28. Systemic amyloidosis Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 454 / Drugs : 430 - (DrugBank : 90) / Drug target genes : 66 - Drug target pathways : 183
| Other names | - | ||
|---|---|---|---|
| Disease group | Metabolic diseases | ||
|
Domestic patients
Med expenses recipients, FY2024 (corrected) (in Japanese) |
8,169 patients Age distribution
|
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| Clinical research form (in Japanese) MHLW Intractable Diseases, FY2026 (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Notice(R7.1.16) (pdf), Notice(R7.8.21) (pdf), Clinical research form (pdf) 028-01, 028-02, 028-03, 028-04 | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 2-5-25. Amyloid nephropathy | ||
| Sub-diseases (Clinical research forms may not be available for all sub-diseases.) | No. | Name | Specific pediatric chronic diseases, Japan (in Japanese) |
| 28-1. | Immunoglobulin light chain amyloidosis;Amyloid light-chain amyloidosis;AL amyloidosis;Immunoglobulin light chain amyloidosis;Immunoglobulin-related amyloidosis;Amyloid heavy-chain amyloidosis;Amyloid heavy-chain amyloidosis;AH amyloidosis; | ||
| 28-2. | Systemic wild-type transthyretin amyloidosis;Senile systemic amyloidosis;SSA;Transthyretin amyloid cardiomyopathy;ATTR-CM; | ||
| 28-3. | Hereditary transthyretin amyloidosis;Familial amyloidosis;Familial amyloid polyneuropathy;FAP;Transthyretin amyloid cardiomyopathy;ATTR-CM; | ||
| 28-4. | Hereditary systemic amyloidosis; | ||
