1. Spinal and bulbar muscular atrophy Disease details / Clinical trials / Drug dev / DR info


Clinical trials : 20 /  Drugs : 19 - (DrugBank : 8) / Drug target genes : 11 - Drug target pathways : 20

Drugs, Primary sponsors and Trial info (Enrollment year, Phase, Trial ID, Countries)
AJ201
   AnnJi Pharmaceutical Co., Ltd.
      2023   Phase 1/Phase 2   NCT05517603   United States
BVS857
   Novartis Farma SpA
      2014   Phase 2   EUCTR2013-002608-15-IT   Denmark;Germany;Italy;United States
   Novartis Pharma Services AG
      2014   Phase 2   EUCTR2013-002608-15-DK   Denmark;Germany;Italy;United States
      2014   Phase 2   EUCTR2013-002608-15-DE   Denmark;Germany;Italy;United States
   Novartis Pharmaceuticals
      2014   Phase 2   NCT02024932   Denmark;Germany;Italy;United States
Clenbuterol
   AZIENDA OSPEDALIERA DI PADOVA
      2010   -   EUCTR2010-022558-18-IT   Italy
   Gianni Soraru
      2024   Phase 2   NCT06169046   Italy
Clenbuterolo
   AZIENDA OSPEDALIERA DI PADOVA
      2021   Phase 2   EUCTR2017-005103-27-IT   Italy
Creatine
   Department of Neurology, Nagoya University Graduate School of Medicine
      2014   -   JPRN-UMIN000012503   Japan
Dutasteride
   National Institute of Neurological Disorders and Stroke (NINDS)
      2006   Phase 2   NCT00303446   United States
Electrophysiologic study
   Ramathibodi Hospital
      2008   Phase 4   NCT00851461   Thailand
Goserelin
   Ramathibodi Hospital
      2008   Phase 4   NCT00851461   Thailand
Leuprolide
   National Center for Research Resources (NCRR)
      1992   Phase 2   NCT00004771   -
Leuprorelin acetate
   Department of Neurology Chiba University Graduate School of Medicine
      2008   -   JPRN-UMIN000001455   Japan
   Department of Neurology, Nagoya University School of Medicine
      2003   Phase 2   JPRN-UMIN000000474   Japan
   TAKEDA PHARMACEUTICAL COMPANY LTD.
      2017   -   JPRN-jRCT1080223924   none
   Takeda
      2017   -   NCT03555578   Japan
Mexiletine hydrochloride
   Katsuno Masahisa
      2025   Phase 2-3   JPRN-jRCT2041240174   -
   Masahisa Katsuno
      2025   Phase 2/Phase 3   NCT06862596   Japan
   Nagoya University Graduate School of Medicine
      2017   Phase 2   JPRN-UMIN000026150   Japan
Monores 20 MCG 30 compresse
   AZIENDA OSPEDALIERA DI PADOVA
      2021   Phase 2   EUCTR2017-005103-27-IT   Italy
Monores*30CPR 20MCG
   AZIENDA OSPEDALIERA DI PADOVA
      2010   -   EUCTR2010-022558-18-IT   Italy
NIDO-361
   Nido Biosciences, Inc.
      2024   Phase 2   NCT06411912   Denmark;Italy;South Korea;United Kingdom
Testosterone
   National Center for Research Resources (NCRR)
      1992   Phase 2   NCT00004771   -
Tissue biopsy
   Ramathibodi Hospital
      2008   Phase 4   NCT00851461   Thailand