3. Spinal muscular atrophy Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 237 / Drugs : 123 - (DrugBank : 29) / Drug target genes : 51 - Drug target pathways : 75
| Other names | Myelopathic muscular atrophy; | ||
|---|---|---|---|
| Disease group | Neuromuscular diseases | ||
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Domestic patients
Med expenses recipients (FY2023) |
955 patients Age distribution
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| Related info (in Japanese) | |||
| Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 11-18-42. spinal muscular atrophy; SMA | ||
| Subtypes | No. | Name | Specific pediatric chronic diseases, Japan (in Japanese) |
| 3-1. | Spinal muscular atrophy type I;SMA I;Werdnig-Hoffman disease; | 11-18-42. spinal muscular atrophy; SMA | |
| 3-2. | Spinal muscular atrophy type II;SMA II;Dubowitz disease; | 11-18-42. spinal muscular atrophy; SMA | |
| 3-3. | Spinal muscular atrophy type III;SMA III;Kugelberg-Welander disease; | 11-18-42. spinal muscular atrophy; SMA | |
| 3-4. | Spinal muscular atrophy type IV;SMA IV; | 11-18-42. spinal muscular atrophy; SMA | |