301. Macular dystrophy Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 59 / Drugs : 42 - (DrugBank : 14) / Drug target genes : 9 - Drug target pathways : 72
Other names | Vitelliform macular dystrophy;Best vitelliform macular dystrophy;Best disease;Stargardt disease;Occult macular dystrophy;Cone dystrophy;Cone rod dystrophy;X-linked juvenile retinoschisis;Central areolar choroidal dystrophy; | ||
---|---|---|---|
Disease group | Eye diseases | ||
Domestic patients
Med expenses recipients (FY2023) |
244 patients Age distribution
![]() |
||
Related info (in Japanese) | |||
Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
Specific pediatric chronic diseases, Japan (in Japanese) | - | ||
Subtypes | - |