Target Gene/Pathway Pathway / Gene


Search results


No. KEGG GENES KEGG PATHWAY KEGG DRUG DrugBank Disease ID
1 ARSB 💬 [2] Glycosaminoglycan degradation, Lysosome Galsulfase 💬 Galsulfase [1] 19 💬
2 CTSC 💬 [2] Lysosome, Apoptosis Brensocatib 💬 Brensocatib [1] 299 💬
3 GAA 💬 [3] Galactose metabolism, Starch and sucrose metabolism, Lysosome Duvoglustat 💬 Duvoglustat [1] 256 💬
4 GAA 💬 [3] Galactose metabolism, Starch and sucrose metabolism, Lysosome Cipaglucosidase alfa 💬 Cipaglucosidase alfa [1] 256 💬
5 GAA 💬 [3] Galactose metabolism, Starch and sucrose metabolism, Lysosome Duvoglustat hydrochloride 💬 Duvoglustat [1] 256 💬
6 GAA 💬 [3] Galactose metabolism, Starch and sucrose metabolism, Lysosome Avalglucosidase alfa 💬 Avalglucosidase alfa [1] 256 💬
7 GAA 💬 [3] Galactose metabolism, Starch and sucrose metabolism, Lysosome Alglucosidase alfa 💬 Alglucosidase alfa [1] 256 💬
8 GAA 💬 [3] Galactose metabolism, Starch and sucrose metabolism, Lysosome Clervonafusp alfa 💬 Clervonafusp alfa [1] 309 💬
9 GAA 💬 [3] Galactose metabolism, Starch and sucrose metabolism, Lysosome Acarbose 💬 Acarbose [1] 298 💬
10 GALNS 💬 [2] Glycosaminoglycan degradation, Lysosome Elosulfase alfa 💬 Elosulfase alfa [1] 19 💬
11 GBA 💬 [4] Other glycan degradation, Sphingolipid metabolism, Lysosome, Cornified envelope formation Imiglucerase 💬 Imiglucerase [1] 19 💬
12 GBA 💬 [4] Other glycan degradation, Sphingolipid metabolism, Lysosome, Cornified envelope formation Alglucerase 💬 Imiglucerase [1] 19 💬
13 GBA 💬 [4] Other glycan degradation, Sphingolipid metabolism, Lysosome, Cornified envelope formation Velaglucerase alfa 💬 Velaglucerase alfa [1] 19 💬
14 GBA 💬 [4] Other glycan degradation, Sphingolipid metabolism, Lysosome, Cornified envelope formation Taliglucerase alfa 💬 Taliglucerase alfa [1] 19 💬
15 GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Sphingolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome Migalastat hydrochloride 💬 Migalastat [1] 19 💬
16 GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Sphingolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome Agalsidase beta 💬 Agalsidase beta [1] 19 💬
17 GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Sphingolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome Agalsidase alfa 💬 Agalsidase alfa [1] 19 💬
18 GLA 💬 [5] Galactose metabolism, Glycerolipid metabolism, Sphingolipid metabolism, Glycosphingolipid biosynthesis - globo and isoglobo series, Lysosome Pegunigalsidase alfa 💬 Pegunigalsidase alfa [1] 19 💬
19 IDS 💬 [2] Glycosaminoglycan degradation, Lysosome Idursulfase 💬 Idursulfase [1] 19 💬
20 IDS 💬 [2] Glycosaminoglycan degradation, Lysosome Pabinafusp alfa 💬 Pabinafusp alfa [1] 19 💬
21 IDS 💬 [2] Glycosaminoglycan degradation, Lysosome Idursulfase beta 💬 Idursulfase beta [1] 19 💬
22 IDS 💬 [2] Glycosaminoglycan degradation, Lysosome Tividenofusp alfa 💬 Tividenofusp alfa [1] 19 💬
23 IDUA 💬 [2] Glycosaminoglycan degradation, Lysosome Laronidase 💬 Laronidase [2] 19, 256 💬
24 LIPA 💬 [4] Steroid biosynthesis, Lysosome, Efferocytosis, Cholesterol metabolism Sebelipase alfa 💬 Sebelipase alfa [1] 19 💬
25 MAN2B1 💬 [2] Other glycan degradation, Lysosome Velmanase alfa 💬 Velmanase alfa [1] 19 💬
26 NAGLU 💬 [2] Glycosaminoglycan degradation, Lysosome Lesinidase alfa 💬 Lesinidase alfa [1] 19 💬
27 SMPD1 💬 [4] Sphingolipid metabolism, Sphingolipid signaling pathway, Lysosome, Necroptosis Olipudase alfa 💬 Olipudase alfa [1] 19 💬
28 SORT1 💬 [3] Lysosome, Neurotrophin signaling pathway, Cholesterol metabolism Latozinemab 💬 Latozinemab [2] 2, 127 💬
29 TPP1 💬 [1] Lysosome Cerliponase alfa 💬 Cerliponase alfa [1] 19 💬
30 uidA 💬 [6] Pentose and glucuronate interconversions, Ascorbate and aldarate metabolism, Glycosaminoglycan degradation, Porphyrin metabolism, Drug metabolism - other enzymes, Lysosome Vestronidase alfa 💬 Vestronidase alfa [1] 19 💬