337. Homocystinuria Clinical trials / Disease details

Clinical trials : 16 / Drugs : 19 - (DrugBank : 7) / Drug target genes : 2 - Drug target pathways : 23

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01793090 (ClinicalTrials.gov)	January 2013	8/2/2013	EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment	Phase 2, Double-Blind, Placebo Controlled Clinical Trial of EPI-743in Subjects With Cobalamin C Defe ...	Methylmalonic Aciduria and Homocystinuria,Cblc Type;Genetic Disease;Retinopathy	Drug: Epi-743;Other: Placebo supplementation	Bambino Gesù Hospital and Research Institute	Catholic University of the Sacred Heart	Completed	1 Year	20 Years	All	30	Phase 2	Italy

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