10. Charcot-Marie-Tooth disease Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 45 / Drugs : 34 - (DrugBank : 10) / Drug target genes : 12 - Drug target pathways : 22
| Other names | CMT; | ||
|---|---|---|---|
| Disease group | Neuromuscular diseases | ||
|
Domestic patients
Med expenses recipients (FY2023) |
922 patients Age distribution
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| Related info (in Japanese) | |||
| Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 11-20-46. Hereditary Motor and Sensory Neuropathy; Charcot-Marie-Tooth disease | ||
| Subtypes | - | ||

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