recombinant human lysosomal acid lipase----[1] 19 💬
457Recombinant human lysosomal alpha-mannosidase----[1] 19 💬
458Recombinant human N-acetylgalactosamine 4-sulfatase----[1] 19 💬
459Recombinant human N-acetylgalactosamine 6-sulfatase, BMN 110----[1] 19 💬
460Recombinant human N-acetylgalactosamine-6-sulfatase, BMN 110[1] Elosulfase alfa[1] Elosulfase alfa 💬 [1] GALNS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
461Recombinant human N-acetylgalactosamine-6-sulfatase, BMN 110 drug substance[1] Elosulfase alfa[1] Elosulfase alfa 💬 [1] GALNS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
462Recombinant human tripeptidyl peptidase-1[1] Cerliponase alfa[1] Cerliponase alfa 💬 [1] TPP1 💬 [1] Lysosome 💬[1] 19 💬
463Recombinant SELF-complementary adeno-associated viral vector serotype 9 containing THE human CLN6 gene----[1] 19 💬
464Reduced intensity conditioning----[2] 19, 65 💬
465Reminder capsules----[1] 19 💬
466Reminder product----[1] 19 💬
467Replagal[1] Agalsidase alfa[1] Agalsidase alfa 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
468Replagal agalsidase alfa[1] Agalsidase alfa[1] Agalsidase alfa 💬 [1] GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome, Sphingolipid metabolism 💬[1] 19 💬
469RGX-111[1] RGX-111---[1] 19 💬
470RGX-121[1] RGX-121---[1] 19 💬
471RH growth hormone----[1] 19 💬
472Rharsa----[1] 19 💬
473Rhasa----[1] 19 💬
474Rhasa - dose level 1----[1] 19 💬
475Rhasa - dose level 2----[1] 19 💬
476Rhasa - dose level 3----[1] 19 💬
477Rhasa [recombinant human arylsulfatase A], formerly HGT-1110, NOW also known AS TAK-611----[1] 19 💬
478Rhasm----[1] 19 💬
479Rhgalns[1] Elosulfase alfa[1] Elosulfase alfa 💬 [1] GALNS 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
480Rhgus----[1] 19 💬
481Rhhns[1] Heparan-N-sulfatase (human, recombinant)---[1] 19 💬
482Rhhns-10 MG[1] Heparan-N-sulfatase (human, recombinant)---[1] 19 💬
483Rhhns-45 MG[1] Heparan-N-sulfatase (human, recombinant)---[1] 19 💬
484Rhhns-90 MG[1] Heparan-N-sulfatase (human, recombinant)---[1] 19 💬
485Rhlaman[1] Velmanase alfa[1] Velmanase alfa 💬 [1] MAN2B1 💬 [2] Lysosome, Other glycan degradation 💬[1] 19 💬
486Rhnaglu----[1] 19 💬
487Rhnaglu radiolabelled----[1] 19 💬
488Rhnaglu-IGF2[1] Tralesinidase alfa---[1] 19 💬
489Rimiducid[1] Rimiducid[1] Rimiducid 💬 [1] CASP9 💬 [34] Alzheimer disease, Amyotrophic lateral sclerosis, Apoptosis, Apoptosis - multiple species, Colorectal cancer, Endometrial cancer, Epstein-Barr virus infection, Hepatitis B, Hepatitis C, Herpes simplex virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Huntington disease, Influenza A, Kaposi sarcoma-associated herpesvirus infection, Legionellosis, Lipid and atherosclerosis, Measles, Non-small cell lung cancer, PI3K-Akt signaling pathway, Pancreatic cancer, Parkinson disease, Pathogenic Escherichia coli infection, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Prion disease, Prostate cancer, Small cell lung cancer, Thyroid hormone signaling pathway, Toxoplasmosis, Tuberculosis, VEGF signaling pathway, Viral myocarditis, p53 signaling pathway 💬[7] 19, 49, 60, 65, 284, 285, 326 💬
490Rituximab[1] Rituximab[1] Rituximab 💬 [1] MS4A1 💬 [1] Hematopoietic cell lineage 💬[52] 11, 13, 14, 19, 26, 34, 35, 36, 40, 41, 42, 43, 44, 45, 46, 49, 50, 51, 52, 53, 55, 56, 60, 61, 62, 63, 64, 65, 66, 83, 84, 85, 86, 93, 94, 96, 97, 162, 172, 220, 222, 229, 256, 271, 274, 283, 284, 285, 288, 296, 300, 331 💬
