18. Spinocerebellar degeneration Disease details / Clinical trials / Drug dev / DR info
Clinical trials : 83 / Drugs : 83 - (DrugBank : 31) / Drug target genes : 30 - Drug target pathways : 53
| Other names | SCD;:Spinocerebellar ataxia;SCA;Machado-Joseph disease;MJD;Dentatorubural pallidoluysian atrophy;Dentatorubropallidoluysial atrophy;DRPLA;Naito-Koyanagi disease;Early-onset ataxia with ocular motor ataxia and hypoalbuminemia;EAOH;Neu:Ataxia with vitamin E deficiency;AVED;Aprataxin deficiency;APTX deficiency;Friedreich ataxia;FRDA;Senataxin deficiency;SETX deficiency;Autosomal recessive spastic ataxia of Charlevoix-Saguenay;Spastic ataxia; | ||
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| Disease group | Neuromuscular diseases | ||
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Domestic patients
Med expenses recipients (FY2023) |
26,578 patients Age distribution
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| Related info (in Japanese) | - | ||
| Clinical research form [April 1, 2025 ~] (in Japanese) | Overview, diagnostic criteria, etc. (pdf), Clinical research form (pdf) | ||
| Specific pediatric chronic diseases, Japan (in Japanese) | 11-30-85. spinocerebellar degeneration; SCD | ||
| Subtypes | - | ||

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