Hematopoetic stem cell transplantation
( DrugBank: - / KEGG DRUG: - )
6 diseases
| ID | Disease name (Link within this page) | Number of trials |
|---|---|---|
| 19 | Lysosomal storage disease | 1 |
| 65 | Primary immunodeficiency | 1 |
| 121 | Neurodegeneration with brain iron accumulation | 1 |
| ID | Disease name (Link within this page) | Number of trials |
|---|---|---|
| 160 | Congenital ichthyosis | 1 |
| 308 | Progressive leukoencephalopathy | 1 |
| 326 | Osteopetrosis | 1 |
19. Lysosomal storage disease
Clinical trials : 990 / Drugs : 584 - (DrugBank : 126) / Drug target genes : 62 - Drug target pathways : 192
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|
65. Primary immunodeficiency
Clinical trials : 798 / Drugs : 585 - (DrugBank : 118) / Drug target genes : 100 - Drug target pathways : 216
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|
121. Neurodegeneration with brain iron accumulation
Clinical trials : 30 / Drugs : 26 - (DrugBank : 5) / Drug target genes : 4 - Drug target pathways : 106
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|
160. Congenital ichthyosis
Clinical trials : 57 / Drugs : 68 - (DrugBank : 25) / Drug target genes : 21 - Drug target pathways : 141
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|
308. Progressive leukoencephalopathy
Clinical trials : 2 / Drugs : 3 - (DrugBank : 1) / Drug target genes : 5 - Drug target pathway : 1
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|
326. Osteopetrosis
Clinical trials : 18 / Drugs : 37 - (DrugBank : 16) / Drug target genes : 25 - Drug target pathways : 93
| No. | TrialID | Date_ enrollment | Date_ registration | Public_title | Scientific_title | Condition | Intervention | Primary_ sponsor | Secondary_ sponsor | Recruitment_ Status | Inclusion_ agemin | Inclusion_ agemax | Inclusion_ gender | Target_ size | Phase | Countries |
|---|