491Rivogenlecleucel[1] Rivogenlecleucel[1] Rivogenlecleucel 💬 --[6] 19, 60, 65, 284, 285, 326 💬
492RP 103----[2] 8, 19 💬
493RP103----[2] 8, 19 💬
494RVX000222----[1] 19 💬
495SAF-301----[1] 19 💬
496Saline solution FOR injection----[1] 19 💬
497SAR402671, GZ402671 or GZ / SAR402671----[1] 19 💬
498SAR402671, GZ402671 or GZ/SAR402671----[3] 6, 19, 67 💬
499SB-318----[1] 19 💬
500SB-47171----[1] 19 💬
501SB-47898----[1] 19 💬
502SB-913----[1] 19 💬
503SB-A6P-HRL donor vector----[1] 19 💬
504SB-FIX----[1] 19 💬
505SB-idua----[1] 19 💬
506SBC-102[1] Sebelipase alfa[1] Sebelipase alfa 💬 [1] LIPA 💬 [4] Cholesterol metabolism, Efferocytosis, Lysosome, Steroid biosynthesis 💬[1] 19 💬
507SBC-102, recombinant human lysosomal acid lipase[1] Sebelipase alfa[1] Sebelipase alfa 💬 [1] LIPA 💬 [4] Cholesterol metabolism, Efferocytosis, Lysosome, Steroid biosynthesis 💬[1] 19 💬
508SBC-103[1] Lesinidase alfa[1] Lesinidase alfa 💬 [1] NAGLU 💬 [2] Glycosaminoglycan degradation, Lysosome 💬[1] 19 💬
509Scaav9.CB.CLN6----[1] 19 💬
510Scaav9.U1A.hsgsh[1] Rebisufligene etisparvovec---[1] 19 💬
511Scaav9.U1A.sgsh----[1] 19 💬
512Sebelipase alfa[1] Sebelipase alfa[1] Sebelipase alfa 💬 [1] LIPA 💬 [4] Cholesterol metabolism, Efferocytosis, Lysosome, Steroid biosynthesis 💬[1] 19 💬
513Sebelipase alfa 0.35 MG/KG[1] Sebelipase alfa[1] Sebelipase alfa 💬 [1] LIPA 💬 [4] Cholesterol metabolism, Efferocytosis, Lysosome, Steroid biosynthesis 💬[1] 19 💬
514Sebelipase alfa 1 MG/KG[1] Sebelipase alfa[1] Sebelipase alfa 💬 [1] LIPA 💬 [4] Cholesterol metabolism, Efferocytosis, Lysosome, Steroid biosynthesis 💬[1] 19 💬
515Sebelipase alfa 3 MG/KG[1] Sebelipase alfa[1] Sebelipase alfa 💬 [1] LIPA 💬 [4] Cholesterol metabolism, Efferocytosis, Lysosome, Steroid biosynthesis 💬[1] 19 💬
516SHP611----[1] 19 💬
517SHP675----[1] 19 💬
518Sirolimus[1] Sirolimus[1] Sirolimus 💬 [1] MTOR 💬 [49] AMPK signaling pathway, Acute myeloid leukemia, Adipocytokine signaling pathway, Alzheimer disease, Amyotrophic lateral sclerosis, Apelin signaling pathway, Autophagy - animal, Autophagy - other, Breast cancer, Cellular senescence, Central carbon metabolism in cancer, Chemical carcinogenesis - receptor activation, Choline metabolism in cancer, Colorectal cancer, Diabetic cardiomyopathy, ErbB signaling pathway, Gastric cancer, Glioma, Growth hormone synthesis, secretion and action, HIF-1 signaling pathway, Hepatocellular carcinoma, Herpes simplex virus 1 infection, Human cytomegalovirus infection, Human immunodeficiency virus 1 infection, Human papillomavirus infection, Huntington disease, Insulin resistance, Insulin signaling pathway, JAK-STAT signaling pathway, Kaposi sarcoma-associated herpesvirus infection, Longevity regulating pathway, Longevity regulating pathway - multiple species, MicroRNAs in cancer, Neutrophil extracellular trap formation, PD-L1 expression and PD-1 checkpoint pathway in cancer, PI3K-Akt signaling pathway, Pancreatic cancer, Pathways in cancer, Pathways of neurodegeneration - multiple diseases, Phospholipase D signaling pathway, Prostate cancer, Proteoglycans in cancer, Shigellosis, Spinocerebellar ataxia, Th17 cell differentiation, Thermogenesis, Thyroid hormone signaling pathway, Type II diabetes mellitus, mTOR signaling pathway 💬[39] 6, 13, 15, 19, 21, 34, 35, 36, 46, 48, 49, 51, 60, 61, 62, 63, 65, 66, 67, 85, 86, 89, 97, 98, 137, 157, 158, 192, 222, 227, 277, 278, 279, 280, 281, 283, 285, 300, 331 💬
