1. Spinal and bulbar muscular atrophy Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 18 / Drugs : 15 - (DrugBank : 8) / Drug target genes : 10 - Drug target pathways : 17
Other names | Spinobulbar muscular atrophy;SBMA;Kennedy disease;Kennedy-Alter-Sung syndrome; | ||
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Disease group | Neuromuscular diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
1,700 patients Age distribution
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Related info (in Japanese) | |||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | - | ||
Subtypes | - |