251. Urea cycle disorder Clinical trials / Disease details

Clinical trials : 54 / Drugs : 61 - (DrugBank : 15) / Drug target genes : 3 - Drug target pathways : 28

3 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03335488 (ClinicalTrials.gov)	February 20, 2018	18/10/2017	Study of Glycerol Phenylbutyrate& Sodium Phenylbutyrate in Phenylbutyrate Naïve Patients With Urea C ...	A Randomised, Controlled, Open-Label Parallel Arm Study of Safety, PK and Ammonia Control of RAVICTI ...	Urea Cycle Disorder	Drug: RAVICTI;Drug: NaPBA	Horizon Therapeutics, LLC	NULL	Completed	N/A	99 Years	All	16	Phase 4	United States;Italy;Spain;Switzerland;Belgium
2	NCT02246218 (ClinicalTrials.gov)	December 31, 2014	17/9/2014	A Study of the Safety, Efficacy and Pharmacokinetics of Glycerol Phenylbutyratein Pediatric Subjects ...	An Open Label Study of the Safety, Efficacy and Pharmacokinetics of Glycerol Phenylbutyrate(GPB; RAV ...	Urea Cycle Disorder	Drug: RAVICTI	Horizon Therapeutics, LLC	NULL	Completed	N/A	2 Years	All	27	Phase 4	United States;Canada
3	EUCTR2008-003865-23-GB (EUCTR)	08/09/2008	25/07/2008	A Phase 2, Switch-Over, Dose-Escalation Study of the Safety and Tolerability of HPN-100 (glyceryl tr ...	A Phase 2, Switch-Over, Dose-Escalation Study of the Safety and Tolerability of HPN-100 (glyceryl tr ...	Urea Cycle Disorder (urea cycle enzyme or transporter deficiency) MedDRA version: 9.1;Level: LLT;Cla ...	Product Name: glyceryl tri-(4-phenylbutyrate)(GT4P) Product Code: HPN-100 INN or Proposed INN: NA Other ...	Hyperion Therapeutics Limited	NULL	Not Recruiting			Female: yes Male: yes	16	Phase 2	United Kingdom

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