519Skeletal survey----[1] 19 💬
520Skin biopsy----[4] 6, 19, 21, 84 💬
521Slit lamp assessment and intra-ocular pressure measurement----[1] 19 💬
522SOBI003----[1] 19 💬
523Somatropin[1] Somatotropin[1] Somatropin 💬 [1] GHR 💬 [6] Cytokine-cytokine receptor interaction, Growth hormone synthesis, secretion and action, Hormone signaling, JAK-STAT signaling pathway, Neuroactive ligand-receptor interaction, PI3K-Akt signaling pathway 💬[18] 2, 3, 19, 74, 75, 78, 96, 97, 107, 113, 187, 193, 195, 238, 265, 274, 276, 299 💬
524Speech and modified barium swallow study----[1] 19 💬
525ST-920----[1] 19 💬
526Stem cell transplant----[7] 19, 20, 60, 65, 96, 164, 284 💬
527Stem cell transplantation----[13] 13, 19, 20, 46, 51, 60, 62, 65, 90, 125, 164, 234, 326 💬
528SUB195712----[1] 19 💬
529TAK-675----[1] 19 💬
530Taliglucerase alfa[1] Taliglucerase alfa[1] Taliglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
531Taliglucerase alfa - recombinant human glucocerebrosidase[1] Taliglucerase alfa[1] Taliglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
532TBD----[5] 19, 86, 90, 276, 299 💬
533Temperature sensitivity measurement with advanced thermal stimulation----[1] 19 💬
534Thiotepa--escalated dose[1] Thiotepa[1] Thiotepa 💬 --[4] 19, 20, 65, 284 💬
535Thiotepa--single daily dose[1] Thiotepa[1] Thiotepa 💬 --[4] 19, 20, 65, 284 💬
536Tividenofusp alfa[1] Tividenofusp alfa[1] Tividenofusp alfa 💬 [2] IDS,
TFRC 💬 		[9] Endocytosis, Ferroptosis, Glycosaminoglycan degradation, HIF-1 signaling pathway, Hematopoietic cell lineage, Lysosome, Phagosome, TGF-beta signaling pathway, Virion - Lassa virus and SFTS virus 💬[1] 19 💬
537Total body irradiation----[13] 19, 20, 36, 49, 51, 60, 62, 65, 96, 222, 283, 284, 285 💬
538Total body irradiation with marrow boosting----[2] 19, 234 💬
539Tralesinidase alfa[1] Tralesinidase alfa---[1] 19 💬
540Transduced CD34+ hematopoietic stem cell----[2] 19, 20 💬
541Trappsol cyclo----[1] 19 💬
542Treosulfan[1] Treosulfan[1] Treosulfan 💬 --[6] 13, 19, 62, 65, 284, 286 💬
543Triapin& triapin mite----[1] 19 💬
544Tropicamide[1] Tropicamide[1] Tropicamide 💬 [5] CHRM1,
CHRM2,
CHRM3,
CHRM4,
CHRM5 💬 		[14] Alzheimer disease, Calcium signaling pathway, Cholinergic synapse, Gastric acid secretion, Insulin secretion, Neuroactive ligand signaling, Neuroactive ligand-receptor interaction, PI3K-Akt signaling pathway, Pancreatic secretion, Pathways of neurodegeneration - multiple diseases, Regulation of actin cytoskeleton, Salivary secretion, Taste transduction, cAMP signaling pathway 💬[1] 19 💬
545TSHA-101[1] TSHA-101---[1] 19 💬
546TTX-381----[1] 19 💬
547Unrelated umbilical cord blood transplant----[1] 19 💬
548Uplyso----[1] 19 💬
549Urine collection----[3] 19, 215, 216 💬
550Usan: sebelipasa alfa[1] Sebelipase alfa[1] Sebelipase alfa 💬 [1] LIPA 💬 [4] Cholesterol metabolism, Efferocytosis, Lysosome, Steroid biosynthesis 💬[1] 19 💬
551Usan: sebelipase alpha----[1] 19 💬
552UX003----[1] 19 💬
553UX111[1] Rebisufligene etisparvovec---[1] 19 💬
554Vector viral adenoasociado DE serotipo 9 QUE contiene EL GEN DE LA sulfamidasa humana----[1] 19 💬
555Velaglucerase alfa[1] Velaglucerase alfa[1] Velaglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
556Velaglucerasi alfa----[1] 19 💬
