Hematopoetic Stem Cell Transplantation

( DrugBank: - / KEGG DRUG: - )


5 diseases
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1
65Primary immunodeficiency1
120Hereditary dystonia1
IDDisease name (Link within this page)Number of trials
160Congenital ichthyosis1
326Osteopetrosis1

19. Lysosomal storage disease


Clinical trials : 899Drugs : 684 - (DrugBank : 99) / Drug target genes : 51 - Drug target pathways : 182 
No.TrialIDDate_
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65. Primary immunodeficiency


Clinical trials : 500Drugs : 614 - (DrugBank : 119) / Drug target genes : 92 - Drug target pathways : 217 
No.TrialIDDate_
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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120. Hereditary dystonia


Clinical trials : 26Drugs : 19 - (DrugBank : 3) / Drug target genes : 2 - Drug target pathways : 2 
No.TrialIDDate_
enrollment
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registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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agemin
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160. Congenital ichthyosis


Clinical trials : 42Drugs : 71 - (DrugBank : 21) / Drug target genes : 18 - Drug target pathways : 112 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
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agemin
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agemax
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326. Osteopetrosis


Clinical trials : 18Drugs : 43 - (DrugBank : 14) / Drug target genes : 17 - Drug target pathways : 82 
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
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Inclusion_
agemin
Inclusion_
agemax
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gender
Target_
size
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