246. Methylmalonic acidemia Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 23 / Drugs : 31 - (DrugBank : 8) / Drug target genes : 17 - Drug target pathways : 23
| Other names | - | ||
|---|---|---|---|
| Disease group | Metabolic diseases | ||
| Related info (in Japanese) | - | ||
| Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 8-2-23. methylmalonic acidaemia; MMA | ||
| Subtypes | - | ||