557Velmanase alfa[1] Velmanase alfa[1] Velmanase alfa 💬 [1] MAN2B1 💬 [2] Lysosome, Other glycan degradation 💬[1] 19 💬
558Venglustat[1] Venglustat[2] Venglustat ,
Venglustat malate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[2] 19, 67 💬
559Venglustat GZ402671[1] Venglustat[2] Venglustat ,
Venglustat malate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[2] 19, 67 💬
560Venglustat L-malate[1] Venglustat[2] Venglustat ,
Venglustat malate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
561Venglustat malate[1] Venglustat[2] Venglustat ,
Venglustat malate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[3] 6, 19, 67 💬
562Venglustat malato[1] Venglustat[2] Venglustat ,
Venglustat malate 💬 		[1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[2] 19, 67 💬
563Verenafusp alfa 12 MG/KG----[1] 19 💬
564Verenafusp alfa 6 MG/KG----[1] 19 💬
565Verenafusp alfa 9 MG/KG----[1] 19 💬
566Vestronidase alfa[1] Vestronidase alfa[1] Vestronidase alfa 💬 [1] uidA 💬 [6] Ascorbate and aldarate metabolism, Drug metabolism - other enzymes, Glycosaminoglycan degradation, Lysosome, Pentose and glucuronate interconversions, Porphyrin metabolism 💬[1] 19 💬
567VGN-R08B----[1] 19 💬
568Visual field testing----[1] 19 💬
569Vital signs----[4] 3, 15, 19, 256 💬
570Vitamin D[1] Vitamin D---[20] 6, 13, 19, 41, 43, 44, 46, 49, 50, 68, 93, 95, 96, 97, 179, 222, 228, 235, 274, 299 💬
571Vitamin E[1] Vitamin E[1] Vitamin E 💬 --[5] 2, 19, 20, 90, 206 💬
572Vosoritide[1] Vosoritide[1] Vosoritide 💬 [1] NPR2 💬 [5] Hormone signaling, Oxytocin signaling pathway, Purine metabolism, Vascular smooth muscle contraction, cGMP-PKG signaling pathway 💬[2] 19, 276 💬
573Vpriv[1] Velaglucerase alfa[1] Velaglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
574Vpriv - 400 U - polvere PER soluzione PER infusione - USO endovenoso - flaconcino(vetro) 1 flaconcino[1] Velaglucerase alfa[1] Velaglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
575Vpriv 400 units powder FOR solution OF infusion[1] Velaglucerase alfa[1] Velaglucerase alfa 💬 [1] GBA 💬 [4] Cornified envelope formation, Lysosome, Other glycan degradation, Sphingolipid metabolism 💬[1] 19 💬
576VTS-270----[1] 19 💬
577Warfarin[1] Warfarin[3] Warfarin sodium ,
Warfarin potassium ,
Warfarin 💬 		[2] NQO1,
VKORC1 💬 		[5] Chemical carcinogenesis - reactive oxygen species, Fluid shear stress and atherosclerosis, Hepatocellular carcinoma, Pathways in cancer, Ubiquinone and other terpenoid-quinone biosynthesis 💬[10] 6, 8, 19, 46, 49, 66, 85, 86, 88, 91 💬
578Water[1] Water[1] Water 💬 --[25] 2, 5, 6, 13, 17, 19, 22, 46, 51, 53, 56, 57, 63, 64, 66, 67, 85, 96, 97, 206, 226, 230, 274, 278, 299 💬
579Whole body protein turnover----[4] 19, 46, 96, 299 💬
580Zavesca[1] Miglustat[1] Miglustat 💬 [1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[3] 19, 256, 299 💬
581Zavesca 84CPS 100MG[1] Miglustat[1] Miglustat 💬 [1] UGCG 💬 [2] Cornified envelope formation, Sphingolipid metabolism 💬[1] 19 💬
582Zestoretic 10,20[1] Lisinopril[2] Lisinopril ,
Lisinopril 💬 		[1] ACE 💬 [6] Chagas disease, Coronavirus disease - COVID-19, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[1] 19 💬
583Zestoric----[1] 19 💬
584Zestril[1] Lisinopril[2] Lisinopril ,
Lisinopril 💬 		[1] ACE 💬 [6] Chagas disease, Coronavirus disease - COVID-19, Diabetic cardiomyopathy, Hypertrophic cardiomyopathy, Renin secretion, Renin-angiotensin system 💬[3] 19, 67, 222 💬