Target Gene/Pathway Pathway / Gene


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No. KEGG GENES KEGG PATHWAY KEGG DRUG DrugBank 指定難病告示番号
1 AKR1B1 💬 5件: Pentose and glucuronate interconversions, Fructose and mannose metabolism, Galactose metabolism, Glycerolipid metabolism, Folate biosynthesis Epalrestat 💬 Epalrestat 1件: 10 💬
2 ALDH1B1 💬 13件: Glycolysis / Gluconeogenesis, Ascorbate and aldarate metabolism, Fatty acid degradation, Valine, leucine and isoleucine degradation, Lysine degradation, Arginine and proline metabolism, Histidine metabolism, Tryptophan metabolism, beta-Alanine metabolism, Glycerolipid metabolism, Pyruvate metabolism, Pantothenate and CoA biosynthesis, Alcoholic liver disease Disulfiram 💬 Disulfiram 3件: 46, 90, 301 💬
3 ALDH2 💬 13件: Glycolysis / Gluconeogenesis, Ascorbate and aldarate metabolism, Fatty acid degradation, Valine, leucine and isoleucine degradation, Lysine degradation, Arginine and proline metabolism, Histidine metabolism, Tryptophan metabolism, beta-Alanine metabolism, Glycerolipid metabolism, Pyruvate metabolism, Pantothenate and CoA biosynthesis, Alcoholic liver disease Disulfiram 💬 Disulfiram 3件: 46, 90, 301 💬
4 ALDH3A2 💬 13件: Glycolysis / Gluconeogenesis, Ascorbate and aldarate metabolism, Fatty acid degradation, Valine, leucine and isoleucine degradation, Lysine degradation, Arginine and proline metabolism, Histidine metabolism, Tryptophan metabolism, beta-Alanine metabolism, Glycerolipid metabolism, Pyruvate metabolism, Pantothenate and CoA biosynthesis, Alcoholic liver disease Disulfiram 💬 Disulfiram 3件: 46, 90, 301 💬
5 GLA 💬 5件: Galactose metabolism, Glycerolipid metabolism, Sphingolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome biogenesis Agalsidase beta 💬 Agalsidase beta 1件: 19 💬
6 GLA 💬 5件: Galactose metabolism, Glycerolipid metabolism, Sphingolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome biogenesis Pegunigalsidase alfa 💬 Pegunigalsidase alfa 1件: 19 💬
7 GLA 💬 5件: Galactose metabolism, Glycerolipid metabolism, Sphingolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome biogenesis Migalastat hydrochloride 💬 Migalastat 1件: 19 💬
8 GLA 💬 5件: Galactose metabolism, Glycerolipid metabolism, Sphingolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome biogenesis Agalsidase alfa 💬 Agalsidase alfa 1件: 19 💬
9 LIPC 💬 2件: Glycerolipid metabolism, Cholesterol metabolism Dextran sulfate sodium 💬 Dextran 5件: 2, 62, 79, 96, 97 💬
10 LPL 💬 4件: Glycerolipid metabolism, PPAR signaling pathway, Cholesterol metabolism, Alzheimer disease Dextran sulfate sodium 💬 Dextran 5件: 2, 62, 79, 96, 97 💬